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Search clinical trials for: Oligonucleotides, Antisense
Total 120 results
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Algemeen Ziekenhuis Maria MiddelaresNot yet recruiting
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Massachusetts General Hospitaln-Lorem FoundationNot yet recruiting
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CAMP4 Therapeutics CorporationRecruiting
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QurAlis CorporationRecruitingAmyotrophic Lateral SclerosisCanada, Germany, Netherlands, Ireland, United Kingdom, Belgium
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GlaxoSmithKlineRecruitingChronic Hepatitis BItaly, Japan, Spain, Korea, Republic of, Argentina, Canada, France, Poland
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GlaxoSmithKlineRecruitingChronic Hepatitis B | Hepatitis B, ChronicUnited States, Australia, France, Germany, Italy, Spain, Taiwan, Mexico, United Kingdom, Greece, Korea, Republic of, China, Argentina, Brazil, Bulgaria, Japan, Poland, Hungary, Philippines, Singapore, India, Turkey, Thailand, Canada, Ro... and more
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Institut National de la Santé Et de la Recherche...Recruiting
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University Hospital, MontpellierRecruiting
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Bio-Path Holdings, Inc.RecruitingAcute Myeloid Leukemia, in Relapse | Acute Myeloid Leukemia RefractoryUnited States
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First Affiliated Hospital of Fujian Medical UniversityPeking Union Medical College Hospital; Fujian Medical University Union HospitalRecruiting
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University Hospital, MontpellierHôpital Cochin; Hôpital Necker-Enfants Malades; Foch Hospital, Suresnes, FRANCERecruitingCystic Fibrosis | CFTR Gene MutationFrance
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ProQR TherapeuticsRecruitingEye Diseases | Neurologic Manifestations | Retinal Degeneration | Retinal Dystrophies | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalBelgium, Brazil, Canada, Germany, Italy, Netherlands, United Kingdom
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Brigham and Women's HospitalNot yet recruitingTransthyretin Amyloid CardiopathyUnited States
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Bio-Path Holdings, Inc.RecruitingFallopian Tube Neoplasms | Carcinoma, Ovarian Epithelial | Solid Tumor | Endometrial Cancer | Peritoneal Cancer | Solid Tumor, AdultUnited States
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Bio-Path Holdings, Inc.RecruitingFollicular Lymphoma | Hodgkin Lymphoma | Waldenstrom Macroglobulinemia | Mantle Cell Lymphoma | Marginal Zone Lymphoma | Chronic Lymphocytic Leukemia (CLL) | Small Lymphocytic Lymphoma (SLL) | DLBCL | Cutaneous T-cell Lymphoma (CTCL) | Peripheral T-cell Lymphoma (PTCL)United States
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Assistance Publique - Hôpitaux de ParisRecruiting
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Novartis PharmaceuticalsActive, not recruitingProgressive Supranuclear Palsy (PSP)Germany, United Kingdom, Canada, United States
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University of OuluLapland Central Hospital Rovaniemi FinlandCompletedSmoking Cessation | Electronic CigaretteFinland
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Ionis Pharmaceuticals, Inc.CompletedPrimary IgA NephropathyCanada, Australia, New Zealand, Singapore
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AstraZenecaCompleted
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n-Lorem FoundationMayo ClinicActive, not recruitingAmyotrophic Lateral SclerosisUnited States
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University of California, San DiegoCalifornia Institute for Regenerative Medicine (CIRM); n-Lorem FoundationActive, not recruitingGenetic DiseaseUnited States
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Daiichi Sankyo Co., Ltd.Orphan Disease Treatment Institute Co., Ltd.Completed
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Hoffmann-La RocheCompletedHuntingtons DiseaseUnited States, United Kingdom, Australia, Canada, Japan, Poland, Netherlands, Germany, Russian Federation, France, Spain, Argentina, New Zealand, Austria, Denmark, Italy, Switzerland, Chile
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AutotelicbioCompletedSolid TumorKorea, Republic of
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Praxis Precision MedicinesActive, not recruitingEpilepsy | SCN2A-DEEUnited States
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University of NebraskaNational Cancer Institute (NCI); Genta IncorporatedTerminatedStage III Adult Diffuse Large Cell Lymphoma | Stage IV Adult Diffuse Large Cell Lymphoma | Contiguous Stage II Adult Diffuse Large Cell Lymphoma | Noncontiguous Stage II Adult Diffuse Large Cell Lymphoma | Stage I Adult Diffuse Large Cell LymphomaUnited States
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Daiichi Sankyo Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyJapan
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Institut National de la Santé Et de la Recherche...Biogen; Ionis Pharmaceuticals, Inc.CompletedSpinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 7France
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ProQR TherapeuticsTerminatedEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, United Kingdom
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Ionis Pharmaceuticals, Inc.Completed
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ProQR TherapeuticsTerminatedEye Diseases | Neurologic Manifestations | Eye Diseases, Hereditary | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Belgium
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ProQR TherapeuticsTerminatedRetinitis Pigmentosa | Usher Syndrome Type 2United States, Canada, France
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ProQR TherapeuticsCompletedLeber's Congenital AmaurosisUnited States, Belgium
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Hospital do CoracaoIonis Pharmaceuticals, Inc.; Hospital Moinhos de VentoCompleted
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The University of Texas Health Science Center at...University of PittsburghCompletedHead and Neck Cancer | Squamous Cell CarcinomaUnited States
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ProQR TherapeuticsActive, not recruitingEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, Netherlands, United Kingdom, Germany
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TAK-Circulator Co.CompletedHealthy VolunteerJapan
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ProQR TherapeuticsActive, not recruitingEye Diseases | Retinitis | Eye Diseases, Hereditary | Retinal Dystrophies | Vision Disorders | Retinal Disease | Autosomal Dominant Retinitis Pigmentosa | Vision TunnelUnited States
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ProQR TherapeuticsCompletedEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, Canada, France
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ProQR TherapeuticsActive, not recruitingEye Diseases | Neurologic Manifestations | Eye Diseases, Hereditary | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Belgium, Brazil, Canada, France, Germany, Italy, Netherlands, United Kingdom
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Phoenicis TherapeuticsTerminatedEpidermolysis Bullosa Dystrophica, Recessive | Epidermolysis Bullosa Dystrophica, DominantUnited States, Spain, France
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National Cancer Institute (NCI)TerminatedAdenocarcinoma of the Gastroesophageal Junction | Stage IV Gastric Cancer | Recurrent Gastric Cancer | Squamous Cell Carcinoma of the Esophagus | Adenocarcinoma of the Esophagus | Recurrent Esophageal Cancer | Stage IV Esophageal Cancer | Diffuse Adenocarcinoma of the Stomach | Intestinal Adenocarcinoma... and other conditionsUnited States
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Brigham and Women's HospitalUnknown
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david andrewsCompletedNeoplasms | Malignant GliomaUnited States
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ProQR TherapeuticsEuropean CommissionCompletedCystic FibrosisUnited States, France, Belgium
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Bio-Path Holdings, Inc.WithdrawnAcute Myeloid Leukemia | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia, Ph1-PositiveUnited States
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Bio-Path Holdings, Inc.CompletedRecurrent Adult Acute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Ph1 Positive CMLUnited States
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Mary Crowley Medical Research CenterTerminatedCarcinoma, Advanced MetastaticUnited States
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Imperial College LondonSarepta Therapeutics, Inc.; Department of Health, United KingdomCompletedDuchenne Muscular DystrophyUnited Kingdom