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- Ensaio Clínico NCT07647510
A Phase 3 Study to Evaluate Claseprubart in Adults With Generalized Myasthenia Gravis (EMERGE)
28 de agosto de 2026 atualizado por: Dianthus Therapeutics
A Phase 3 Global, Multicenter, Randomized, Double-blind, Placebo-controlled Study to Demonstrate the Efficacy, Safety, and Tolerability of Claseprubart (DNTH103) in Patients With Generalized Myasthenia Gravis (EMERGE)
The purpose of this Phase 3 study is to demonstrate the efficacy, safety, and tolerability of claseprubart in participants with generalized myasthenia gravis (gMG).
Visão geral do estudo
Status
Recrutamento
Condições
Intervenção / Tratamento
Descrição detalhada
The study includes the following periods:
- Screening (up to 12 weeks)
- Randomized, blinded, controlled treatment (RCT) period (17 weeks)
- Extended treatment period (ETP) (104 weeks) (optional) for eligible participants [includes blinded extension period (BEP) and open-label extension (OLE) period]
- Safety Follow-Up period (40 weeks)
Tipo de estudo
Intervencional
Inscrição (Estimado)
195
Estágio
- Fase 3
Contactos e Locais
Esta seção fornece os detalhes de contato para aqueles que conduzem o estudo e informações sobre onde este estudo está sendo realizado.
Contato de estudo
- Nome: Dianthus Clinical Contact Center
- Número de telefone: 929-999-4055
- E-mail: clinicaltrials@dianthustx.com
Locais de estudo
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Florida
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Boca Raton, Florida, Estados Unidos, 33432
- Recrutamento
- Cinical Study Site
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North Carolina
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Fayetteville, North Carolina, Estados Unidos, 28304
- Ainda não está recrutando
- Cinical Study Site
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Texas
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Houston, Texas, Estados Unidos, 77009
- Recrutamento
- Cinical Study Site
-
-
Critérios de participação
Os pesquisadores procuram pessoas que se encaixem em uma determinada descrição, chamada de critérios de elegibilidade. Alguns exemplos desses critérios são a condição geral de saúde de uma pessoa ou tratamentos anteriores.
Critérios de elegibilidade
Idades elegíveis para estudo
- Adulto
- Adulto mais velho
Aceita Voluntários Saudáveis
Não
Descrição
Inclusion Criteria:
- Must have given written informed consent before any study-related activities are carried out
- Weight range between 40-130 kg at Screening
Diagnosis of gMG by the following tests:
- Acetylcholine receptor antibody (AChR Ab) positive, and
- One of the following:
i. History of abnormal neuromuscular transmission test; ii. History of positive anticholinesterase test; iii. Clinical response to acetylcholinesterase inhibitors.
- Myasthenia Gravis Foundation of America (MGFA) Class II-IVa
- MG-ADL scale score of 6 or more
- QMG scale score of 10 or more
- Documented vaccinations against encapsulated bacteria in accordance with local requirements and based on vaccine availability
- Female participants must be of non-childbearing potential, or if of childbearing potential, must agree not to donate ova, not to attempt to become pregnant and, if engaging in sexual intercourse with a male partner, must agree to use a highly effective method of contraception
- Male participants agree not to donate sperm and, if engaging in sexual intercourse with a female partner who could become pregnant, must agree to use an acceptable method of contraception
Exclusion Criteria:
- History or presence of significant medical/surgical condition including any acute illness, mental illness, or major surgery considered to be clinically significant or that could have potential impact on safety/efficacy or study procedures
- Known complement deficiency
- Prior history (at any time) of N. meningitidis infection
- Participants with known seropositivity or who test positive for an active viral infection with human immunodeficiency virus (HIV-1 or HIV-2), hepatitis B (HBV; except participants who are seropositive because of HBV vaccination) or hepatitis C virus (HCV) during Screening
- Previous treatment with claseprubart (DNTH103) or participation in a clinical trial with claseprubart. [
- Any thymic surgery/biopsy within 1 year of Screening
- Any known or untreated thymoma.
- Any history of thymic carcinoma or thymic malignancy
- History of active malignancy within 5 years prior to Screening, except basal cell carcinoma of the skin, curatively resected squamous cell carcinoma of the skin, cervical carcinoma in situ curatively treated or low-grade prostate adenocarcinoma for which appropriate management is observation alone
Concurrent or previous use of the following medication within the time periods specified below.
- Rituximab or other B-cell targeting therapies (ie, inebilizumab) within 6 months (180 days) prior to randomization (Day 1);
- Intravenous immunoglobulin (IVIg) and plasma exchange (PLEX) within 4 weeks (28 days) prior to randomization (Day 1)
- Participation in another clinical study of an investigational drug within 90 days or 5 half-lives of the investigational agent
- Diagnosis of systemic lupus erythematosus (SLE) or family history (defined as a parent, sibling, or child) of SLE
Plano de estudo
Esta seção fornece detalhes do plano de estudo, incluindo como o estudo é projetado e o que o estudo está medindo.
Como o estudo é projetado?
Detalhes do projeto
- Finalidade Principal: Tratamento
- Alocação: Randomizado
- Modelo Intervencional: Atribuição Paralela
- Mascaramento: Quadruplicar
Armas e Intervenções
Grupo de Participantes / Braço |
Intervenção / Tratamento |
|---|---|
|
Comparador de Placebo: Placebo
Intravenous (IV) infusion of Placebo on Day 1 followed by subcutaneous (SC) injections of Placebo every 2 weeks (Q2W) starting at Week 1 (Day 8).
|
IV infusion on Day 1
Prefilled syringe containing placebo for SC administration
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Experimental: Claseprubart Q2W
IV loading dose of claseprubart on Day 1 followed by SC injections of claseprubart Q2W starting at Week 1 (Day 8).
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IV loading dose on Day 1
Outros nomes:
Prefilled syringe containing claseprubart for SC administration
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Experimental: Claseprubart Every 4 weeks (Q4W)
IV loading dose of claseprubart on Day 1 followed by SC injections of claseprubart or Placebo Q2W starting at Week 1 (Day 8), with doses alternating between claseprubart and placebo.
|
Prefilled syringe containing placebo for SC administration
IV loading dose on Day 1
Outros nomes:
Prefilled syringe containing claseprubart for SC administration
|
O que o estudo está medindo?
Medidas de resultados primários
Medida de resultado |
Descrição da medida |
Prazo |
|---|---|---|
|
Change from Baseline to Week 17 in Myasthenia Gravis Activities of Daily Living (MG-ADL) Scale Score
Prazo: Baseline (Day 1) to Week 17
|
The MG-ADL score is an 8-item patient reported outcome (PRO) instrument.
The MG-ADL targets symptoms of disability across ocular, bulbar, respiratory, and axial symptoms.
The item responses are scored from 0 to 3, and the total score of the MG-ADL is the sum of the 8 items and ranges from 0 to 24, with a higher score indicating more disability.
|
Baseline (Day 1) to Week 17
|
Medidas de resultados secundários
Medida de resultado |
Descrição da medida |
Prazo |
|---|---|---|
|
Change from Baseline to Week 17 in Quantitative Myasthenia Gravis (QMG) Scale Score
Prazo: Baseline (Day 1) to Week 17
|
The QMG is a clinician-reported assessment to evaluate muscle strength.
The QMG consists of 13 items that measure endurance or fatiguability, with each item having a possible score that ranges from 0 - 3. The total possible QMG scores range from 0 - 39, with a higher score indicating greater disease burden.
|
Baseline (Day 1) to Week 17
|
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Change from Baseline to Week 17 in Myasthenia Gravis Composite (MGC) Scale Score
Prazo: Baseline (Day 1) to Week 17
|
The MGC is a validated assessment tool for measuring clinical status of participants with MG.
The range of total MGC score is 0 to 50, with higher scores indicating more severe disease.
A clinically meaningful improvement is reflected by a 3-point improvement in MGC score.
The MGC assesses 10 important functional areas most frequently affected by MG and the scales are weighted for clinical significance that incorporates patient-reported outcomes.
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Baseline (Day 1) to Week 17
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Proportion of Participants with Greater Than or Equal to (≥) a 5-point Reduction in MG-ADL Scale Score at Week 17 Compared to Baseline
Prazo: Baseline (Day 1) to Week 17
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Baseline (Day 1) to Week 17
|
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Proportion of Participants Who Reach Minimal Symptom Expression (MSE), Defined as MG-ADL 0 or 1 at Week 17, Without Use of Rescue Therapy
Prazo: Baseline (Day 1) to Week 17
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Baseline (Day 1) to Week 17
|
|
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Proportion of Participants with a ≥ 5-point Reduction in QMG Scale Score at Week 17 Compared to Baseline
Prazo: Baseline (Day 1) to Week 17
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Baseline (Day 1) to Week 17
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Incidence of Treatment-emergent Adverse Events (TEAEs) and Treatment-Emergent and Treatment-Emergent Serious Adverse Events (SAEs) in the RCT period, BEP, OLE, and Safety Follow-Up
Prazo: Baseline (Day 1) through Safety Follow-Up period (up to approximately 161 weeks)
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Number of participants with TEAEs and treatment-emergent SAEs will be reported.
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Baseline (Day 1) through Safety Follow-Up period (up to approximately 161 weeks)
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Serum Concentrations of Claseprubart
Prazo: Baseline (Day 1) through Safety Follow-Up period (up to approximately 161 weeks)
|
Blood samples will be collected for measurement of serum concentrations of claseprubart at various timepoints both pre- and post-dose.
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Baseline (Day 1) through Safety Follow-Up period (up to approximately 161 weeks)
|
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Change from Baseline in Complement Total Blood Test (CH50) in Serum ex vivo
Prazo: Baseline (Day 1) through Safety Follow-Up period (up to approximately 161 weeks)
|
Blood samples will be collected to determine changes in CH50 at various timepoints.
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Baseline (Day 1) through Safety Follow-Up period (up to approximately 161 weeks)
|
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Incidence of Antidrug Antibody (ADAs) Against Claseprubart in the RCT Period, BEP, OLE, and Safety Follow-Up
Prazo: Baseline (Day 1) through Safety Follow-Up period (up to approximately 161 weeks)
|
Blood samples will be collected to measure ADA against claseprubart at various timepoints.
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Baseline (Day 1) through Safety Follow-Up period (up to approximately 161 weeks)
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Titer of ADAs Against Claseprubart in the RCT Period, BEP, OLE, and Safety Follow-Up
Prazo: Baseline (Day 1) through Safety Follow-Up period (up to approximately 161 weeks)
|
Blood samples will be collected to measure ADA against claseprubart at various timepoints.
|
Baseline (Day 1) through Safety Follow-Up period (up to approximately 161 weeks)
|
Colaboradores e Investigadores
É aqui que você encontrará pessoas e organizações envolvidas com este estudo.
Patrocinador
Datas de registro do estudo
Essas datas acompanham o progresso do registro do estudo e os envios de resumo dos resultados para ClinicalTrials.gov. Os registros do estudo e os resultados relatados são revisados pela National Library of Medicine (NLM) para garantir que atendam aos padrões específicos de controle de qualidade antes de serem publicados no site público.
Datas Principais do Estudo
Início do estudo (Real)
29 de junho de 2026
Conclusão Primária (Estimado)
1 de dezembro de 2028
Conclusão do estudo (Estimado)
1 de setembro de 2031
Datas de inscrição no estudo
Enviado pela primeira vez
27 de maio de 2026
Enviado pela primeira vez que atendeu aos critérios de CQ
9 de junho de 2026
Primeira postagem (Real)
15 de junho de 2026
Atualizações de registro de estudo
Última Atualização Postada (Real)
1 de setembro de 2026
Última atualização enviada que atendeu aos critérios de controle de qualidade
28 de agosto de 2026
Última verificação
1 de junho de 2026
Mais Informações
Termos relacionados a este estudo
Termos MeSH relevantes adicionais
- Doenças do Sistema Nervoso
- Neoplasias por local
- Neoplasias
- Doenças Neuromusculares
- Doenças autoimunes
- Doenças do sistema imunológico
- Doenças Autoimunes do Sistema Nervoso
- Doenças Neurodegenerativas
- Síndromes Paraneoplásicas do Sistema Nervoso
- Neoplasias do Sistema Nervoso
- Síndromes Paraneoplásicas
- Doenças da Junção Neuromuscular
- Miastenia grave
Outros números de identificação do estudo
- DNTH103-MG-301
- 2026-525298-38-00 (Ctis)
Plano para dados de participantes individuais (IPD)
Planeja compartilhar dados de participantes individuais (IPD)?
NÃO
Informações sobre medicamentos e dispositivos, documentos de estudo
Estuda um medicamento regulamentado pela FDA dos EUA
Sim
Estuda um produto de dispositivo regulamentado pela FDA dos EUA
Não
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