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Clinical Trials on Alpha and Beta Thalassemia
Total 722 results
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Wolfson Medical CenterUnknownPatients With Thalassemia Intermedia, | Congenital Dyserythropoietic Anemia Type I
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Ersi VoskaridouCompletedOsteoporosis | Thalassemia MajorGreece
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Ain Shams UniversityUnknownDNA Damage | Endocrine Disease | Fertility Decreased MaleEgypt
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HaEmek Medical Center, IsraelUnknownIron Deficiency | ThalassemiaIsrael
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Fakultas Kedokteran Universitas IndonesiaCompletedThalassemia | Pneumococcal InfectionIndonesia
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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New York Medical CollegeCompletedLymphoma | Leukemia | Sickle Cell Disease | Histiocytosis | Immunodeficiencies | Inborn Errors of Metabolism | Bone Marrow Failure | Beta ThalassemiaUnited States
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Ente Ospedaliero Ospedali GallieraCompletedPulmonary Arterial Hypertension | Thalassemia Major | Thalassemia IntermediaItaly
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Masonic Cancer Center, University of MinnesotaRecruitingSickle Cell Disease | Severe Congenital Neutropenia | Paroxysmal Nocturnal Hemoglobinuria | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Diamond Blackfan Anemia | Transfusion Dependent Alpha- or Beta- Thalassemia | Non-Malignant Hematologic DisordersUnited States
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Azienda Ospedaliero-Universitaria di ModenaRecruitingIron Overload | Hemochromatosis | Thalassemia Major | Thalassemia Intermedia | EndocrinopathyItaly
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Invenux, LLCState University of New York - Downstate Medical CenterActive, not recruitingSickle Cell Disease | Sickle-Beta Zero ThalassemiaUnited States
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Fairview University Medical CenterCompletedNeutropenia | Sickle Cell Anemia | Red-Cell Aplasia, Pure | Thalassemia MajorUnited States
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University Health Network, TorontoRecruitingThalassemia MajorCanada
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Ospedale MicrocitemicoAzienda Sanitaria Locale di CagliariCompletedIron Overload | CardiomyopathyItaly
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ApoPharmaCompletedHemosiderosis | Thalassemia MajorGreece, Italy
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University Health Network, TorontoCompletedThalassemia Major | Chronic Blood Transfusion Related Iron OverloadCanada
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Novartis PharmaceuticalsCompletedAnemia | HemosiderosisUnited States, Germany, Belgium, United Kingdom, Italy, Canada, France
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Chinese University of Hong KongRecruitingHaemoglobin Barts HydropsHong Kong
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Shanghai First Maternity and Infant HospitalUnknown
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Mahidol UniversityCompletedFibrosis | Hepatitis C | ThalassemiaThailand
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Imara, Inc.Quintiles, Inc.CompletedSickle Cell Disease | Sickle Beta 0 Thalassemia | Sickle-Cell; Hb-SCUnited States
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Baxalta now part of ShireArriva Pharmaceuticals, Inc.CompletedAlpha1-antitrypsin DeficiencyUnited States
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Greenwood Genetic CenterCompletedGalactosialidosis | Sialidosis | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Beta Mannosidosis | Mucolipidosis II | Mucolipidosis III | Schindler DiseaseUnited States
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Grifols Therapeutics LLCRecruiting
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Vertex Pharmaceuticals IncorporatedCompletedAlpha1-Antitrypsin DeficiencyUnited States, Germany, Canada, Ireland, Sweden, United Kingdom
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Grifols Therapeutics LLCGrifols Japan K.K.Completed
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Baxalta now part of ShireCompletedAlpha1-antitrypsin DeficiencyUnited States, Canada
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Baxalta now part of ShireTerminated
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Grifols Therapeutics LLCGrifols Japan K.K.CompletedAlpha1-Antitrypsin DeficiencyJapan
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Baxalta now part of ShireArriva Pharmaceuticals, Inc.CompletedAlpha1-antitrypsin DeficiencyUnited States
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Obstetrix Medical GroupTerminatedFetal Growth Retardation | Hydrops FetalisUnited States
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Boston Children's HospitalNovartisCompletedSickle Cell Disease | Thalassemia Major | Transfusion-dependent HemachromatosisUnited States
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Z Factor LimitedHammersmith Medicines Research; Centessa Pharmaceuticals plcTerminatedAlpha1 Anti-Trypsin DeficiencyUnited Kingdom
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Baxalta now part of ShireCompleted
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RWTH Aachen UniversityUnknown
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TakedaRecruitingAlpha1-Antitrypsin DeficiencyItaly, United States, Poland, Portugal
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TakedaTakeda Development Center Americas, Inc.RecruitingAlpha1-Antitrypsin DeficiencyUnited States, Belgium, Switzerland, Canada, Australia, Germany, United Kingdom, Austria, France, Spain, Portugal, Italy, Poland, Brazil
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Istanbul UniversityCompletedHeart Diseases | Breast Cancer | Thalassemia MinorTurkey
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TakedaEnrolling by invitationAlpha1-Antitrypsin DeficiencyUnited Kingdom, Germany, United States, Austria, Portugal
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University of Milano BicoccaCompletedCovid19 | Thalassemia MajorItaly
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Jeffrey Zwicker, MDQuercegen PharmaceuticalsWithdrawnSickle Cell Disease | Sickle Cell-Beta0-Thalassemia
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Anemia | Sickle Cell-Beta0-ThalassemiaUnited States
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Singapore General HospitalShanghai Yueyang Integrated Medicine Hospital; Singapore Bao Zhong Tang TCM...CompletedMyelodysplastic Syndrome (MDS) | Myelofibrosis (MF) | Thalassemia Intermedia | Aplastic Anaemia (AA)Singapore
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University of California, San FranciscoEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationHydrops Fetalis | Birth Defect | Fetal AnomalyUnited States
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University of California, San FranciscoJohns Hopkins University; Eunice Kennedy Shriver National Institute of Child... and other collaboratorsEnrolling by invitation
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Columbia UniversityCompletedMyelodysplastic Syndromes | Sickle Cell Disease | Aplastic Anemia | Transfusional Iron Overload | Thalassemia MajorUnited States
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Thomas Jefferson UniversityGlaxoSmithKline; Drexel UniversityUnknownQuality of Life | Inflammation | Sickle Cell Disease | HEMOGLOBIN SS | Hemoglobin S Beta-0 ThalassemiaUnited States