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Clinical Trials on Alpha Thalassemia
Total 622 results
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Emmaus Medical, Inc.CompletedSickle Cell Anemia | Sickle ß0-ThalassemiaUnited States
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HaEmek Medical Center, IsraelCompletedSickle Cell Anemia | Sickle Cell ThalassemiaIsrael
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Columbia UniversityNational Heart, Lung, and Blood Institute (NHLBI); Alpha-1 FoundationActive, not recruitingAlpha 1-Antitrypsin Deficiency | Genetic DiseaseUnited States
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University of Alabama at BirminghamNational Institutes of Health (NIH); Mereo BioPharmaCompletedEmphysema or COPD | Alpha-1 Antitrypsin Deficiency (AATD) | Pi*ZZ, Pi*SZ, Pi*Null, Another Rare Phenotype/Genotype Known to be Associated With Either Low or Functionally Impaired AAT Including F or I MutationsUnited States
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Gamida Cell ltdCompletedSickle Cell Disease & ThalassemiaUnited States
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Jeffrey Zwicker, MDQuercegen PharmaceuticalsWithdrawnSickle Cell Disease | Sickle Cell-Beta0-Thalassemia
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Anemia | Sickle Cell-Beta0-ThalassemiaUnited States
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Istanbul UniversityCompletedHeart Diseases | Breast Cancer | Thalassemia MinorTurkey
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University of Milano BicoccaCompletedCovid19 | Thalassemia MajorItaly
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University of Michigan Rogel Cancer CenterCSL Behring; The Leukemia and Lymphoma SocietyCompletedGraft vs Host DiseaseUnited States
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Alnylam PharmaceuticalsTerminatedAntitrypsin Deficiency Liver DiseaseUnited Kingdom
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Soroka University Medical CenterUnknownPost Cardiac Surgery Systemic Inflammatory Response
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University of Texas Southwestern Medical CenterWithdrawn
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University of FloridaCompletedAlpha-1 Antitrypsin Deficiency | Liver Fibrosis | AATD | AAT DeficiencyUnited States
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Kamada, Ltd.Completed
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Invenux, LLCState University of New York - Downstate Medical CenterActive, not recruitingSickle Cell Disease | Sickle-Beta Zero ThalassemiaUnited States
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The University of Hong KongCompletedHomozygous αº-thalassemia | Hb Bart's DiseaseChina
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Singapore General HospitalShanghai Yueyang Integrated Medicine Hospital; Singapore Bao Zhong Tang TCM...CompletedMyelodysplastic Syndrome (MDS) | Myelofibrosis (MF) | Thalassemia Intermedia | Aplastic Anaemia (AA)Singapore
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HaEmek Medical Center, IsraelCompletedSickle Cell Anemia | Sickle Cell ThalassemiaIsrael
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Kamada, Ltd.CompletedEmphysemaUnited Kingdom, Canada, Denmark, Germany, Ireland, Netherlands, Sweden
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Huashan HospitalRecruitingPositron-Emission Tomography | Alpha Synuclein PathologyChina
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Indonesia UniversityDanone Institute InternationalCompletedOverweight | Nutritional Status | Complementary Feeding Recommendation | Linear Programming, | Omega-3 Fatty Acids | Malondialdehyde | Alpha-TocopherolIndonesia
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Novo Nordisk A/SNot yet recruitingHealthy Volunteers Sickle Cell Disease, ThalassemiaUnited States
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HaEmek Medical Center, IsraelUnknownSickle Cell Anemia | Sickle Cell β+ or β0 ThalassemiaUnited States, Israel
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Medical University of South CarolinaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedChronic PancreatitisUnited States
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Gerard TurinoCompletedEmphysema | Alpha 1-Antitrypsin DeficiencyUnited States, Canada
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Shiraz University of Medical SciencesCompleted
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Hospital Authority, Hong KongUnknownProstatic Hyperplasia | Adrenergic Alpha-AntagonistsChina
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Medical University of South CarolinaCSL BehringCompletedSmoking | Emphysema | Alpha-1 Antitrypsin Deficiency | COPDUnited States
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Julia FinkelCompletedSCD With Severe Phenotype (HbSS, HbSβ0 Thalassemia, HbSOARab)United States
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Sun Yat-sen UniversityNot yet recruitingLong-term Effects of Thymosin Alpha 1 Treatment
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Columbia UniversityCompletedMyelodysplastic Syndromes | Sickle Cell Disease | Aplastic Anemia | Transfusional Iron Overload | Thalassemia MajorUnited States
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Grifols Therapeutics LLCCompletedAlpha 1-Antitrypsin DeficiencyDenmark, Sweden, United Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)CompletedLung Diseases, Obstructive | Emphysema | Alpha 1-Antitrypsin DeficiencyUnited States
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Novartis PharmaceuticalsCompletedNon-transfusion Dependent ThalassemiaGreece, Taiwan, Italy, United Kingdom, Lebanon, Turkey, Malaysia, Thailand, United States
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Novartis PharmaceuticalsWithdrawnFocus on Transfusion Dependent Thalassemia Patients Who Are Inadequate Responders to Deferasirox > 35mg/kgQD
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Grifols Therapeutics LLCTerminatedType 1 Diabetes MellitusUnited States
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University of Campania "Luigi Vanvitelli"CompletedIron Overload | Endocrine; Complications | Transfusion-dependent ThalassemiaItaly
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Assistance Publique - Hôpitaux de ParisCompletedMajor Sickle Cell Syndrome of Type SS or Sβ ThalassemiaFrance
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University of NottinghamNottingham University Hospitals NHS TrustRecruitingChronic Obstructive Pulmonary Disease | Alpha 1-Antitrypsin DeficiencyUnited Kingdom
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Assistance Publique - Hôpitaux de ParisUnknownEmphysema | Alpha 1-Antitrypsin DeficiencyFrance
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Mitchell CairoRecruitingHodgkin Lymphoma | Sickle Cell Disease | Acute Leukemia | Beta-Thalassemia | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Diamond Blackfan Anemia | Amegakaryocytic Thrombocytopenia | KostmannUnited States
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States
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Imara, Inc.Quintiles, Inc.CompletedSickle Cell Disease | Sickle Beta 0 Thalassemia | Sickle-Cell; Hb-SCUnited States
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New York Medical CollegeCompletedLymphoma | Leukemia | Sickle Cell Disease | Histiocytosis | Immunodeficiencies | Inborn Errors of Metabolism | Bone Marrow Failure | Beta ThalassemiaUnited States
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Novartis PharmaceuticalsCompletedThalassemia, Non-transfusional-dependent Thalassemia (NTDT), Myeloplastic Dysplasia (MDS), Other AnemiaAustralia
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Reproductive & Genetic Hospital of CITIC-XiangyaCompletedThalassemia,Embryonic Development,Reproductive Sterility and InfertilityChina
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Inhibrx, Inc.Not yet recruitingEmphysema | Alpha 1-Antitrypsin Deficiency
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Inhibrx Biosciences, IncRecruitingEmphysema | Alpha 1-Antitrypsin DeficiencyUnited States, Australia, United Kingdom, New Zealand
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University of FloridaRecruitingAlpha-1 Antitrypsin Deficiency | Cystic Fibrosis (CF) | AATD | AAT DeficiencyUnited States