- ICH GCP
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Search clinical trials for: thérapie génique
Total 25948 results
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SparingVisionRecruiting
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International Extranodal Lymphoma Study Group (IELSG)RecruitingSplenic Marginal Zone LymphomaSpain, Denmark, France, Norway, Switzerland, Sweden, Italy
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Replimune Inc.Roche Pharma AGNot yet recruitingRecurrent Hepatocellular Carcinoma | Metastatic Hepatocellular Carcinoma | Locally Advanced Hepatocellular CarcinomaUnited States, United Kingdom, France, Germany, Greece
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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Genprex, Inc.RecruitingSmall Cell Lung Cancer Extensive StageUnited States
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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PfizerRecruitingDuchenne Muscular DystrophyUnited States
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Christian HinrichsRecruitingCervical Cancer | HPV-Related Malignancy | Metastatic Cancer | Anal Cancer | Oropharynx Cancer | Vaginal Cancer | HPV-Related Carcinoma | HPV-Related Cervical Carcinoma | HPV Positive Oropharyngeal Squamous Cell Carcinoma | Penile Cancer | HPV-Related Adenocarcinoma | HPV-Related Adenosquamous Carcinoma | HPV-Related... and other conditionsUnited States
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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Christian HinrichsNational Cancer Institute (NCI)Not yet recruitingCervical Cancer | HPV-Related Malignancy | Vulvar Cancer | Anal Cancer | Oropharynx Cancer | Vaginal Cancer | HPV-Related Carcinoma | HPV Positive Oropharyngeal Squamous Cell Carcinoma | Penile Cancer | HPV-Associated Cervical Carcinoma | HPV-Related Adenocarcinoma | HPV-Related Adenosquamous Carcinoma | HPV-Related... and other conditionsUnited States
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Washington University School of MedicineBiogen; BioLineRx, Ltd.RecruitingSickle Cell DiseaseUnited States
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Opus Genetics, IncRecruiting
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Asklepios Biopharmaceutical, Inc.RecruitingCongestive Heart FailureUnited States
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PfizerRecruitingHemophilia A | Hemophilia BAustralia, United States, Turkey
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Intima Bioscience, Inc.Not yet recruitingCarcinoma, Non-Small-Cell Lung | Adenocarcinoma of Lung | Stage IV Non-small Cell Lung Cancer | Squamous Cell Lung Cancer | Metastatic Non Small Cell Lung Cancer | Large Cell Lung CancerUnited States
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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Prevail TherapeuticsEli Lilly and CompanyRecruitingGaucher Disease | Gaucher Disease, Type 1United States, Spain, Germany
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Christian HinrichsNational Cancer Institute (NCI); Cancer Immunology and Metabolism Center of...RecruitingCervical Cancer | Breast Cancer | Gastric Cancer | Lung CancerUnited States
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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ICM Co. Ltd.Not yet recruiting
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Lexeo TherapeuticsRecruitingFriedreich Ataxia | Cardiomyopathy, SecondaryUnited States, Canada
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University of California, Los AngelesRecruitingAdenosine Deaminase Severe Combined Immune DeficiencyUnited States
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AbbVieRecruitingCNV | AMD | nAMD | Wet Age-related Macular Degeneration | wAMD | WetAMDUnited States, Puerto Rico, Canada
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SwanBio Therapeutics, Inc.RecruitingAMN | AMN Gene Mutation | X-ALDNetherlands, United States
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David WilliamsNational Heart, Lung, and Blood Institute (NHLBI); bluebird bio; California Institute... and other collaboratorsRecruitingA Gene Transfer Study Inducing Fetal Hemoglobin in Sickle Cell Disease (GRASP, BMT CTN 2001) (GRASP)Sickle Cell DiseaseUnited States
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Novartis PharmaceuticalsRecruitingSpinal Muscular Atrophy (SMA)Spain, Canada, Taiwan, Belgium, Japan, Italy, Singapore, United Kingdom, France, Australia, Denmark, United States
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4D Molecular TherapeuticsRecruiting
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UniQure Biopharma B.V.RecruitingHuntington DiseasePoland, United Kingdom, Germany
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Bacchetta, Rosa, MDFood and Drug Administration (FDA); California Institute for Regenerative Medicine...Recruiting
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Asklepios Biopharmaceutical, Inc.RecruitingMuscular Dystrophy | Limb Girdle Muscular Dystrophy | LGMD2I | LGMD | Limb-Girdle Muscular Dystrophy Type 2 | LGMD2 | FKRP | FKRP Mutation | Fukutin Related ProteinUnited States
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Neurogene Inc.RecruitingNeuronal Ceroid Lipofuscinosis CLN5United States, United Kingdom
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4D Molecular TherapeuticsRecruitingNeovascular (Wet) Age-Related Macular DegenerationUnited States, Puerto Rico
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Ottawa Hospital Research InstituteRecruitingProstate CancerCanada
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Vanderbilt University Medical CenterJohns Hopkins University; Emory University; Children's National Research InstituteRecruitingHeart Disease | Sickle Cell Disease | Pulmonary Disease | Renal DiseaseUnited States
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Institute of Hematology & Blood Diseases HospitalRecruiting
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BeiGeneRecruitingMarginal Zone Lymphoma | Relapsed/Refractory Follicular LymphomaUnited States, Italy, Spain, China, United Kingdom, Australia, Israel, Korea, Republic of, France, Brazil, Ireland, Czechia, Romania, Argentina, Puerto Rico, Austria
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Assistance Publique - Hôpitaux de ParisRecruitingArtemis (DCLRE1C ) Deficient Severe Combined ImmunodeficiencyFrance
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Genprex, Inc.RecruitingNon Small Cell Lung CancerUnited States
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St. Jude Children's Research HospitalRecruitingHemophilia B | Gene TherapyUnited States
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Mark TuszynskiOhio State UniversityRecruitingMild Cognitive Impairment | Alzheimer's DiseaseUnited States
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National Cancer Institute (NCI)RecruitingKita-kyushu Lung Cancer Antigen 1, HumanUnited States
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National Cancer Institute (NCI)RecruitingHepatocellular Carcinoma | Hepatocellular Cancer | Metastatic Hepatocellular CarcinomaUnited States
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Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
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The Methodist Hospital Research InstituteGenentech, Inc.Recruiting
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World Federation of HemophiliaNot yet recruiting
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ICM Biotech Australia Pty Ltd.Recruiting
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Beacon TherapeuticsRecruitingX-Linked Retinitis PigmentosaUnited States
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Myrtelle Inc.RecruitingCanavan DiseaseUnited States
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Kamau TherapeuticsRecruitingSickle Cell DiseaseUnited States
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Leiden University Medical CenterZonMw: The Netherlands Organisation for Health Research and Development; Horizon...RecruitingSevere Combined Immunodeficiency Due to RAG1 DeficiencySpain, Netherlands, Italy, Poland, Australia, Turkey, United Kingdom