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Clinical Trials on Alpha Thalassemia Major
Total 3363 results
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Sangamo TherapeuticsSanofiCompletedTransfusion Dependent Beta-thalassemiaUnited States
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Novartis PharmaceuticalsCompletedBeta Thalassemia Transfusion DependentItaly
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Tehran University of Medical SciencesNovartisUnknownBone Marrow Transplantation | Beta-ThalassemiaIran, Islamic Republic of
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Cairo UniversityRecruitingPulmonary Function | Physical Fitness | β-ThalassemiaEgypt
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Vanderbilt University Medical CenterMedical College of Wisconsin; VersitiCompletedSickle Cell Anemia (HbSS, or HbSβ-thalassemia0)United States
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Zymenex A/SEuropean CommissionCompleted
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Assiut UniversityNot yet recruiting
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Ain Shams UniversityUnknownBeta-thalassemia | Serum Ferritin | Iron Chelation TherapyEgypt
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Protagonist Therapeutics, Inc.CompletedChronic Anemia | β-thalassemia | Ineffective ErythropoiesisUnited States, Malaysia, Turkey, Thailand, United Kingdom, Italy, Lebanon, Tunisia, Greece
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Tanta UniversityRecruitingStress | Dexmedetomidine | Mechanical Ventilation | Propofol | Salivary Alpha AmylaseEgypt
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Assiut UniversityNot yet recruitingPre-Eclampsia | Intrauterine Growth Restriction | alpha1 Anti-trypsin
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Phoenicia BioScienceNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Beta Thalassemia IntermediaUnited States, Canada
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CelgeneCompletedBeta-ThalassemiaGreece, Italy, Lebanon, Thailand, Turkey
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Tanta UniversityRecruitingBeta Thalassemia With Increased Tricuspid Regurgitant Jet VelocityEgypt
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Assiut UniversityNot yet recruiting
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Assiut UniversityUnknown
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Anemia, Sickle Cell | Beta-Thalassemia | Hematopoietic Stem Cell TransplantationUnited States, Canada
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsEnrolling by invitationHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Canada, Italy, United Kingdom, Germany
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Nova Laboratories LimitedCompletedSickle Cell Disease | Sickle Cell Hemoglobin C | Sickle Cell-beta-thalassemia | Sickle-Cell; Hemoglobin Disease, ThalassemiaUnited Kingdom, Jamaica
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Editas Medicine, Inc.Not yet recruitingSickle Cell Disease | Hemoglobinopathies | Transfusion-dependent Beta-Thalassemia
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Institute of Hematology & Blood Diseases HospitalRecruitingGene Therapy | Transfusion-dependent Beta-ThalassemiaChina
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Italy, Germany
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Assiut UniversityNot yet recruitingSickle Cell Disease, Beta Thalassemia Intermedia
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CelgeneCompletedMyelodysplastic Syndromes | Beta-thalassemiaAustria
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NovartisCompletedIron Overload | Beta-thalassemiaUnited States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)TerminatedHeart Diseases | Cardiovascular Diseases | Beta-ThalassemiaUnited States
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Kenneth Ataga, MDAugusta UniversityCompletedSickle Cell Anemia | Sickle - Beta Thalassemia
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Sideris PharmaceuticalsTerminatedIron Overload | Beta-ThalassemiaUnited States, Canada, Lebanon, Thailand, Turkey
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Novartis PharmaceuticalsCompletedBeta-ThalassemiaUnited States
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Cairo UniversityCompletedQuality of Life | Fatigue | Cognitive Change | Beta-ThalassemiaEgypt
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Abfero Pharmaceuticals, IncWithdrawnIron Overload | Beta-ThalassemiaThailand, Lebanon, Turkey, Canada
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La Jolla Pharmaceutical CompanyTerminatedBeta-ThalassemiaAustralia, Thailand, United States, Greece, Italy, Lebanon, Turkey, United Kingdom
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Zymenex A/SEuropean CommissionCompletedAlpha MannosidosisCzechia, Germany, Norway, United Kingdom
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Hospices Civils de LyonCompleted
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Bioray LaboratoriesXiangya Hospital of Central South University; Sun Yat-Sen Memorial Hospital... and other collaboratorsNot yet recruiting
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Nanfang Hospital of Southern Medical UniversityShenzhen Second People's Hospital; Shenzhen Children's Hospital; ZhuHai Hospital and other collaboratorsRecruitingBeta ThalassemiaChina
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ChaingMai UniversityActive, not recruitingThalassemia Trait | Thalassemia; MixedThailand
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Federico II UniversityCompleted
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HemaQuest Pharmaceuticals Inc.Completed
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Genzyme, a Sanofi CompanyCompletedBeta-ThalassemiaUnited States
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Grifols Therapeutics LLCCompletedAlpha₁-Antitrypsin DeficiencyUnited States
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ShireTerminatedBeta-Thalassemia | Transfusional Iron OverloadUnited States, Lebanon, Canada, Italy, Turkey
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Bioray LaboratoriesXiangya Hospital of Central South University; The 923rd Hospital of Joint Logistics...Recruiting
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Shanghai BDgene Co., Ltd.920th Hospital of Joint Logistics Support Force of People's Liberation Army...RecruitingHematologic DiseasesChina
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Nanfang Hospital of Southern Medical UniversityShenzhen Second People's Hospital; Shenzhen Children's Hospital; ZhuHai Hospital and other collaboratorsRecruiting
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Nanfang Hospital of Southern Medical University303rd Hospital of the People's Liberation Army; Liuzhou Municipal Maternity... and other collaboratorsRecruiting
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HaEmek Medical Center, IsraelCompleted
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Deborah RundCompleted
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedThalassemiaUnited States, Canada
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Mahidol UniversityCompleted