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Clinical Trials on Anémie aplasique congénitale
Total 11477 results
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Children's Hospital Medical Center, CincinnatiRecruitingCongenital Dyserythropoietic Anemia (CDA)United States
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Northwell HealthCompletedPure Red Cell Aplasia | Diamond Blackfan Anemia | Blackfan Diamond Syndrome | DBA | Congenital Hypoplastic AnemiaUnited States
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Lille Catholic UniversityUnknown
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Wolfson Medical CenterUnknownPatients With Thalassemia Intermedia, | Congenital Dyserythropoietic Anemia Type I
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Congenital Hemolytic AnemiaUnited States
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Stanford UniversityUniversity of Alabama at Birmingham; University of MinnesotaCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States
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UCSF Benioff Children's Hospital OaklandNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited Kingdom, United States, Germany
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Paul SzabolcsRecruitingSickle Cell Anemia | Diamond-blackfan Anemia | Beta-thalassemia MajorUnited States
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UCSF Benioff Children's Hospital OaklandNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States, United Kingdom, Germany
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Masonic Cancer Center, University of MinnesotaNational Marrow Donor ProgramCompletedSickle Cell Disease | Thalassemia | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Shwachman-Diamond SyndromeUnited States
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Novartis PharmaceuticalsCompletedMyelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan AnemiaUnited States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
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Queen Fabiola Children's University HospitalRecruitingIron Deficiency Anemia | Congenital Heart Disease in Children | Cardiac Surgical Procedures | Iron DeficienciesBelgium
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital Neutropenia | Diamond-blackfan AnemiaUnited States
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Boston Children's HospitalAgios Pharmaceuticals, Inc.CompletedPyruvate Kinase Deficiency | Congenital Non-Spherocytic Hemolytic AnemiaUnited States, Germany, Canada, Czechia, Italy, Netherlands
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Northwell HealthTerminatedDiamond Blackfan AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedDiamond Blackfan AnemiaUnited States
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Talaris Therapeutics Inc.Duke UniversityWithdrawnAnemia, Sickle Cell | Thalassemia | Beta-Thalassemia | Bone Marrow Failure Syndromes | Diamond-Blackfan Anemia | Alpha-Thalassemia | Complex and Transfusion-dependent HemoglobinopathiesUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Aplastic | Red-Cell Aplasia, Pure | Anemia, Diamond-BlackfanUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSteroid-refractory Diamond-Blackfan Anemia (DBA)United States
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National Heart, Lung, and Blood Institute (NHLBI)TerminatedAplastic Anemia | Pure Red Cell Aplasia | Diamond Blackfan AnemiaUnited States
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Feinstein Institute for Medical ResearchDiamond Blackfan Anemia Foundation, Inc.Recruiting
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Federal Scientific Clinical Centre of Pediatric...Unknown
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingAnemia, Diamond-BlackfanUnited States
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Agios Pharmaceuticals, Inc.Active, not recruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Denmark, Turkey, Netherlands, Czechia, United Kingdom, Germany, Canada, Switzerland
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Memorial Sloan Kettering Cancer CenterCompletedBeta Thalassemia Major | Congenital AnemiasUnited States
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St. Jude Children's Research HospitalCompletedAnemia, Aplastic | Diamond-Blackfan Anemia | Amegakaryocytic Thrombocytopenia | Kostmann SyndromeUnited States
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Agios Pharmaceuticals, Inc.RecruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Germany, Netherlands, Canada, France, Israel, Switzerland, Italy
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St. Jude Children's Research HospitalBaylor College of Medicine; Children's Hospital of Philadelphia; Dana-Farber... and other collaboratorsRecruitingMyelodysplastic Syndromes | Sickle Cell Disease | Fanconi Anemia | Severe Congenital Neutropenia | Bone Marrow Failure Syndromes | Blood Coagulation Disorder | Erythrocyte Disorder | Leukocyte Disorder | Hemostasis | Dyskeratosis Congenita | Diamond-Blackfan Anemia | Congenital Thrombocytopenia | Myeloproliferative...United States
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Emory UniversityNational Heart, Lung, and Blood Institute (NHLBI)Recruiting
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The University of Hong KongCompletedHomozygous αº-thalassemia | Hb Bart's DiseaseChina
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Adrianna Vlachos, MDTerminatedPure Red Cell Aplasia | Diamond Blackfan AnemiaUnited States
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University of California, San FranciscoCompletedSickle Cell Disease | Hemoglobinopathies | Thalassemia | Hematologic Malignancies | Immunodeficiencies | Fanconi's Anemia | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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Elizabeth Yang, MD, PhDUniversity of California, San Francisco; Global Blood Therapeutics; PediatrixCompleted
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National Heart, Lung, and Blood Institute (NHLBI)National Institutes of Health (NIH)CompletedSickle Cell AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle CellUnited States
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Children's Hospital Medical Center, CincinnatiCompletedSickle Cell AnemiaUnited States
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Duke UniversityNational Institutes of Health (NIH)Completed
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Lagos State UniversityCompletedSickle Cell AnemiaNigeria
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Assistance Publique - Hôpitaux de ParisCompleted
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Fred Hutchinson Cancer CenterCompletedSickle Cell AnemiaUnited States
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National Institutes of Health Clinical Center (CC)Completed
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National Center for Research Resources (NCRR)Shirley Ryan AbilityLabCompletedSickle Cell Anemia
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Mitchell CairoRecruitingHodgkin Lymphoma | Sickle Cell Disease | Acute Leukemia | Beta-Thalassemia | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Diamond Blackfan Anemia | Amegakaryocytic Thrombocytopenia | KostmannUnited States
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Agios Pharmaceuticals, Inc.TerminatedAnemia | Anemia, Hemolytic | Pyruvate Kinase Deficiency | Pyruvate Kinase Deficiency AnemiaUnited States, United Kingdom, Italy, Spain, Netherlands
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Children's Hospital Medical Center, CincinnatiWithdrawn
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Washington University School of MedicineTerminatedAnemia, Sickle CellUnited States
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); University of Tennessee; Assisi...Completed
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Hillhurst Biopharmaceuticals, Inc.National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle CellUnited States
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Global Blood TherapeuticsCompletedAnemia, Sickle CellUnited States
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Amy TangPfizerRecruitingSickle Cell Anemia in ChildrenUnited States