- ICH GCP
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Clinical Trials on Amino Acid Metabolism, Inborn Errors
Total 4768 results
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Nutricia UK LtdCompletedPhenylketonurias | Hyperphenylalaninaemia, Type IUnited Kingdom
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University of Southern CaliforniaBioMarin PharmaceuticalCompleted
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Stanford UniversityBioMarin PharmaceuticalWithdrawnClassical Phenylketonuria(PKU)
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University Children's Hospital, ZurichRecruitingUrea Cycle DisordersSwitzerland
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States, Germany, Italy
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Nutricia ResearchCompleted
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BioMarin PharmaceuticalActive, not recruiting
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States, Turkey, Canada, France, Germany, Italy, United Kingdom
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Sutphin DrugsUnknownHereditary Tyrosinemia, Type IIndia
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Charite University, Berlin, GermanyJohannes Gutenberg University MainzCompletedPhenylketonuria | Endothelial Dysfunction
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Washington University School of MedicineUniversity of Missouri-Columbia; Northwestern University; Oregon Health and Science... and other collaboratorsTerminated
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Fondation Ophtalmologique Adolphe de RothschildCompleted
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metaX Institut fuer Diatetik GmbHBirmingham Children's HospitalCompletedPhenylketonurias | Hyperphenylalaninaemia | Tetrahydrobiopterin DeficiencyUnited Kingdom
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BioMarin PharmaceuticalActive, not recruitingPhenylketonuria (PKU)United States, Germany
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Homology Medicines, IncEnrolling by invitationPhenylketonuria | PAH DeficiencyUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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University of British ColumbiaRare Disease Foundation, Vancouver, CanadaCompleted
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Brendan LeeCompleted
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University of GlasgowUnknownPhenylketonuria (PKU)United Kingdom
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University Hospital, ToursInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedPKU | HyperphenylalaninemiaFrance
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Dr. Linda RandolphBioMarin PharmaceuticalTerminated
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Children's National Research InstituteBoston Children's HospitalRecruitingUrea Cycle DisordersUnited States
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Cytonet GmbH & Co. KGCRS Clinical Research Services Mannheim GmbHCompleted
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University of South FloridaNational Institutes of Health (NIH)CompletedUrea Cycle DisordersUnited States
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Cytonet GmbH & Co. KGCompletedUrea Cycle DisordersGermany
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Rigshospitalet, DenmarkNot yet recruitingBrain Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Brain Diseases, Metabolic | Phenylketonurias | Brain Diseases, Metabolic, Inborn | Amino Acid Metabolism, Inborn Errors | Metabolic DiseaseDenmark
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University Hospital, ToursCompletedAdult Phenylketonuria Non Treated PatientsFrance
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Austria, Czechia, Finland, Hungary, Ireland, Italy, Netherlands, Norway, Poland, Portugal, Spain, Sweden, United Kingdom
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Cycle Pharmaceuticals Ltd.ParexelCompletedHereditary Tyrosinemia, Type ISouth Africa
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Brendan LeeEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedAmino Acid Metabolism, Inborn Errors | Urea Cycle Disorders | Argininosuccinic AciduriaUnited States
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Andrea GropmanEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingBrain Diseases, Metabolic, Inborn | Amino Acid Metabolism, Inborn Errors | Urea Cycle DisordersUnited States, Canada, Germany, Switzerland
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Yassin Abdelghaffar Charity Center for Liver Disease...Society of Friends of Liver Patients in the Arab World (SLPAW)RecruitingHereditary Tyrosinemia, Type IEgypt
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University of Missouri-ColumbiaCompleted
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University Hospital, ToursCompletedPhenylketonuriaFrance
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Cycle Pharmaceuticals Ltd.ParexelCompletedHereditary Tyrosinemia, Type ISouth Africa
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University of ZurichCompletedPhenylketonuria (PKU) and HyperphenylalaninemiaSwitzerland
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IGermany, United Kingdom, France
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Orphanetics Pharma Entwicklungs GmbHTerminatedPhenylalanine Hydroxylase Deficiencies
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National Center for Research Resources (NCRR)University of TexasCompleted
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University of Novi Sad, Faculty of Sport and Physical...Completed
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Vitaflo International, LtdActive, not recruiting
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Cycle Pharmaceuticals Ltd.ParexelCompletedHereditary Tyrosinemia, Type ISouth Africa
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Swedish Orphan BiovitrumCompletedEfficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1 (HT-1)Hereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Sweden
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University of TorontoCompletedProtein/Amino Acid Metabolism | Indicator Amino Acid Oxidation MethodCanada
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Baylor College of MedicineCompletedCitrullinemiaUnited States
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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Shanghai Vitalgen BioPharma Co., Ltd.RecruitingGlutaric Acidemia Type I | Glutaric Aciduria Type IChina
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Baylor Research InstituteNational Institutes of Health (NIH)CompletedHyperhomocysteinemiaUnited States