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Clinical Trials on ALA Dehydratase Deficient Porphyria (ADP)
Total 11513 results
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Centre for the AIDS Programme of Research in South...Johns Hopkins University; National Institute of Allergy and Infectious Diseases... and other collaboratorsActive, not recruitingHIV/AIDS | Tuberculosis, PulmonarySouth Africa
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Children's Hospital Medical Center, CincinnatiFood and Drug Administration (FDA)Completed
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National Cancer Institute (NCI)CompletedMelanoma | Skin Cancer | Basal Cell Carcinoma | Squamous Cell Carcinoma | Xeroderma PigmentosumUnited States
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Leiden University Medical CenterTerminatedPituitary Adenoma | Pituitary Tumor | Diabetes Insipidus Cranial Type | Endocrine; DeficiencyNetherlands
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NYU Langone HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedCystinuria | Primary Hyperoxaluria | Dent Disease | Adenine Phosphoribosyl Transferase DeficiencyUnited States, Iceland
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University of Southern DenmarkOdense University Hospital; University of Ghana; Odense Patient Data Explorative... and other collaboratorsCompletedAcquired Immunodeficiency Syndrome | Tuberculosis, Pulmonary | Human Immunodeficiency Virus (HIV) | Extrapulmonary TuberculosisGhana
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National Institute of Allergy and Infectious Diseases...CompletedHIV Infections | Mycobacterium Avium-intracellulare InfectionUnited States
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National Institute of Allergy and Infectious Diseases...CompletedHIV Infections | Mycobacterium Avium-intracellulare InfectionUnited States
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RWJ Barnabas Health at Jersey City Medical CenterUnknownLynch Syndrome | Endometrial Cancer | Somatic Mutation | Cancer Gene MutationUnited States
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Assistance Publique - Hôpitaux de ParisCompleted
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JULIANY DE SOUZA ARAUJOCompletedLipodystrophy | HIV/AIDS and Infections | Disorder Sleep
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University of Colorado, DenverColorado Clinical & Translational Sciences InstituteCompletedRheumatologic Disorder | Dialysis | Human Immunodeficiency Virus (HIV) | Solid Organ Transplant Recipient (Liver, Kidney, Heart) | Bone Marrow Transplant (BMT)United States
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Unspecified Adult Solid Tumor, Protocol Specific | Fanconi AnemiaUnited States
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Hospital Universitari Vall d'Hebron Research InstituteUniversidad de MurciaUnknownCongenital Heart Diseases | Antithrombin III Deficiency | Congenital Disorder of Glycosylation | Conotruncal DefectsSpain
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Acquired Bleeding Disorder | Acquired Haemophilia | Congenital FVII Deficiency | Glanzmann's DiseaseFrance
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Maimónides Biomedical Research Institute of CórdobaUnknownChronic Hepatitis C | Human Immunodeficiency Virus (HIV)
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University Hospital Schleswig-HolsteinWithdrawnDisorders of Sex Development | Congenital Adrenal Hyperplasia | Adrenal Insufficiency | Congenital Adrenal Hypoplasia | Mineralocorticoid Deficiency | Intersex
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Chiltern Pesquisa Clinica LtdaCompletedH1N1 Influenza Virus | Human Immunodeficiency Virus Type 1 (HIV-1) InfectionBrazil
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Bio Products LaboratoryCompletedPrimary Immunodeficiency | Wiskott-Aldrich Syndrome | Hypogammaglobulinemia | Common Variable Hypogammaglobulinemia | X-linked Hypogammaglobulinemia | Immunodeficiency With Hyper-IgMUnited States
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ViiV HealthcarePfizerWithdrawnHepatitis B | Hepatitis C, Chronic | Human Immunodeficiency VirusUnited States, Canada, Poland
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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National Institute of Allergy and Infectious Diseases...CompletedHIV Infections | Chronic Hepatitis BUnited States
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I.M. Sechenov First Moscow State Medical UniversityRecruitingCOVID-19 | Quality of Life | Hypertension | Arrhythmia | Chronic Heart Failure | Endothelial Dysfunction | Conduct Disorder | Oxygen Consumption | Diastolic Dysfunction | Chronic Coronary Syndrome | Exercise ToleranceRussian Federation
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Children's Hospital of PhiladelphiaEli Lilly and Company; University of Pennsylvania; Takeda; National Institute of... and other collaboratorsRecruitingMucopolysaccharidoses | Leukoencephalopathies | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2... and other conditionsUnited States
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Fondation LenvalActive, not recruitingCOVID-19 | Psychiatric Disorder | Eating Disorders in AdolescenceFrance
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Leigh R. Hochberg, MD, PhD.National Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Tetraplegia | Dysarthria | Brain Stem Infarctions | Locked in Syndrome | AnarthriaUnited States
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Mayo ClinicEnrolling by invitationParkinson Disease | Semantic Dementia | Behavioral Variant of Frontotemporal Dementia | CBD | Apraxia of Speech | MSA - Multiple System Atrophy | FTD | PPA | PSP | PCA | LPA | Semantic AphasiaUnited States
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IntraBio IncCompletedNiemann-Pick Disease, Type CUnited States, United Kingdom, Germany, Slovakia, Spain
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Eunice Kennedy Shriver National Institute of Child...TerminatedNiemann-Pick Disease, Type C1United States
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Cyclo Therapeutics, Inc.CompletedNiemann-Pick Disease, Type C1Israel, Sweden, United Kingdom
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Vtesse, LLC, a Mallinckrodt Pharmaceuticals CompanyCompletedNiemann-Pick Disease, Type C1United States
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Cyclo Therapeutics, Inc.Active, not recruitingNiemann-Pick Disease, Type C1United States
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CENTOGENE GmbH RostockCompleted
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University Health Network, TorontoUnknownProgressive Supranuclear Palsy | Semantic Dementia | Corticobasal Syndrome | Progressive Nonfluent Aphasia | Behavioral Variant Frontotemporal Dementia | Amyotrophic Lateral Sclerosis and/or Frontotemporal DementiaCanada
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KemPharm Denmark A/SCompletedNiemann-Pick Disease, Type CSpain, France, United Kingdom, Switzerland, Denmark, Poland, Italy, Germany
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ExonhitCompletedMild Cognitive Impairment | Primary Progressive Aphasia | Vascular Dementia | Alzheimer's Disease | Mixed Dementia | Fronto-temporal Dementia | Parkinson' Disease DementiaUnited States
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Children's Hospital of PhiladelphiaIllumina, Inc.Active, not recruitingMucopolysaccharidoses | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2 Gangliosidosis | Zellweger... and other conditionsUnited States
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Kangbuk Samsung HospitalHanyang University; Kyunghee University Medical CenterNot yet recruitingChronic Hepatitis b | Human Immunodeficiency Virus | Gut Microbiome
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Stellah MpagamaRadboud University Medical Center; University of St AndrewsRecruitingTuberculosis | Human Immunodeficiency VirusTanzania
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University of CopenhagenHvidovre University HospitalRecruitingColorectal Cancer | Lynch Syndrome | Familial Adenomatous Polyposis | Hereditary Non-polyposis Colon CancerDenmark
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Dong-A ST Co., Ltd.RecruitingGrowth Hormone Deficiency | Turner Syndrome | Small for Gestational Age | Idiopathic Short StatureKorea, Republic of
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National Cancer Institute (NCI)RecruitingAcute Adult T-Cell Leukemia/Lymphoma | Adult T-Cell Leukemia/Lymphoma | Chronic Adult T-Cell Leukemia/Lymphoma | HTLV-1 InfectionUnited States
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Udai KammulaRecruitingSarcoma | Gastric Cancer | Colorectal Cancer | Pancreatic Cancer | Neuroendocrine Tumors | Mesothelioma | Merkel Cell Carcinoma | Microsatellite Instability | Squamous Cell Cancer | Mismatch Repair DeficiencyUnited States
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Mayo ClinicRecruitingCystinuria | Primary Hyperoxaluria | Dent Disease | APRT DeficiencyUnited States
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Vanderbilt University Medical CenterNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Brigham... and other collaboratorsSuspendedKidney Diseases | HIV/AIDS | Albuminuria | Genetic PredispositionNigeria
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Memorial Sloan Kettering Cancer CenterHarvard University; Broad InstituteActive, not recruitingLynch Syndrome | Hereditary Colonic Polyposis SyndromesUnited States
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Hospitales Universitarios Virgen del RocíoInstituto de Biomedicina de SevillaEnrolling by invitationHepatitis, Viral, Human | HIV Infection Primary | Sexually Transmitted Infections, Excluding HIV and HepatitisSpain
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CENTOGENE GmbH RostockWithdrawnSplenomegaly | Hepatomegaly | Ceramidase Deficiency | Farber's LipogranulomatosisGermany, India, Egypt
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SanofiApproved for marketing