- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: chromosomal abnormalities in single cells
Total 459167 results
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Great Ormond Street Hospital for Children NHS Foundation...UnknownX-linked Severe Combined ImmunodeficiencyUnited Kingdom
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KU LeuvenUnknown
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Eunice Kennedy Shriver National Institute of Child...UnknownChromosome DisordersUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Chronic Granulomatous DiseaseUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingHemophilia A | Hemophilia B | Cystic Fibrosis | Sickle Cell Disease | Muscular Dystrophy, Duchenne | Fragile X Syndrome | Huntington Disease | Myotonic Dystrophy | Autosomal Recessive Polycystic Kidney Disease | Neurofibromatosis-Noonan Syndrome | Muscular Dystrophy, Becker | Invasive PreNatal Diagnosis in a... and other conditionsFrance
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Assistance Publique - Hôpitaux de ParisNot yet recruitingMultiple Sclerosis | Autoimmune Diseases | Rheumatoid Arthritis | Systemic Lupus Erythematosus | Atopic Dermatitis | Vitiligo | Alopecia | Autoimmune Thyroiditis | Inflammatory Disease | Acquired Bone Marrow Aplasia | Gvhd
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Beacon TherapeuticsRecruitingX-Linked Retinitis PigmentosaUnited States
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSevere Combined Immunodeficiency, X-LinkedUnited Kingdom
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IRCCS San RaffaeleFondazione TelethonRecruitingChronic Granulomatous Disease X-linked (X-CGD)Italy
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Metcela Inc.RecruitingHypoplastic Left Heart Syndrome | Single VentricleJapan
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Children's Hospital of PhiladelphiaRecruitingLeukemia | Bone Marrow Failure Syndromes | Immunodeficiencies | Inborn Errors of Metabolism | Immunodysregulation Polyendocrinopathy Enteropathy X-linked SyndromeUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingX-linked Severe Combined Immunodeficiency (XSCID)United States
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Nationwide Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI)Recruiting
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University of PittsburghNational Institutes of Health (NIH)Recruiting
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Mayo ClinicActive, not recruitingEnd Stage Renal Disease (ESRD) | Vascular Access ComplicationUnited States
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PfizerTerminatedSickle Cell Disease | Vaso-occlusive Pain Episode in Sickle Cell Disease | Vaso-occlusive CrisisUnited States, Oman, France, Brazil, Colombia, Lebanon, Nigeria, Germany, Italy, Kenya, Saudi Arabia, Turkey, United Kingdom, Zambia
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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University of FloridaLive Like Bella Pediatric Cancer ResearchCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Sickle Cell Disease | Hurler Syndrome | Chronic Granulomatous Disease | Thalassemia | Wiskott-Aldrich Syndrome | Adrenoleukodystrophy | X-linked Lymphoproliferative Disease | Diamond Blackfan Anemia | Bone Marrow Failure Syndrome | Hemophagocytic... and other conditionsUnited States
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David WilliamsActive, not recruiting
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Timothy J Nelson, MD, PhDChildren's Hospital of Philadelphia; Children's Hospital Colorado; University... and other collaboratorsActive, not recruitingHypoplastic Left Heart SyndromeUnited States
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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Okayama UniversityNational Cerebral and Cardiovascular CenterCompletedHeart Failure | Hypoplastic Left Heart Syndrome | Single VentricleJapan
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Timothy J Nelson, MD, PhDMayo ClinicCompletedCongenital Heart DiseaseUnited States
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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Institut fuer anwendungsorientierte Forschung und...University Medical Center GoettingenCompletedMyelodysplastic Syndromes (MDS) | Chromosmal Aberrations | Karyotype Evolution | Rare Abnormalities | Cytogenetic MonitoringGermany
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Shenzhen Geno-Immune Medical InstituteUnknownSCID, X LinkedChina
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Allergy and Asthma Consultants, Wichita, KansasAidan Foundation; Neil H. Riordan PhDCompletedDuchenne's Muscular DystrophyUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedSevere Combined Immunodeficiency | Adenosine Deaminase Deficiency | Immune System Disorder | Autosomal Recessive Disorder | Purine-Nucleoside Phosphorylase Deficiency | Severe Combined Immunodeficiency With Absence of T and B Cells | X-Linked Severe Combined ImmunodeficiencyUnited States
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Changhai HospitalUnknownDiagnoses Disease | Urothelial Carcinoma | Chromosomal Abnormality | Urine MarkingChina
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jCyte, IncCalifornia Institute for Regenerative Medicine (CIRM)CompletedRetinitis Pigmentosa (RP)United States
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Masonic Cancer Center, University of MinnesotaTerminatedHematologic Diseases | Hemophagocytic Lymphohistiocytosis | Immunologic Diseases | Chediak-Higashi Syndrome | X-Linked Lymphoproliferative Disorders | Griscelli Syndrome | Langerhans-Cell HistiocytosisUnited States
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National Institute of Allergy and Infectious Diseases...CompletedGenetic Diseases, X-Linked | Lymphoproliferative Disease | X-Linked Lymphoproliferative DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...CompletedSevere Combined ImmunodeficiencyUnited States
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Children's Hospital Los AngelesLucile Packard Children's HospitalTerminatedMetabolic Diseases | Stem Cell Transplantation | Chronic Granulomatous Disease | Bone Marrow Transplantation | Thalassemia | Wiskott-Aldrich Syndrome | Genetic Diseases | Peripheral Blood Stem Cell Transplantation | Pediatrics | Diamond-Blackfan Anemia | Allogeneic Transplantation | Combined Immune Deficiency | X-linked Lymphoproliferative Disease
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University of Medicine and Dentistry of New JerseyNational Cancer Institute (NCI)WithdrawnRecurrent Adult Acute Myeloid Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent... and other conditionsUnited States
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Children's Hospital Los AngelesCompletedGranuloma | Anemia | Thrombocytopenia | Neutropenia | Sickle Cell Disease | Thalassemia | Niemann-Pick Disease | Wiskott-Aldrich Syndrome | Osteopetrosis | Fucosidosis | Chediak Higashi Syndrome | Hurler DiseaseUnited States
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Vanderbilt-Ingram Cancer CenterNational Cancer Institute (NCI)TerminatedLymphoma | Myelodysplastic Syndromes | Leukemia | Multiple Myeloma and Plasma Cell Neoplasm | Graft Versus Host DiseaseUnited States
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Great Ormond Street Hospital for Children NHS Foundation...WithdrawnGranulomatous Disease, Chronic, X-linked, VariantUnited Kingdom
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Celgene CorporationUnknown
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityRecruitingCarpal Tunnel Syndrome | Surgery | Ultralsound-GuideChina
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Novartis PharmaceuticalsNot yet recruiting
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Boston Children's HospitalNot yet recruitingThrombosis | Congenital Heart Disease | Single-ventricleUnited States
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Beijing Geekgene Technology Co., LTDRecruitingCervical Cancer | Gastric Cancer | Esophageal Cancer | Non-Small Cell Lung Cancer NSCLC | Triple Negative Breast Cancer TNBCChina
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Shandong Qilu Stem Cells Engineering Co., Ltd.Qilu Children's Hospital of Shandong UniversityRecruitingBronchopulmonary Dysplasia | Hypoxic-Ischemic Encephalopathy | Short Bowel SyndromeChina
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University of St. Augustine for Health SciencesRecruitingSpina BifidaUnited States
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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Shanghai Changzheng HospitalCARsgen Therapeutics Co., Ltd.Not yet recruiting
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Wave Life Sciences Ltd.Not yet recruiting
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Peking University First HospitalRecruitingRenal Cell Carcinoma | VHL SyndromeChina
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University of Campania "Luigi Vanvitelli"Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico; University of Milan and other collaboratorsRecruitingChronic Kidney Diseases | Ureteropelvic Junction ObstructionItaly