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Search clinical trials for: Spinocerebellar ataxia-SCA2
Total 400 results
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European Friedreich's Ataxia Consortium for Translational...RecruitingFriedreich's AtaxiaAustria, Germany, Italy, Spain, Belgium, Czechia, France, Greece, Ireland, United Kingdom
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Murdoch Childrens Research InstituteActive, not recruiting
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Design Therapeutics, Inc.CompletedFriedreich AtaxiaUnited States
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RWTH Aachen UniversityAssistance Publique - Hôpitaux de ParisWithdrawnFriedreich AtaxiaSpain, Italy, Austria, Germany, United Kingdom, France
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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University of MinnesotaCompleted
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research Alliance; Vidara Therapeutics Research LtdCompleted
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLCCompletedFriedreich AtaxiaUnited States
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PTC TherapeuticsCompletedFriedreich's AtaxiaUnited States
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University Hospital, MontpellierNeurogenetic department, CHU Bordeaux; Genetic Department , CHU Montpellier-France and other collaboratorsUnknown
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IpsenCompleted
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Ralitza GavrilovaCardero Therapeutics, Inc.Completed
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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Azienda Policlinico Umberto ICompleted
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University of Colorado, DenverCompleted
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, United Kingdom, Belgium, France, Germany
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, Germany, United Kingdom
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Federico II UniversityFriedreich's Ataxia Research Alliance; Associazione Italiana per la lotta alle...Completed
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University of South FloridaPfizer; Friedreich's Ataxia Research AllianceTerminatedFriedreich's AtaxiaUnited States
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National Human Genome Research Institute (NHGRI)CompletedFriedreich AtaxiaUnited States
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National Institute of Neurological Disorders and...CompletedFriedreich AtaxiaUnited States
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Institut National de la Santé Et de la Recherche...Imagine InstituteRecruiting
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Children's Hospital of PhiladelphiaNational Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Larimar Therapeutics, Inc.CompletedFriedreich AtaxiaUnited States
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Reata, a wholly owned subsidiary of BiogenAbbVie; Friedreich's Ataxia Research AllianceActive, not recruitingFriedreich AtaxiaUnited States, Australia, Austria, Italy, United Kingdom
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Monash UniversityChildren's Hospital of Philadelphia; McGill University; University of Florida; University... and other collaboratorsActive, not recruitingFriedreich AtaxiaUnited States, Canada, Australia, Brazil, Germany
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Berta AlemanyInstitut d'Investigació Biomèdica de Girona Dr. Josep Trueta; Universitat de... and other collaboratorsCompleted
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IRCCS Eugenio MedeaUniversity of Rome Tor VergataCompleted
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Neurocrine BiosciencesTakedaCompletedFriedreich AtaxiaUnited States
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Institut National de la Santé Et de la Recherche...Completed
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Larimar Therapeutics, Inc.Children's Hospital of PhiladelphiaCompletedFriedreich AtaxiaUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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Bioblast Pharma Ltd.CompletedMachado-Joseph Disease / Spinocerebellar Ataxia 3Israel
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H. Lundbeck A/SCompletedFriedreich's AtaxiaGermany, Austria, Italy
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Assistance Publique - Hôpitaux de ParisCompletedEffect of Pioglitazone Administered to Patients With Friedreich's Ataxia: Proof of Concept (ACTFRIE)Friedreich's AtaxiaFrance
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Assistance Publique - Hôpitaux de ParisCompleted
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Cairo UniversityCompletedCore Stability | Ataxic Cerebral Palsied Children | Balance and Coordination | Severity of the AtaxiaEgypt
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University of California, Los AngelesUniversity of South Florida; University of RochesterWithdrawn
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Hospital de Clinicas de Porto AlegreCompletedSpinocerebellar Ataxia Type 3 | Machado Joseph DiseaseBrazil
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German Center for Neurodegenerative Diseases (DZNE)McMaster University; Sorbonne UniversityRecruitingFriedreich AtaxiaAustria, Germany, France
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Werium Assistive SolutionsCentro Lescer; Cajal Institute of the Spanish National Research CouncilCompleted
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Adverum Biotechnologies, Inc.Adverum Biotechnologies SAS, a wholly owned subsidiary of Adverum Biotechnologies...CompletedFriedreich's AtaxiaFrance
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University of PittsburghFriedreich's Ataxia Research AllianceCompleted
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Murdoch Childrens Research InstituteFriedreich's Ataxia Research AllianceCompleted
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University of Sao Paulo General HospitalUnknownCerebellar AtaxiaBrazil
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingCerebellar AtaxiaUnited States