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Clinical Trials on ADA-SCID in Austria
Total 57 results
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Green BeatMedical University of GrazCompletedInflammation | Oxidative Stress | AcidosisAustria
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Medical University of ViennaCompletedMetabolic Acidosis | Hyperkalaemia Requiring Postoperative DialysisAustria
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Medical University of GrazCompletedHealthy | Oxidative Stress | Vitamin B 12 Deficiency | Polyphenols | Thiamine and Niacin Deficiency States | Pyridoxine Deficiency | Folic Acid Deficiency Anemia, Dietary | Peroxidase; Defect | Homocystine; Metabolic DisorderAustria
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Medical University of ViennaCompletedHeart Failure | Acidosis, Lactic | Thiamine DeficiencyAustria
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Medtronic CardiovascularTerminatedAbdominal Aortic Aneurysm | AAANetherlands, Belgium, Denmark, Sweden, Austria
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Paracelsus Medical UniversityCompletedCardiovascular Risk Factor | SCI - Spinal Cord InjuryAustria
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Medical University of ViennaCompletedObesity, Morbid | Bariatric Surgery Candidate | Vitamin B 12 Deficiency | Folate Deficiency | Homocystine; Metabolic DisorderAustria
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Aplos MedicalNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National...Recruiting
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Vascutek Ltd.TerminatedAbdominal Aortic Aneurysms (AAA)United Kingdom, Netherlands, Switzerland, Spain, Germany, Belgium, Sweden, Canada, France, Italy, Austria, Monaco
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Australian and New Zealand Intensive Care Research...RecruitingShock | Metabolic AcidosisAustralia
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St Vincent's Hospital MelbourneCompletedDiabetes Mellitus | KetoacidosisAustralia
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Reneo Pharma LtdCompletedFatty Acid Oxidation DisorderUnited States, Spain, France, Austria, Poland, Belgium, Czechia, Denmark, Hungary, Italy, United Kingdom
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CoA Therapeutics, Inc., a BridgeBio companyTerminatedHealthy Volunteers | Propionic Acidemia | Methylmalonic Acidemia | Organic AcidemiaUnited States
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Medical University of ViennaCompletedHyperemesis Gravidarum | Nausea Gravidarum | Vitamin C DeficiencyAustria
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KoBioLabsNovotech (Australia) Pty LimitedCompletedAtopic Dermatitis (AD)Australia
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Nectero Medical, Inc.Active, not recruitingAbdominal Aortic Aneurysm | AAA | Dilation AortaNew Zealand, Australia, China, Colombia
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Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan
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NestléCompletedPhenylketonuriaAustralia, Germany
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Medtronic Cardiac Rhythm and Heart FailureCompletedClass I or II Indication for Implantation of a Single Chamber Ventricular Pacemaker According to ACC/AHA/HRS 2001 Guidelines and Any National GuidelinesUnited States, Netherlands, Japan, Serbia, Spain, Greece, Canada, India, Denmark, Czechia, South Africa, Malaysia, Austria, United Kingdom, Hungary, China, Australia, France, Italy
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The George InstituteNot yet recruitingDiabetic KetoacidosisAustralia
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ModernaTX, Inc.RecruitingPhenylketonuriaUnited States, Australia
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Medtronic CardiovascularRecruitingAAA - Abdominal Aortic AneurysmSpain, Germany, Portugal, Switzerland, Austria, France, Greece, Ireland, Italy, Netherlands, Russian Federation, Slovakia, Sweden, United Kingdom
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Medtronic CardiovascularTerminated
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ModernaTX, Inc.RecruitingMethylmalonic AcidemiaUnited States, Spain, Canada, Netherlands, France, Australia, United Kingdom
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SangartCompletedShock, Hemorrhagic | Acidosis, Lactic | Shock, TraumaticNorway, Singapore, Israel, France, United Kingdom, Germany, Switzerland, Australia, Brazil, South Africa, New Zealand, Colombia, Austria, Spain
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Bayside HealthNational Health and Medical Research Council, Australia; Monash University; Cystic...UnknownCystic FibrosisAustralia
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HemoShear TherapeuticsTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Saudi Arabia, Australia
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Atridia Pty Ltd.Not yet recruitingAlzheimer's Disease (AD)Australia
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US BionicsCompleted
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Ultragenyx Pharmaceutical IncCompletedOrnithine Transcarbamylase DeficiencyUnited States
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UCB Biopharma SRLRecruitingMyelin Oligodendrocyte Glycoprotein Antibody-associated Disease (MOG-AD)United States, Australia, Belgium, Czechia, France, Germany, Italy, Japan, Korea, Republic of, Mexico, Spain, Sweden, Switzerland, Turkey, Portugal, United Kingdom, Brazil, Ukraine, Taiwan
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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Jnana TherapeuticsRecruitingPhenylketonuriaUnited States, Australia
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BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Turkey, United Kingdom, Germany, Netherlands, Slovakia, Austria, Belgium, Czechia
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SanofiCompletedHyponatremia | Inappropriate ADH SyndromeUnited States, France, Brazil, Russian Federation, Australia, Germany, Switzerland, Belgium, Hungary, Hong Kong, Canada
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Aeglea BiotherapeuticsTerminatedHomocystinuria Due to Cystathionine Beta-Synthase DeficiencyUnited States, United Kingdom, Australia
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Foregut Research FoundationRecruitingHiatal Hernia Large | Gastro Esophageal Reflux | Hiatal Hernia | Hiatal Hernia, Paraesophageal | Reflux, Gastroesophageal | Reflux AcidUnited States
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SangartWithdrawnTrauma | Hemorrhagic Shock | Lactic AcidosisNew Zealand, United Kingdom, Israel, France, Switzerland, Australia, Belgium, Brazil, Germany, Norway, South Africa
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Spain, Netherlands, France, United Kingdom, Australia, Canada, Italy
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AbbVieRecruitingSpinal Cord Injury (SCI)United States, Australia, Canada, Israel, Japan, Spain, Korea, Republic of
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AbbVieRecruitingAlzheimer's Disease (AD)United States, Japan, New Zealand, Australia, Spain, Germany, United Kingdom
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States, Germany, Spain, Australia, Brazil, United Kingdom, Denmark, Mexico, Portugal, Turkey, Canada, Georgia, Italy, Netherlands, Japan
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant Hypocalcemia (ADH)United States, Australia, United Kingdom, Denmark, Italy, France, Japan, Taiwan, Canada, Czechia, Netherlands
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencySpain, Germany, Italy, United States, Croatia, Canada, Russian Federation, Denmark, United Kingdom, Belgium, Mexico, Australia, Netherlands, Brazil, Turkey
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PTC TherapeuticsCompletedPhenylketonuriaSpain, United States, Australia, Germany, United Kingdom, Brazil, Denmark, Canada, France, Georgia, Italy, Mexico, Netherlands, Portugal, Turkey
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Austria, Czechia, Finland, Hungary, Ireland, Italy, Netherlands, Norway, Poland, Portugal, Spain, Sweden, United Kingdom
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencyFrance, Poland, United Kingdom, Spain, Mexico, Turkey, Japan, Australia, Russian Federation, United States, Germany, Italy, Czechia, Argentina, Croatia
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Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Australia, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
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BioMarin PharmaceuticalCompletedHyperphenylalaninemia (HPA) Due to Phenylketonuria (PKU) or Tetrahydrobiopterin (BH4) DeficiencySweden, France, Italy, Spain, Germany, Netherlands, Austria, Slovakia, Portugal