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Search clinical trials for: alpha 1-Antitrypsin Deficiency
Total 18115 results
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Wave Life Sciences Ltd.Not yet recruiting
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Beam Therapeutics Inc.Not yet recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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Wave Life Sciences Ltd.RecruitingAlpha-1 Antitrypsin DeficiencyUnited Kingdom
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Chiesi Farmaceutici S.p.A.Not yet recruiting
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TakedaRecruitingAlpha1-Antitrypsin DeficiencyUnited States, Poland
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Krystal Biotech, Inc.RecruitingAlpha 1-Antitrypsin DeficiencyUnited States
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Permian Health Lung InstituteThe Gambia Committee on Traditional Practices Affecting the Health of Women...Not yet recruitingCOPD | Lung Function Decreased | Alpha 1-AntitrypsinGambia
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Valneva Austria GmbHRecruitingChikungunya Virus InfectionPanama
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Inhibrx, Inc.Not yet recruitingEmphysema | Alpha 1-Antitrypsin Deficiency
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Inhibrx, Inc.RecruitingEmphysema | Alpha 1-Antitrypsin DeficiencyUnited States, Australia, United Kingdom, New Zealand
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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TakedaTakeda Development Center Americas, Inc.RecruitingAlpha1-Antitrypsin DeficiencyUnited States, Belgium, Switzerland, Canada, Australia, Germany, United Kingdom, Austria, France, Spain, Portugal, Italy, Poland, Brazil
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Assiut UniversityNot yet recruitingPre-Eclampsia | Intrauterine Growth Restriction | alpha1 Anti-trypsin
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University of ThessalyNot yet recruitingOxidative Stress | Carbohydrate Metabolism Disorder | G6PD Deficiency
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University of California, Los AngelesRecruitingAdenosine Deaminase Severe Combined Immune DeficiencyUnited States
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National Cancer Institute (NCI)RecruitingLynch SyndromeUnited States, Puerto Rico
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University of California, IrvineHudson Valley Healing Arts CenterNot yet recruiting
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University of CopenhagenHvidovre University HospitalRecruitingChronic Liver DiseaseDenmark
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Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRecruitingPyruvate Dehydrogenase Complex Deficiency | Pyruvate Dehydrogenase E1 Alpha Deficiency | Pyruvate Dehydrogenase E1-Beta Deficiency | Pyruvate Dehydrogenase E2 Deficiency | Pyruvate Dehydrogenase Phosphatase DeficiencyUnited Kingdom
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RecruitingHaploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion (HAPLOTAB)Myelodysplastic Syndromes | Primary Immunodeficiency Diseases | Hemoglobinopathies | Chronic Myeloid Leukemia | Cytopenia | Severe Aplastic Anemia | Bone Marrow Failure Syndrome | Acute Myeloid Leukemia in Remission | Hemophagocytic Lymphohistiocytoses | Acute Lymphoblastic Leukemia in Remission | Severe...United States
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University Hospital, MontpellierRecruitingAromatic L-Amino Acid Decarboxylase DeficiencyFrance
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Thomayer University HospitalMasaryk UniversityRecruiting
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University of NottinghamNottingham University Hospitals NHS TrustRecruitingChronic Obstructive Pulmonary Disease | Alpha 1-Antitrypsin DeficiencyUnited Kingdom
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Grifols Therapeutics LLCRecruiting
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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Johns Hopkins All Children's HospitalRecruitingMetabolic Disease | Primary Immune Deficiency DisordersUnited States
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National Cancer Institute (NCI)RecruitingAcute Adult T-Cell Leukemia/Lymphoma | Adult T-Cell Leukemia/Lymphoma | Chronic Adult T-Cell Leukemia/Lymphoma | HTLV-1 InfectionUnited States
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Kamada, Ltd.Syneos HealthRecruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, Sweden, Ireland, Netherlands, Belgium, Finland
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Hospital Universitari Vall d'Hebron Research InstituteEuropean Respiratory SocietyRecruitingAlpha 1-Antitrypsin DeficiencySpain
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Alpha-1 FoundationRecruiting
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National Institute of Allergy and Infectious Diseases...Not yet recruitingHyper-Immunoglobulin E. Syndrome (HEIS) | Chronic Granulomatous Disease (CGD)United States
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Columbia UniversityAlpha-1 FoundationRecruitingChronic Obstructive Pulmonary Disease | Acute Exacerbation Copd | Alpha-1 Anti-trypsin DeficiencyUnited States
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CSL BehringRecruitingAcute-graft-versus-host DiseaseUnited States, Korea, Republic of, Spain, Australia, Germany, Italy, Turkey, Japan
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McMaster UniversitySt. Joseph's Healthcare HamiltonRecruitingBronchiectasis | Chronic Obstructive Pulmonary Disease | Asthma | Emphysema | Pulmonary Fibrosis | Alpha 1-Antitrypsin Deficiency | Bronchopulmonary Dysplasia | Sarcoidosis, PulmonaryCanada
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Children's Hospital of PhiladelphiaUniversity of California, San FranciscoRecruitingImmunodeficiencies | Immune Dysregulation SyndromesUnited States
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Schön Klinik Berchtesgadener LandCSL BehringRecruitingChronic Obstructive Pulmonary DiseaseGermany
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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St. Anna KinderkrebsforschungAssistance Publique - Hôpitaux de Paris; Australian & New Zealand Children's... and other collaboratorsRecruitingAllogeneic Stem Cell Transplantation for Children and Adolescents With Acute Lymphoblastic LeukaemiaAcute Lymphoblastic LeukaemiaItaly, Israel, Spain, Argentina, Australia, Austria, Belarus, Belgium, Canada, Chile, Croatia, Czechia, Denmark, Finland, Greece, Malaysia, Mexico, Netherlands, Norway, Poland, Romania, Saudi Arabia, Slovakia, Sweden, Switzerland, Turkey, F... and more
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University of FloridaRecruitingAlpha-1 Antitrypsin Deficiency | Cystic Fibrosis (CF) | AATD | AAT DeficiencyUnited States
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McGill University Health Centre/Research Institute...RecruitingPeroxisome Biogenesis Disorder | Zellweger Spectrum Disorder | RCDP - Rhizomelic Chondrodysplasia Punctata | D-Bifunctional Protein Deficiency | Alpha-Methylacyl-CoA Racemase Deficiency | Peroxisomal Acyl-CoA Oxidase Deficiency | Peroxisomal Acyl-CoA Oxidase 2 Deficiency | ATP Binding Cassette Subfamily... and other conditionsCanada
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingPompe DiseaseUnited States
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Cure CMDRecruitingEmery-Dreifuss Muscular Dystrophy | Congenital Myasthenic Syndrome | Limb-Girdle Muscular Dystrophy | Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency | Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy and Abnormal Glycosylation of Dystroglycan With Severe Epilepsy) and other conditionsUnited States
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingLiver Diseases | Alpha 1-Antitrypsin Deficiency | Alagille SyndromeUnited States, Canada
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University of FloridaRecruitingAlpha-1 Antitrypsin DeficiencyUnited States
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Genzyme, a Sanofi CompanyRecruitingFabry DiseaseCroatia, United States, Argentina, Australia, Belgium, Bulgaria, Canada, Germany, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Malaysia, Philippines, Poland, Romania, Singapore, Slovakia, Taiwan, Thailand, United Kingdom, Vietn... and more
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National Institute of Allergy and Infectious Diseases...Active, not recruitingPGM3 Deficiency | Eosinophilic and/or Atopic Dermatitis | OSMR Deficiency | Primary Localized Cutaneous Amyloidosis | Hereditary Alpha-tryptasemiaUnited States