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Clinical Trials on β -Thalassemia
Total 437 results
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Julia FinkelCompletedSCD With Severe Phenotype (HbSS, HbSβ0 Thalassemia, HbSOARab)United States
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Columbia UniversityCompletedMyelodysplastic Syndromes | Sickle Cell Disease | Aplastic Anemia | Transfusional Iron Overload | Thalassemia MajorUnited States
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Novartis PharmaceuticalsCompletedNon-transfusion Dependent ThalassemiaGreece, Taiwan, Italy, United Kingdom, Lebanon, Turkey, Malaysia, Thailand, United States
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Novartis PharmaceuticalsWithdrawnFocus on Transfusion Dependent Thalassemia Patients Who Are Inadequate Responders to Deferasirox > 35mg/kgQD
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University of Campania "Luigi Vanvitelli"CompletedIron Overload | Endocrine; Complications | Transfusion-dependent ThalassemiaItaly
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Assistance Publique - Hôpitaux de ParisCompletedMajor Sickle Cell Syndrome of Type SS or Sβ ThalassemiaFrance
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Imara, Inc.Quintiles, Inc.CompletedSickle Cell Disease | Sickle Beta 0 Thalassemia | Sickle-Cell; Hb-SCUnited States
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Mitchell CairoRecruitingHodgkin Lymphoma | Sickle Cell Disease | Acute Leukemia | Beta-Thalassemia | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Diamond Blackfan Anemia | Amegakaryocytic Thrombocytopenia | KostmannUnited States
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States
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New York Medical CollegeCompletedLymphoma | Leukemia | Sickle Cell Disease | Histiocytosis | Immunodeficiencies | Inborn Errors of Metabolism | Bone Marrow Failure | Beta ThalassemiaUnited States
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Novartis PharmaceuticalsCompletedThalassemia, Non-transfusional-dependent Thalassemia (NTDT), Myeloplastic Dysplasia (MDS), Other AnemiaAustralia
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Reproductive & Genetic Hospital of CITIC-XiangyaCompletedThalassemia,Embryonic Development,Reproductive Sterility and InfertilityChina
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Chinese University of Hong KongRecruitingHaemoglobin Barts HydropsHong Kong
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Shanghai First Maternity and Infant HospitalUnknown
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HaEmek Medical Center, IsraelWolfson Medical CenterCompletedMRI | Iron Overload | Sickle Cell Anemia | Sickle Cell ThalassemiaIsrael
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HaEmek Medical Center, IsraelCompletedSickle Cell Anemia | Sickle Cell ThalassemiaIsrael
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Obstetrix Medical GroupTerminatedFetal Growth Retardation | Hydrops FetalisUnited States
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Klein Buendel, Inc.National Institute on Minority Health and Health Disparities (NIMHD); Hilton...CompletedSickle Cell Disease | Sickle Cell Anemia in Children | Sickle Cell Thalassemia | Sickle Cell SC DiseaseUnited States
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Sidney Kimmel Cancer Center at Thomas Jefferson...National Heart, Lung, and Blood Institute (NHLBI)TerminatedSickle Cell Anemia | Sickle Cell-hemoglobin C Disease | Sickle Cell-β0-thalassemiaUnited States
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Ain Shams UniversityCompletedDiabetes | Prediabetes | B-Thalassemia
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Thomas Jefferson UniversityGlaxoSmithKline; Drexel UniversityUnknownQuality of Life | Inflammation | Sickle Cell Disease | HEMOGLOBIN SS | Hemoglobin S Beta-0 ThalassemiaUnited States
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University of California, San FranciscoEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationHydrops Fetalis | Birth Defect | Fetal AnomalyUnited States
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University of California, San FranciscoJohns Hopkins University; Eunice Kennedy Shriver National Institute of Child... and other collaboratorsEnrolling by invitation
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Thomas Jefferson UniversityRecruitingGenetic Disorders | Nonimmune Fetal Hydrops | Nonimmune Hydrops in NeonateUnited States
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Muğla Sıtkı Koçman UniversityCompletedPelvic Organ Prolapse | Urge Urinary Incontinence | SMAD2 | SMAD3 | TGF-βTurkey
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Bristol-Myers SquibbRecruitingAnemiaThailand, China, Canada, Turkey, Greece, Taiwan, Italy, Hong Kong
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CelgeneAcceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway...CompletedThalassemiaUnited States, Greece, Italy, Lebanon, Thailand, United Kingdom
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UCSF Benioff Children's Hospital OaklandChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsCompleted
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Ionis Pharmaceuticals, Inc.Completed
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedThalassemiaUnited States, Canada
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; Paris 12...Completed
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Hospices Civils de LyonRecruiting
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Fakultas Kedokteran Universitas IndonesiaNot yet recruiting
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Agios Pharmaceuticals, Inc.Active, not recruitingThalassemiaUnited States, Canada, United Kingdom
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Hangzhou Zede Pharma-Tech Co., Ltd.Completed
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Blood Diseases ClinicUniversity of PeshawarCompleted
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Hangzhou Zede Pharma-Tech Co., Ltd.Completed
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Guang'anmen Hospital of China Academy of Chinese...Completed
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Reem Ali ShakerRecruiting
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Menoufia UniversityCompleted
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Baylor College of MedicineTerminated
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The First Affiliated Hospital, Guangzhou University...Unknown
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Yanfang LiUnknown
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)Completed
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Novartis PharmaceuticalsCompleted
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Thalassemia Clinical Research...CompletedThalassemiaUnited States, Canada, United Kingdom
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Mersin UniversityCompleted
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The First Affiliated Hospital, Guangzhou University...National Natural Science Foundation of ChinaUnknownPregnancy | ThalassemiaChina