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Clinical Trials on ADA-SCID in Netherlands
Total 63 results
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Academisch Medisch Centrum - Universiteit van Amsterdam...Recruiting
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FrieslandCampinaWageningen University and ResearchCompletedAmino Acid Plasma ProfileNetherlands
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Rijnstate HospitalCompletedAAA | Iliac Aneurysm | AngiographyNetherlands
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Nutricia ResearchRecruitingPostprandial Amino Acid Concentrations in Healthy AdultsNetherlands
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Academisch Medisch Centrum - Universiteit van Amsterdam...Stichting StofwisselkrachtNot yet recruitingLong-chain Fatty Acid Oxidation Disorders \(LC-FAOD\)Netherlands
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Boston Scientific CorporationCompletedACC/AHA/NASPE Class 1, IIa or IIb IndicationsNetherlands, Italy, United Kingdom, New Zealand
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Amphia HospitalCompletedBlood Loss | Cardiac Surgery | Tranexamic AcidNetherlands
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Medtronic CardiovascularTerminatedAbdominal Aortic Aneurysm | AAANetherlands, Belgium, Denmark, Sweden, Austria
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Rijnstate HospitalKarolinska Institutet; University Medical Center Groningen; Amsterdam UMC, location... and other collaboratorsRecruitingAAA - Abdominal Aortic AneurysmNetherlands, Sweden
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Radboud University Medical CenterStichting Bevordering Tandheelkundige Kennis of the Nederlands Tijdschrift...CompletedReflux Acid | Bruxism | Tooth WearNetherlands
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Radboud University Medical CenterMerck Sharp & Dohme LLCCompletedHCV Infections | Gastric Acid-related DisordersNetherlands
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Marc van SambeekActive, not recruitingAbdominal Aortic Aneurysm (AAA)Netherlands, Italy, United Kingdom, Spain, France
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Amphia HospitalCompletedDelirium | Surgery | Surgery--Complications | Aortic Aneurysm, Abdominal | AAA | Intensive Care Unit DeliriumNetherlands
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Erasmus Medical CenterCompletedChronic Kidney DiseaseNetherlands
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Novartis PharmaceuticalsTerminatedAbdominal Aortic Aneurysm (AAA)Denmark, United States, Netherlands, Sweden, United Kingdom
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Vascutek Ltd.TerminatedAbdominal Aortic Aneurysms (AAA)United Kingdom, Netherlands, Switzerland, Spain, Germany, Belgium, Sweden, Canada, France, Italy, Austria, Monaco
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Maasstad HospitalRed Cross Hospital Beverwijk; Association of Dutch Burn Centres; Martini Hospital...RecruitingBurns | Blood Loss | Blood Loss, Surgical | Tranexamic Acid | Burn Excisional SurgeryNetherlands
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Radboud University Medical CenterCompletedEpilepsy | Ketogenic Dieting | Lactic Acid Blood Increased | GLUT1DS1 | GLUT1 Deficiency Syndrome | GLUT1DS2Netherlands
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Academisch Medisch Centrum - Universiteit van Amsterdam...CompletedDiabetes Mellitus | Ketosis | Ketoses, Metabolic | Keto Acidosis | Ketosis, Diabetic | Peri-operativeNetherlands
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Netherlands Institute for Pigment DisordersAvita MedicalCompletedPiebaldism | Segmental VitiligoNetherlands
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Academisch Medisch Centrum - Universiteit van Amsterdam...UnknownPiebaldism | Segmental VitiligoNetherlands
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Radboud University Medical CenterCompletedMild HyperhomocysteinemiaNetherlands
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University Medical Center GroningenUMC Utrecht; University of Oxford; Academisch Medisch Centrum - Universiteit... and other collaboratorsCompletedVLCAD Deficiency | Fatty Acid Oxidation DefectsNetherlands
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Nutricia ResearchCompletedPhenylketonuriasGermany, Netherlands
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Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan
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Academisch Medisch Centrum - Universiteit van Amsterdam...UnknownPiebaldism | Segmental Vitiligo | Non-segmental VitiligoNetherlands
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Erasmus Medical CenterEnrolling by invitationCKD | Electrolyte and Fluid Balance Conditions | Metabolic AcidosisNetherlands
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ModernaTX, Inc.RecruitingMethylmalonic AcidemiaUnited States, Spain, Canada, Netherlands, France, Australia, United Kingdom
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2Netherlands
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Medtronic CardiovascularRecruitingAAA - Abdominal Aortic AneurysmSpain, Germany, Portugal, Switzerland, Austria, France, Greece, Ireland, Italy, Netherlands, Russian Federation, Slovakia, Sweden, United Kingdom
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EndologixCompletedAbdominal Aortic Aneurysm (AAA)United States, United Kingdom, Germany, Netherlands
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Prof. Tobias FeuchtingerEuropean Commission; Simbec-Orion Group Ltd, Merthyr Tydfil, UK; Miltenyi Biotec... and other collaboratorsRecruitingCMV Infection | EBV Infection | Stem Cell Transplant Complications | AdV InfectionBelgium, Spain, France, Germany, Italy, Netherlands
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Medtronic Cardiac Rhythm and Heart FailureCompletedClass I or II Indication for Implantation of a Single Chamber Ventricular Pacemaker According to ACC/AHA/HRS 2001 Guidelines and Any National GuidelinesUnited States, Netherlands, Japan, Serbia, Spain, Greece, Canada, India, Denmark, Czechia, South Africa, Malaysia, Austria, United Kingdom, Hungary, China, Australia, France, Italy
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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C.T. Development America, Inc.CompletedAmyloidosisSpain, United States, Italy, Belgium, Netherlands, India, Tunisia, Latvia, Turkey, France, Germany, Estonia, Lithuania, Poland, Russian Federation, Georgia, United Kingdom, Israel, Egypt, Finland, Peru, Sweden, Ukraine
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Maastricht University Medical CenterRecruitingQuality of Life | Tuberous Sclerosis | Basal Cell Nevus Syndrome | Cutis Laxa | Epidermolysis Bullosa | Ichthyosis | Ectodermal Dysplasia | Albinism | Birt-Hogg-Dube Syndrome | Palmoplantar KeratosesNetherlands
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Maastricht University Medical CenterEnrolling by invitationTuberous Sclerosis | Basal Cell Nevus Syndrome | Cutis Laxa | Epidermolysis Bullosa | Ichthyosis | Ectodermal Dysplasia | Albinism | Xeroderma Pigmentosum | Birt-Hogg-Dube Syndrome | Palmoplantar KeratosesNetherlands
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SanofiCompletedHyponatremia | Inappropriate ADH SyndromeUnited States, Canada, Brazil, Germany, Netherlands, Portugal, Spain, Belgium, Croatia, Hungary, Hong Kong
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LMU KlinikumSeventh Framework Programme; NBIA AllianceRecruitingNeurodegeneration With Brain Iron Accumulation (NBIA) | Pantothenate Kinase-associated Neurodegeneration (PKAN) | Aceruloplasminemia | Beta-Propeller Protein-Associated Neurodegeneration (BPAN) | Mitochondrial Membrane Protein Associated Neurodegeneration (MPAN) | Fatty Acid Hydroxylase-associated... and other conditionsCanada, Czechia, Germany, Italy, Netherlands, Poland, Serbia, Spain
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Vivoryon Therapeutics N.V.Amsterdam UMC, location VUmc; Nordic Bioscience A/SCompletedEarly Alzheimers Disease | Mild Cognitive Impairment Due to ADNetherlands, Spain, Denmark, Germany, Poland
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BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Turkey, United Kingdom, Germany, Netherlands, Slovakia, Austria, Belgium, Czechia
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Spain, Netherlands, France, United Kingdom, Australia, Canada, Italy
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EndoStim Inc.TerminatedGastroesophageal Reflux | Reflux, Gastroesophageal | Gastroesophageal Reflux Disease (GERD) | Acid RefluxUnited States, Belgium, Netherlands, United Kingdom
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency | Isolated Sulfite Oxidase DeficiencySpain, Israel, United States, United Kingdom, Canada, Netherlands, Germany, Saudi Arabia, Tunisia, Japan, Italy, Malaysia, Poland, Turkey
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencySpain, Germany, Italy, United States, Croatia, Canada, Russian Federation, Denmark, United Kingdom, Belgium, Mexico, Australia, Netherlands, Brazil, Turkey
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Khondrion BVJulius Clinical; ProPharma Group; CertaraCompletedMitochondrial Diseases | Mitochondrial DNA tRNALeu(UUR) m.3243A<G Mutation | Maternally Inherited Diabetes and Deafness (MIDD) | Mitochondrial Encephalomyopathy, Lactic Acidosis and Stroke Like Episodes (MELAS) | Chronic Progressive External Ophthalmoplegia (CPEO)Netherlands, Denmark, United Kingdom, Germany
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant Hypocalcemia (ADH)United States, Australia, United Kingdom, Denmark, Italy, France, Japan, Taiwan, Canada, Czechia, Netherlands
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2United States, France, Netherlands
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Genzyme, a Sanofi CompanyCompletedPompe Disease | Glycogen Storage Disease Type II (GSD II) | Acid Maltase DeficiencyUnited States, Belgium, Denmark, France, Germany, Netherlands, United Kingdom
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Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Australia, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil