- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: thérapie génique
Total 25948 results
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STZ eyetrialEnrolling by invitationRetinitis PigmentosaGermany
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UNC Lineberger Comprehensive Cancer CenterActive, not recruitingBreast CancerUnited States
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Orchard TherapeuticsOspedale San RaffaeleActive, not recruitingLysosomal Storage Disease | Metachromatic LeukodystrophyItaly
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Brazil
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Canada
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Novartis PharmaceuticalsCompletedMuscular Atrophy, SpinalBrazil, Argentina
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Nanoscope Therapeutics Inc.Completed
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Nanoscope Therapeutics Inc.Enrolling by invitationStargardt DiseaseUnited States
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Jonsson Comprehensive Cancer CenterCalifornia Institute for Regenerative Medicine (CIRM)TerminatedSarcoma | Unresectable Malignant Neoplasm | Locally Advanced Malignant Neoplasm | HLA-A*0201 Positive Cells Present | NY-ESO-1 PositiveUnited States
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REGENXBIO Inc.Enrolling by invitation
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Adverum Biotechnologies, Inc.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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BioMarin PharmaceuticalCompleted
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University of NebraskaNational Cancer Institute (NCI)Completed
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Maxivax SAActive, not recruiting
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Eric Bernicker, MDTerminatedNonsquamous Nonsmall Cell Neoplasm of Lung | Metastatic Uveal Melanoma | Lung Squamous Cell Carcinoma Stage IVUnited States
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University of NebraskaNational Cancer Institute (NCI)Terminated
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom
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AVROBIOTerminatedFabry DiseaseAustralia, Brazil
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AVROBIOTerminatedType 1 Gaucher DiseaseUnited States, Canada
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Alaunos TherapeuticsActive, not recruitingGynecologic Cancer | Colorectal Cancer | Pancreatic Cancer | Ovarian Cancer | Cholangiocarcinoma | Adenocarcinoma of Lung | Endometrial Cancer | Non-small Cell Lung Cancer | Ovarian Carcinoma | Squamous Cell Lung Cancer | Ovary Neoplasm | Adenosquamous Cell Lung CancerUnited States
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Candel Therapeutics, Inc.University of PennsylvaniaCompletedBreast Cancer | Ovarian Cancer | Lung Cancer | Mesothelioma | Malignant Pleural EffusionUnited States
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Candel Therapeutics, Inc.CompletedGlioblastoma Multiforme | Malignant Glioma | Anaplastic AstrocytomaUnited States
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Candel Therapeutics, Inc.Boston Children's HospitalCompletedMalignant Glioma | Recurrent EpendymomaUnited States
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Candel Therapeutics, Inc.CompletedPancreatic Cancer | Pancreatic AdenocarcinomaUnited States
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University of FloridaUniversity of Miami; University of Massachusetts, WorcesterNo longer available
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MeiraGTx, LLCNational Institute of Dental and Craniofacial Research (NIDCR)Active, not recruitingSquamous Cell Head and Neck Cancer | Radiation Induced Xerostomia | Salivary HypofunctionUnited States
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David WilliamsActive, not recruitingWiskott-Aldrich SyndromeUnited States
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Shanghai Belief-Delivery BioMed Co., LtdActive, not recruiting
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David WilliamsActive, not recruiting
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AVROBIOWithdrawn
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Adverum Biotechnologies, Inc.CompletedDiabetic Retinopathy | Diabetic Macular EdemaUnited States, Puerto Rico
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Adverum Biotechnologies, Inc.CompletedNeovascular Age-related Macular Degeneration | Wet Age-related Macular DegenerationUnited States
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Aveni FoundationWithdrawnCOVID-19 | Acute Respiratory Distress Syndrome | Cytokine Storm
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Nanoscope Therapeutics Inc.Enrolling by invitationRetinal Degeneration | Retinitis Pigmentosa | Retinal DiseaseIndia
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTerminatedMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Spain, Australia
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REGENXBIO Inc.National Heart, Lung, and Blood Institute (NHLBI)TerminatedHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Italy, Netherlands
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Brainvectis, a subsidiary of Asklepios BioPharmaceutical...Active, not recruitingHuntington DiseaseFrance
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Helixmith Co., Ltd.CompletedPainful Diabetic NeuropathiesUnited States, Korea, Republic of
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Johnson & Johnson Pharmaceutical Research & Development...Completed
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Asklepios Biopharmaceutical, Inc.Active, not recruiting
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CelgeneCompletedLymphoma, Large B-Cell, DiffuseUnited States, Australia, Belgium, Canada, China, Czechia, France, Ireland, Israel, Italy, Japan, Korea, Republic of, Netherlands, New Zealand, Portugal, Puerto Rico, Russian Federation, Spain, Switzerland, Taiwan, Turkey
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Applied Genetic Technologies CorpCompletedX-linked RetinoschisisUnited States
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Freeline TherapeuticsTerminatedLysosomal Storage Diseases | Fabry DiseaseUnited States, Norway, Germany, Austria, United Kingdom, Italy, Canada
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University of ReadingWild Blueberry Association of North America (WBANA)Completed
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AbbVieAbbVieEnrolling by invitationWet Macular Degeneration | Neovascular Age-related Macular DegenerationUnited States
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AbbVieAbbVieEnrolling by invitationGene Therapy | AMD | nAMD | Wet AMD | Neovascular Age-Related Macular Degeneration (nAMD) | wAMDUnited States
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REGENXBIO Inc.CompletedNeovascular Age-related Macular Degeneration | Wet Age-related Macular DegenerationUnited States
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland