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Clinical Trials on AAT Deficiency
Total 34782 results
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingUndifferentiated Pleomorphic Sarcoma | Recurrent Undifferentiated Pleomorphic Sarcoma | Dedifferentiated Liposarcoma | Resectable Dedifferentiated Liposarcoma | Resectable Undifferentiated Pleomorphic Sarcoma | Recurrent Dedifferentiated LiposarcomaUnited States
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Washington University School of MedicineCompletedDoxorubicin With Upfront Dexrazoxane for the Treatment of Advanced or Metastatic Soft Tissue SarcomaSoft Tissue Sarcoma | Sarcoma, Soft Tissue | Leiomyosarcoma | Fibrosarcoma | Liposarcoma | Angiosarcoma | Malignant Peripheral Nerve Sheath Tumor | Synovial Sarcoma | Undifferentiated Pleomorphic Sarcoma | Epithelioid Sarcoma | MyxofibrosarcomaUnited States
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University Hospital, ToulouseActive, not recruitingCerebral Amyloid AngiopathyFrance
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Aldeyra Therapeutics, Inc.CompletedSjogren-Larsson SyndromeUnited States
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ActelionCompleted
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MacroGenicsCompletedOsteosarcoma | Ewing Sarcoma | Neuroblastoma | Rhabdomyosarcoma | Wilms Tumor | Desmoplastic Small Round Cell TumorUnited States
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Universitaire Ziekenhuizen KU LeuvenCompletedRegistry With Information About Colitis Ulcerosa and Familial Adenomatous Polyposis Patients (KOPOF)Adenomatous Polyposis Coli | Colitis,Ulcerative | Reservoir, IleoanalBelgium
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Sidney Kimmel Comprehensive Cancer Center at Johns...Massachusetts General Hospital; Washington University School of Medicine; Gla... and other collaboratorsCompletedNeurofibromatosis 2 | Vestibular Schwannoma | Acoustic Neuroma | NF2 | Auditory TumorUnited States
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Case Comprehensive Cancer CenterCompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative DiseasesUnited States
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Vtesse, LLC, a Mallinckrodt Pharmaceuticals CompanyWithdrawnNiemann-Pick Disease, Type C
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IpsenCompletedCerebral Palsy | Cervical Dystonia | Muscle Spasticity | Cerebrovascular Accident | Equinus Deformity | Hemifacial Spasm | Blepharospasm | Spasmodic Torticollis | Facial Hyperdynamic LinesFrance, Germany, Russian Federation
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University of South FloridaUniversity of Miami; National Institutes of Health (NIH); University of KansasCompletedAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | Hereditary Spastic Paraplegia
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The Cleveland ClinicNational Cancer Institute (NCI)CompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative Diseases | Psychosocial Effects of Cancer and Its TreatmentUnited States
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Masonic Cancer Center, University of MinnesotaTerminatedSarcoma | Kidney Cancer | Brain and Central Nervous System Tumors | Retinoblastoma | Liver CancerUnited States
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Ludwig-Maximilians - University of MunichUnknownIschemic Stroke | Cerebral Amyloid Angiopathy | Intracerebral HemorrhageGermany
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedRecurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities | Adult Acute Myeloid Leukemia With Del(5q) | Adult Acute Myeloid Leukemia With Inv(16)(p13;q22) | Adult Acute Myeloid Leukemia With t(16;16)(p13;q22) | Adult Acute Myeloid Leukemia With t(8... and other conditionsUnited States
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National Institute of Arthritis and Musculoskeletal...WithdrawnBehcet's Disease | Muckle Wells Syndrome | AutoinflammatoryUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHeart Failure | Coronary Disease | Pulmonary Hypertension | Peripheral Artery Disease | Dilated Cardiomyopathy | Renal Artery Stenosis | Diabetes and Heart FailureUnited States
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DePuy InternationalWithdrawnOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Traumatic Femoral Fractures | Nonunion of Femoral Fractures
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DePuy InternationalTerminatedOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Traumatic Femoral Fractures | Nonunion of Femoral FracturesUnited Kingdom
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Massachusetts General HospitalCompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Multiple Myeloma and Plasma Cell Neoplasm | Graft Versus Host Disease | Myelodysplastic/Myeloproliferative NeoplasmsUnited States
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National Cancer Institute (NCI)CompletedMyelodysplastic Syndrome (MDS) | Non-Hodgkin's Lymphoma (NHL) | Leukemia, Acute Myelogenous (AML) | Leukemia, Acute Lymphocytic (ALL) | Leukemia, Chronic Myelogenous (CML)United States
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Vanderbilt-Ingram Cancer CenterNational Cancer Institute (NCI)CompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Multiple Myeloma and Plasma Cell Neoplasm | Graft Versus Host Disease | Myelodysplastic/Myeloproliferative NeoplasmsUnited States
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NYU Langone HealthBayer Healthcare Pharmaceuticals, Inc./Bayer Schering PharmaTerminatedneurofibromatosis1 (NF1) | Recurrent or Progressive Optic Pathway Gliomas (OPG) | Recurrent or Progressive Low-grade GliomaUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedAdult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities | Adult Acute Myeloid Leukemia With Del(5q) | Secondary Acute Myeloid Leukemia | Untreated Adult Acute Myeloid Leukemia | Previously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | Adult Acute Myeloid Leukemia... and other conditionsUnited States
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Université de SherbrookeUnknownPathologic Processes | Respiratory Tract Infections | Respiratory Tract Diseases | Pneumonia | Hemorrhage | Bronchiectasis | Mycobacterium Infections | Signs and Symptoms, Respiratory | Lung Cancer | Tuberculosis | Lung Disease | Bronchitis | Pulmonary Embolism | Arteriovenous Fistula | Signs and Symptoms | Pulmonary Hemorrhage and other conditionsCanada
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University College, LondonUnknownHypopituitarism | Primary Ovarian Insufficiency | Turner's Syndrome | Hypogonadotrophic Hypogonadism | Primary Amenorrhoea | Hypothalamic AmenorrhoeaUnited Kingdom
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University of AarhusUnknownHypertension | Ischemic Heart Disease | Aortic Aneurysm | Turner Syndrome | Congenital Heart DefectDenmark
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Skulpt, Inc.CompletedMultiple Sclerosis | Charcot-Marie-Tooth Disease | Motor Neuron Disease | Amyotrophic Lateral SclerosisUnited States
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FDA Office of Orphan Products DevelopmentCochlearCompleted
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Ain Shams UniversityUnknownMuscular Dystrophy | Polyneuropathies | Spinal Muscular Atrophy | Muscle Diseases | Myasthenic SyndromesEgypt
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Sidney Kimmel Comprehensive Cancer Center at Johns...National Cancer Institute (NCI)CompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative Diseases | Graft Versus Host DiseaseUnited States
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University Health Network, TorontoCompletedEffects of Photographic Aids (Photos of Faces) on Patient Recall of Their Clinical Care Team | Effects of Photographic Aids (Photos of Faces) on Clinician-patient Communication | Effects of Photographic Aids (Photos of Faces) on Overall Patient SatisfactionCanada
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Memorial Sloan Kettering Cancer CenterCompleted
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National Cancer Institute (NCI)CompletedSarcoma | Lymphoma | Kidney Cancer | Leukemia | Neutropenia | Neuroblastoma | Infection | Fever, Sweats, and Hot FlashesUnited States
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Zhongshan Bo Ai HospitalCompletedThe Investigators Collected 534 PCOS Patients as the Case Group,and 580 Infertile Women With Normal Ovulatory Cycle of the Control Group; | At the Same Time, the Investigators Continuedly Collect Cases to October 2012, and Totally Collected 579 Patients With PCOS Altogether; | 534... and other conditionsChina
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)TerminatedSarcoma | Lymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative Diseases | Graft Versus Host DiseaseUnited States
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Case Comprehensive Cancer CenterNational Cancer Institute (NCI)CompletedPain | Lymphoma | Leukemia | Fatigue | Small Intestine Cancer | Cancer Survivor | Anxiety Disorder | Psychosocial Effects of Cancer and Its Treatment | Lymphoproliferative Disorder | Long-term Effects Secondary to Cancer Therapy in AdultsUnited States
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University of Medicine and Dentistry of New JerseyNational Cancer Institute (NCI)TerminatedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative Diseases | Precancerous/Nonmalignant ConditionUnited States
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St. Jude Children's Research HospitalUniversity of MiamiCompletedNeuroblastoma | Central Nervous System Tumors | Wilms Tumor | LymphomasUnited States
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House Ear InstituteUnknownMeningioma | Neurofibromatosis 2 | Schwannoma, VestibularUnited States
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University of AarhusRecruitingFertility Disorders | Turner Syndrome | Premature Ovarian FailureDenmark
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St. Jude Children's Research HospitalWallace H. Coulter FoundationRecruitingIdentifying the Determinants of Bleeding and Hypermobility in Patients With Heavy Menstrual BleedingHypermobile Ehlers-Danlos Syndrome | Heavy Menstrual Bleeding | Hypermobility Syndrome (Disorder)United States
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Australian and New Zealand Intensive Care Research...The AlfredNot yet recruitingPneumonia | Extracorporeal Membrane Oxygenation | Mechanical Ventilation Complication | Hypoxemia | COVID-19 Respiratory Infection | Acute Respiratory Distress Syndrome Due to COVID-19Australia, Germany
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Chinese University of Hong KongHong Kong Children's Hospital; Hong Kong Young Women's Christian AssociationRecruitingGastrointestinal Diseases | Vascular Diseases | Urologic Diseases | Neurodevelopmental Disorders | Autism Spectrum Disorder | Cleft Lip and Palate | Attention Deficit Hyperactivity Disorder | Developmental DelayHong Kong
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Novo Nordisk A/SRecruitingSGA, Turner Syndrome, Noonan Syndrome, ISSKorea, Republic of, United States, Ireland, United Kingdom, Finland, France, Netherlands, Japan, Thailand, Belgium, China, Israel, Brazil, India, Portugal, Austria, Bulgaria, Canada, Croatia, Germany, Greece, Malaysia, Poland, Saudi Arabia and more
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Medical College of WisconsinUniversity College, London; Indiana UniversityRecruitingFunctional Gastrointestinal Disorders | Postural Orthostatic Tachycardia Syndrome | Hypermobile Ehlers-Danlos Syndrome | Autonomic Nervous System Disease | Autonomic Nervous System ImbalanceUnited States
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National Research Centre, EgyptEgyptian Military Medical ServicesNot yet recruitingCOVID-19 | Coronavirus Infection | SARS-CoV 2 | Acute Respiratory Distress Syndrome | Corona Virus Infection | Middle East Respiratory Syndrome (MERS)Egypt
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RWTH Aachen UniversityDLR German Aerospace CenterRecruitingPostural Tachycardia Syndrome | Autonomic Neuropathy | Small Fiber Neuropathy | Ehlers-Danlos Syndrome Hypermobility TypeGermany
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Johns Hopkins All Children's HospitalRecruitingPremature Birth | Chronic Lung Disease of Prematurity | Feeding; Difficult, Newborn | Feeding Disorder Neonatal | BPD - Bronchopulmonary Dysplasia | VLBW - Very Low Birth Weight InfantUnited States