- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Homozygous Sitosterolemia
Total 130 results
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Craig MillerNational Institute of Dental and Craniofacial Research (NIDCR)Completed
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University Hospital, Strasbourg, FranceCompletedCystic Fibrosis Homozygous for Phe 508 Del CFTR | Glucose Intolerance or Newly Diagnosis DiabetesFrance
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Acrotech Biopharma Inc.Axis Clinicals LimitedCompletedSolid Tumors | Hematological MalignanciesUnited States
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Centre Hospitalier Universitaire de Saint EtienneClaude Bernard University; Laboratoire de Physiologie de l'Exercice; Centre de...CompletedHemoglobin S Disease | Sickle Cell Hemoglobin C DiseaseFrance
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisBelgium, United Kingdom, Australia, Germany
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Parion SciencesVertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited Kingdom, United States, France, Ireland
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Vertex Pharmaceuticals IncorporatedCompleted
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Regeneron PharmaceuticalsSanofiCompletedHomozygous Familial HypercholesterolemiaUnited States, South Africa, Canada, Greece, Japan, Ukraine, Austria, Czechia, France, Germany, Italy, Taiwan, Turkey
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Nantes University HospitalCompletedStudy of cardiovAscular Contrasted Phenotypes in Patients With FamIliaI hypercholesteRolemia (SAFIR)Homozygous Familial HypercholesterolemiaFrance
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Australia, Austria, Canada, France, Greece, Italy, Japan, South Africa, Ukraine
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University of PennsylvaniaRegeneron PharmaceuticalsCompleted
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Carmel Medical CenterCompleted
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REGENXBIO Inc.CompletedHomozygous Familial Hypercholesterolemia (HoFH)United States
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Lundquist Institute for Biomedical Innovation at...Emmaus Medical, Inc.Terminated
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Emmaus Medical, Inc.FDA Office of Orphan Products DevelopmentCompletedSickle Cell Anemia | ThalassemiaUnited States
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolemiaSlovenia, Taiwan, Russian Federation, Canada, Netherlands, Brazil, Denmark, Mexico, Spain, Turkey
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Columbia UniversityCompletedAdverse Reaction to Spinal Anesthetic | Maternal Care for Cervical IncompetenceUnited States
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AmgenCompletedHomozygous Familial Hypercholesterolemia HoFHIndia
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University of ManitobaUnknown
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada
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NeuroBo Pharmaceuticals Inc.CompletedHypercholesteremiaUnited States, Canada, Israel
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The Medicines CompanyCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa
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Baylor College of MedicineTerminated
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University of PennsylvaniaCompletedHypercholesterolemia, FamilialUnited States
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Belgium, Netherlands, United Kingdom
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Canada
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Vertex Pharmaceuticals IncorporatedCompleted
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Spain, Australia, United Kingdom, Germany, Ireland
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisAustralia, United Kingdom
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HDL TherapeuticsMedStar Heart and Vascular InstituteUnknownHomozygous Familial Hypercholesterolemia | HoFHUnited States
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ProQR TherapeuticsEuropean CommissionCompletedCystic FibrosisUnited States, Spain, United Kingdom, Germany, Italy, Belgium, Canada, Czechia, Denmark, France
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University Hospital, BrestCyclacel Pharmaceuticals, Inc.; ManRos TherapeuticsTerminated
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.WithdrawnHomozygous Familial HypercholesterolemiaCanada
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AmgenCompletedHomozygous Familial HypercholesterolemiaNew Zealand, South Africa, France, United States, Spain, Belgium, Czechia, Italy, Netherlands, Hong Kong, Canada, Lebanon
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada
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Aegerion Pharmaceuticals, Inc.CompletedFamilial Hypercholesterolemia - HomozygousJapan
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Vertex Pharmaceuticals IncorporatedTerminated
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Aegerion Pharmaceuticals, Inc.CompletedFamilial HypercholesterolemiaUnited States, Canada, Italy, South Africa
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, United Kingdom, Germany, Spain, Switzerland, Canada, Netherlands, Italy, Ireland, Sweden, France, Denmark
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Novartis PharmaceuticalsTerminatedc-MET Inhibitor; PI3K Inhibitor, PTEN Mutations, Homozygous Del. of PTEN or PTEN Neg. by IHC, c-Met Ampli. by FISH, INC280, BKM120, Buparlisib; Recurrent GBMSpain, Switzerland, Germany, United States, Netherlands
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National Institute of Diabetes and Digestive and...Completed
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada, Germany, United Kingdom
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Vertex Pharmaceuticals IncorporatedCompleted
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Aegerion Pharmaceuticals, Inc.FDA Office of Orphan Products DevelopmentCompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, South Africa
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Assistance Publique - Hôpitaux de ParisActelion; CRCM (Centres de Ressources et de Compétences de la Mucoviscidose)Completed
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Taiwan, Belgium, Denmark, Israel
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Aegerion Pharmaceuticals, Inc.WithdrawnHomozygous Familial Hypercholesterolemia
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Aegerion Pharmaceuticals, Inc.WithdrawnHomozygous Familial Hypercholesterolemia
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, France, United Kingdom, Germany, Belgium, Australia, Denmark, Canada, Sweden