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Clinical Trials on Anémie aplasique congénitale
Total 11504 results
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Mayo ClinicNational Cancer Institute (NCI)CompletedLymphoma | Leukemia | Anemia | Unspecified Adult Solid Tumor, Protocol Specific | Multiple Myeloma and Plasma Cell Neoplasm | Precancerous Condition | Lymphoproliferative DisorderUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedLymphoma | Leukemia | Anemia | Multiple Myeloma and Plasma Cell NeoplasmUnited States
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Ankara City Hospital BilkentNot yet recruiting
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University of Campania "Luigi Vanvitelli"Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico; University of Milan and other collaboratorsRecruitingChronic Kidney Diseases | Ureteropelvic Junction ObstructionItaly
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ENCellRecruitingCharcot-Marie-Tooth Disease Type 1AKorea, Republic of
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Istituto Ortopedico RizzoliRecruitingCollagen Diseases | Joint Hypermobility | Hypermobility Syndrome | Laxity of Ligament | Danlos Disease, EhlersItaly
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University of the PunjabHigher Education Commission (Pakistan); Centre of Excellence in Molecular Biology... and other collaboratorsRecruitingBurn Scar | Craniofacial Microsomia | Romberg Disease | Post-Traumatic Scar (Disorder)Pakistan
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University of Colorado, DenverMayo Clinic; National Institute of Diabetes and Digestive and Kidney Diseases...RecruitingOverweight and Obesity | Autosomal Dominant Polycystic KidneyUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingDisorders of Sex Development (DSD) | Pediatric and Adolescent Cancers of the Genital Tract | Reproductive Endocrine Conditions in Puberty | Structural Gynecologic Conditions Including Vulvar and Vaginal ConditionsUnited States
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Children's Hospital of Eastern OntarioThe Physicians' Services Incorporated FoundationRecruitingChild | Obstructive Sleep Apnea | Down SyndromeCanada
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Johns Hopkins UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAnhydramnios | Potter Syndrome | Lung Hypoplasia | Multicystic Dysplastic Kidney | Multicystic Renal Dysplasia, Bilateral | Lower Urinary Tract Obstructive Syndrome | Fetal Renal AnomalyUnited States
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National Institute of Neurological Disorders and...RecruitingMuscular Dystrophies | Inherited Neuromuscular Conditions | Inherited Neuropathies | Muscle Myopathies | Hereditary Spastic ParaplegiasUnited States
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National Cancer Institute (NCI)SuspendedDown Syndrome | Recurrent B Acute Lymphoblastic LeukemiaUnited States, Canada, Puerto Rico, Australia
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Pharnext S.C.A.Premier Research Group plc; Eurofins Optimed; Synteract HCR (Syneos Health); Gr... and other collaboratorsActive, not recruitingCharcot-Marie-Tooth Disease, Type IAUnited States, Belgium, Canada, France, Netherlands, Spain, United Kingdom
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Vastra Gotaland RegionGöteborg UniversityCompletedHypermobile Ehlers-Danlos Syndrome | Joint Hypermobility SyndromeSweden
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Imperial College LondonCompletedHereditary Hemorrhagic Telangiectasia | Pulmonary Arteriovenous MalformationsUnited Kingdom
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Texas Tech University Health Sciences Center, El...TerminatedCerebral Cavernous Malformation | Hemorrhagic Stroke, IntracerebralUnited States
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Sol-Gel Technologies, Ltd.TerminatedBasal Cell Nevus SyndromeUnited States, France, Belgium, Denmark, Germany, Italy, Netherlands, Spain, United Kingdom
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Institut Jerome LejeuneHôpital Necker-Enfants MaladesActive, not recruitingDown Syndrome | Obstructive Sleep Apnea of NewbornFrance
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ProQR TherapeuticsTerminatedRetinitis Pigmentosa | Usher Syndrome Type 2United States, Canada, France
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University Hospital, BordeauxAMRO-HHT-France - Association Maladie de Rendu-OslerCompletedHereditary Hemorrhagic Telangiectasia | Osler Weber Rendu DiseaseFrance
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SanofiActive, not recruitingUsher's SyndromeUnited States, France
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Yuzuncu Yıl UniversityCompleted
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Poznan University of Life SciencesCompletedObesity | Polycystic Ovary Syndrome | Hyperandrogenism | Insulin ResistancePoland
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Indiana University School of MedicineTerminatedSleep Apnea, Obstructive | Respiration DisordersUnited States
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Near East University, TurkeyCompletedPolycystic Ovary Syndrome | c Type Natriuretic Peptide | Menstrual Irregularity | HyperandrogenismCyprus
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UCSF Benioff Children's Hospital OaklandNational Cancer Institute (NCI)CompletedNeoplastic SyndromeUnited States
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Edward Maytin, MD, PhDDUSA Pharmaceuticals, Inc.CompletedBasal Cell Nevus SyndromeUnited States
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Pharnext SACompletedPhase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients (PLEO-CMT) (PLEO-CMT)Charcot-Marie-Tooth Disease Type 1AUnited States, United Kingdom, Belgium, Canada, France, Netherlands, Spain, Germany
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NobelpharmaCompletedPlaque | Tuberous Sclerosis | Angiofibroma | Hypomelanotic MaculeJapan
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University of AarhusUnknownPseudohypoparathyroidism | Idiopathic Hypoparathyroidism | Autosomal Dominant HypocalcaemiaDenmark
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Alta Bates Summit Medical CenterTerminatedUrinary Tract Infections | Breast Cancer Female | Dyspareunia | Dysuria | Genitourinary Abnormality | Vaginal AbnormalityUnited States
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Milton S. Hershey Medical CenterUniversity of PennsylvaniaCompletedPolycystic Ovary SyndromeUnited States
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Vancouver General HospitalNovo Nordisk A/STerminated
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Kenneth Peters, MDWilliam Beaumont HospitalsCompletedUrinary Incontinence | Spinal Cord Injury | Spina Bifida
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Children's Hospital and Health System Foundation...University of Wisconsin, MadisonCompletedEpilepsy | Asthma | Spina Bifida | Rheumatologic Conditions (JRA,Lupus)United States
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Guy Hains ChiropractorCompletedCompression Neuropathy, Carpal TunnelCanada
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Ministry of Health, Labour and Welfare, JapanUnknownKidney, Polycystic, Autosomal DominantJapan
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Jonsson Comprehensive Cancer CenterNational Cancer Institute (NCI)CompletedLymphoma | Leukemia | Anemia | Unspecified Adult Solid Tumor, Protocol Specific | Multiple Myeloma and Plasma Cell Neoplasm | Precancerous Condition | Lymphoproliferative DisorderUnited States
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States
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University of UtahTerminatedPrimary Myelofibrosis | Anemia | Thrombocytopenia | Plasma Cell Myeloma | Recurrent Plasma Cell Myeloma | IDH2 Gene Mutation | IDH1 Gene Mutation | Secondary Myelofibrosis | ASXL1 Gene Mutation | EZH2 Gene MutationUnited States
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LMU KlinikumUniversity of Pisa; German Federal Ministry of Education and Research; European...RecruitingMitochondrial Diseases | MDS | Mitochondrial Myopathies | MELAS Syndrome | MIDD | Kearns-Sayre Syndrome | MERRF Syndrome | Barth Syndrome | Leigh Syndrome | MNGIE | LHON | Pearson Syndrome | NARP Syndrome | Coenzyme Q10 Deficiency | SANDO | SCAE | MIRAS | CPEOAustria, Germany, Italy
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Cantonal Hospital GraubuendenUniversity of ZurichNot yet recruitingAutosomal Dominant Polycystic Kidney DiseaseSwitzerland
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Rege Nephro Co., Ltd.RecruitingAutosomal Dominant Polycystic Kidney Disease (ADPKD)Japan
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Children's Health IrelandBelfast Health and Social Care Trust; University of Edinburgh; University Hospital... and other collaboratorsRecruitingQuality of Life | Obstructive Sleep Apnea | Down Syndrome | Behavior | Adherence, TreatmentUnited Kingdom, Ireland
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Institut National de la Santé Et de la Recherche...Recruiting
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Maxima Medical CenterRecruitingChronic Pain Syndrome | Nerve Entrapment Syndrome | Anterior Cutaneous Nerve Entrapment SyndromeNetherlands
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New York Institute of TechnologyRecruitingPain, Chronic | Ehlers-Danlos SyndromeUnited States
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Palvella Therapeutics, Inc.RecruitingBCCs in Gorlin Syndrome PatientsUnited States, United Kingdom
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingAutosomal Dominant Polycystic Kidney DiseaseUnited States