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Clinical Trials on Anemia, Hemolytic, Congenital Nonspherocytic
Total 1753 results
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Duke UniversityNational Institute of Nursing Research (NINR); National Institutes of Health...Active, not recruitingChronic Kidney Diseases | Diabetes Mellitus, Type 1 | Systemic Lupus Erythematosus | Inflammatory Bowel Diseases | Cystic Fibrosis | Sickle Cell Disease | Stem Cell Transplant | Childhood Cancer | Organ TransplantUnited States
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria de... and other collaboratorsCompletedFanconi AnemiaSpain
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Cystinosis Research FoundationUnknownCystinosis | Nephropathic Cystinosis | Renal Fanconi SyndromeUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Porteus, Matthew, MDRecruiting
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Sanguine BiosciencesTerminated
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Children's Hospital Medical Center, CincinnatiFood and Drug Administration (FDA)Completed
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Fred Hutchinson Cancer CenterNational Heart, Lung, and Blood Institute (NHLBI); Rocket Pharma LimitedActive, not recruiting
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Unspecified Adult Solid Tumor, Protocol Specific | Fanconi AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedNeoplasms | Myelodysplastic Syndromes | Hematologic Diseases | Leukemia | Severe Combined Immunodeficiency | Fanconi Anemia | Anemia, Aplastic | Hematopoietic Stem Cell Transplantation
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Kaohsiung Medical University Chung-Ho Memorial...CompletedInflammation | Fatigue | Hemolysis | Oxidative Stress | Iron Deficiency | Sports AnemiaTaiwan
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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Masonic Cancer Center, University of MinnesotaNot yet recruitingAcquired Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria | Severe Aplastic Anemia | Acquired Amegakaryocytic Thrombocytopenia
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AO GENERIUMCompletedParoxysmal Nocturnal Hemoglobinuria | Marchiafava-Micheli Syndrome | Paroxysmal HemoglobinuriaRussian Federation
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Children's Hospital Medical Center, CincinnatiRecruiting
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Columbia UniversityUnknownSevere Combined Immunodeficiency | Fanconi Anemia | Bone Marrow Failure | OsteopetrosisUnited States
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Panineeya Mahavidyalaya Institute of Dental Sciences...CompletedMelasma, Periodontitis, Vitamin D Abnormalities, Anaemia
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AstraZenecaRecruitingParoxysmal Nocturnal HemoglobinuriaChina
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Regeneron PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaTaiwan, Korea, Republic of, Turkey, Spain, Thailand, Singapore, Japan, Canada, Malaysia, Poland, Italy
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Alexion Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal HemoglobinuriaItaly
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Hoffmann-La RocheChugai PharmaceuticalRecruitingParoxysmal Nocturnal HemoglobinuriaUnited States, Korea, Republic of, Spain, Germany, Estonia, Japan, Colombia, Saudi Arabia, Turkey, Brazil, France, Greece, Poland, Taiwan, Netherlands, Italy, Australia, Sweden, Singapore, Portugal, Hungary, Belgium, Canada, Czechia, Hong... and more
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Alexion Pharmaceuticals, Inc.AstraZenecaActive, not recruitingParoxysmal Nocturnal HemoglobinuriaChina
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Alexion Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaItaly, Spain, Belgium, France, Turkey, Austria, Brazil, Netherlands, Australia, Finland, Russian Federation, Sweden, Canada, United States
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Alexion Pharmaceuticals, Inc.Active, not recruitingParoxysmal Nocturnal HemoglobinuriaFrance, Italy, Spain, United States, Thailand, Korea, Republic of, United Kingdom, Israel, Czechia, Greece, Poland, Brazil, Japan, Canada, Malaysia
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Samsung Bioepis Co., Ltd.CompletedParoxysmal Nocturnal HemoglobinuriaKorea, Republic of, Taiwan, Malaysia, Thailand, Romania, India, Mexico, Ukraine
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Hoffmann-La RocheActive, not recruiting
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Chengdu Suncadia Medicine Co., Ltd.Active, not recruitingParoxysmal Nocturnal HemoglobinuriaChina
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AO GENERIUMCompletedParoxysmal Nocturnal HemoglobinuriaRussian Federation
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Wuhan Createrna Science and Technology Co., LtdCompletedParoxysmal Nocturnal HemoglobinuriaChina
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Regeneron PharmaceuticalsTerminatedParoxysmal Nocturnal HemoglobinuriaUnited States
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AlexionCompleted
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Novartis PharmaceuticalsNot yet recruitingParoxysmal Nocturnal Hemoglobinuria
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Chengdu Suncadia Medicine Co., Ltd.RecruitingParoxysmal Nocturnal HemoglobinuriaChina
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Wuhan Createrna Science and Technology Co., LtdRecruitingParoxysmal Nocturnal HemoglobinuriaChina
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Omeros CorporationRecruitingParoxysmal Nocturnal HemoglobinuriaUkraine
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NovelMed TherapeuticsNot yet recruitingParoxysmal Nocturnal Hemoglobinuria
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Novartis PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaFrance, Spain, Italy, Turkey, Germany, United States, Korea, Republic of, United Kingdom
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Regeneron PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaMexico, Korea, Republic of, Turkey, Italy, United Kingdom, Thailand, Poland, Singapore, Spain, Taiwan, Canada, Japan, United States, Malaysia, Greece, Romania, Hungary
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Novartis PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaUnited States, Korea, Republic of, Singapore, Taiwan, Italy, Turkey, France, Germany, Malaysia, Lithuania, Netherlands, United Kingdom, Japan, Czechia, Spain, China, Brazil
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Alexion Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal HemoglobinuriaUnited States
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BioCryst PharmaceuticalsTerminatedParoxysmal Nocturnal Hemoglobinuria | PNHUnited Kingdom, Austria, South Africa
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BioCryst PharmaceuticalsActive, not recruitingParoxysmal Nocturnal HemoglobinuriaUnited Kingdom, Hungary, France, Spain, Malaysia, South Africa, Korea, Republic of
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaTaiwan, Singapore, Korea, Republic of, Malaysia
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Regeneron PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaKorea, Republic of, Taiwan, Malaysia, Hong Kong, Hungary, United Kingdom
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Regeneron PharmaceuticalsAvailableParoxysmal Nocturnal Hemoglobinuria
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Regeneron PharmaceuticalsTerminatedParoxysmal Nocturnal HemoglobinuriaHong Kong, Korea, Republic of, Malaysia, Hungary, Taiwan, United Kingdom
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University of Milano BicoccaComitato Maria Letizia Verga,ItalyRecruitingLymphoma, Non-Hodgkin | Leukemia, Myeloid, Acute | Leukemia, B-cell | Adrenoleukodystrophy | Lymphoma, Hodgkin | Thalassemia Major | Leukemia, T Cell | DrepanocytosisItaly
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Omeros CorporationRecruitingParoxysmal Nocturnal HemoglobinuriaSwitzerland, Germany, Ukraine, United Kingdom