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Clinical Trials on Albright Hereditary Osteodystrophy
Total 2672 results
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, Spain, United Kingdom
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Huazhong University of Science and TechnologyShiyan Taihe HospitalActive, not recruitingLeber Hereditary Optic NeuropathyChina
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyFrance
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Santhera PharmaceuticalsEuropean Vision Institute Clinical Research NetworkCompletedLeber Hereditary Optic Neuropathy (LHON)Belgium, France, Denmark, Italy, Slovenia
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Seoul National University HospitalCompletedEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Eye Disease, HereditaryKorea, Republic of
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EuroBloodNet AssociationNot yet recruitingHereditary Red Blood Cell Disorder (Disorder)Denmark, Netherlands
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Applied Therapeutics, Inc.Active, not recruitingHereditary Neuropathy Caused by SORD DeficiencyUnited States, United Kingdom, Czechia, Italy
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Neurophth Therapeutics IncRecruitingLeber Hereditary Optic Neuropathy (LHON)China, United States
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Wuhan Neurophth Biotechnology Limited CompanyRecruitingLeber's Hereditary Optic Neuropathy (LHON)China
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Medical College of WisconsinTerminatedLeber's Hereditary Optic Neuropathy (LHON)United States
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University Hospital, AngersUnknownLeber Hereditary Optic NeuropathyFrance
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Netherlands Institute for Innovative Ocular SurgeryAmnitrans Eyebank Rotterdam; Melles CorneaClinic RotterdamCompletedCorneal Dystrophies, HereditaryNetherlands
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Netherlands Institute for Innovative Ocular SurgeryAmnitrans Eyebank RotterdamCompletedCorneal Dystrophies, HereditaryNetherlands
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Children's Mercy Hospital Kansas CityKBRCompleted
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Hospital de Olhos Sadalla Amin GhanemCompletedEye Diseases, Hereditary
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HAE Global Registry FoundationRecruitingHereditary Angioedema Type I and IIItaly
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Austria, Czechia, Germany, Hungary, Italy, Netherlands, North Macedonia, Poland, United Kingdom
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Bin LiHuazhong University of Science and TechnologyCompletedLeber Hereditary Optic NeuropathyChina
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Prothya BiosolutionsCompletedHereditary Angioedema Type I | Angioneurotic EdemaNetherlands
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University Hospital, Clermont-FerrandRecruitingHereditary DysfibrinogenemiaFrance
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Wolfson Medical CenterUnknown
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Centre Hospitalier Régional Metz-ThionvilleCompleted
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AstraZenecaCompletedMcCune-Albright SyndromeFrance, Italy, United Kingdom, Germany
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National Institute of Dental and Craniofacial Research...RecruitingMcCune-Albright SyndromeUnited States
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National Institute of Mental Health (NIMH)CompletedPET Imaging of Phosphodiesterase-4 (PDE4) in Brain and Peripheral Organs of McCune-Albright SyndromeNervous System DiseaseUnited States
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Price Vision GroupTerminatedFuchs' Endothelial DystrophyUnited States
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Singapore National Eye CentreUnknownFuchs' Endothelial DystrophySingapore
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Massachusetts General HospitalCompletedHereditary Sensory and Autonomic Neuropathy Type IUnited States
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Santhera PharmaceuticalsWithdrawnLeber's Hereditary Optic Neuropathy
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Massachusetts Eye and Ear InfirmaryCompletedFuchs' Endothelial DystrophyUnited States
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University of AarhusActive, not recruitingFuchs' Endothelial DystrophyDenmark
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Maastricht University Medical CenterZonMw: The Netherlands Organisation for Health Research and DevelopmentCompleted
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Oregon Health and Science UniversityTerminated
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Santhera PharmaceuticalsNo longer availableLeber's Hereditary Optic Neuropathy
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Stealth BioTherapeutics Inc.CompletedLeber's Hereditary Optic NeuropathyUnited States
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Medical University of ViennaRecruiting
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Argo SanteGenSight BiologicsCompleted
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National Eye Institute (NEI)CompletedCorneal Dystrophies, Hereditary | Corneal DiseaseUnited States, China, Italy
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Boston Children's HospitalCureAP4 FoundationRecruitingHereditary Spastic Paraplegia | SPG50 | SPG47 | SPG51 | SPG52 | AP4-related Hereditary Spastic Paraplegia | Early Onset Hereditary Spastic Paraplegia | SPG4 | SPG3A | SPG15 | SPG11United States
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Institut National de la Santé Et de la Recherche...UnknownAutoinflammatory Diseases, Hereditary
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Universitaire Ziekenhuizen KU LeuvenFund for Scientific Research, Flanders, Belgium; Funds for Research in Ophthalmology... and other collaboratorsCompletedFuchs' Endothelial DystrophyBelgium
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Johns Hopkins UniversityRecruitingGranular Dystrophy, CornealUnited States
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Weill Medical College of Cornell UniversityRecruitingGynecologic Cancer | Hereditary Cancer SyndromeUnited States
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University Eye Hospital, FreiburgCompletedFuchs' Endothelial DystrophyGermany
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Byron LamNational Eye Institute (NEI)Active, not recruitingLeber's Hereditary Optic NeuropathyUnited States
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic NeuropathyCanada, Germany, United Kingdom
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TakedaRecruitingAngioedema | Hereditary Angioedema (HAE)Canada
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TakedaRecruitingHereditary Angioedema (HAE)United Kingdom
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ShireTakeda Development Center Americas, Inc.No longer availableAngioedema | Hereditary Angioedema (HAE)United States, Canada, Germany, Hungary, Spain
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ShireCompletedHereditary Angioedema (HAE)Japan