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Clinical Trials on Angioedemas, Hereditary in New Zealand
Total 368 results
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Yale UniversityThe Hospital for Sick Children; United States Department of Defense; Connecticut...CompletedChronic Pain | Neurofibromatosis 1United States
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The Cooper Health SystemCompletedMetachromatic LeukodystrophyUnited States
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NFlection Therapeutics, Inc.CompletedNeurofibromatosis 1 | Cutaneous NeurofibromaUnited States
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La Jolla Pharmaceutical CompanyPRA Health SciencesCompletedHereditary HemochromatosisUnited States, Australia, France, United Kingdom
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National Human Genome Research Institute (NHGRI)CompletedMelanoma | Breast Neoplasm | Ovarian Neoplasm | Hereditary Neoplastic SyndromeUnited States, Finland, Iceland, Sweden
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NightstaRx Ltd, a Biogen CompanyCompletedChoroideremiaFinland, United States, Canada, Denmark, Netherlands, Germany, United Kingdom, Brazil, France
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National Cancer Institute (NCI)CompletedRecurrent Fallopian Tube Carcinoma | Recurrent Ovarian Carcinoma | Recurrent Primary Peritoneal Carcinoma | Breast Carcinoma | Ovarian Carcinoma | Pancreatic Carcinoma | Prostate Carcinoma | Recurrent Breast Carcinoma | Estrogen Receptor Negative | HER2/Neu Negative | Progesterone Receptor Negative | Triple-Negative... and other conditionsUnited States
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Aspa TherapeuticsRecruiting
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National Cancer Institute (NCI)Completed
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Gemini Therapeutics, Inc.TerminatedMacular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal DiseaseUnited States
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NYU Langone HealthCompletedNeurofibromatosis 1 and 2 (NF1 and NF2)United States
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AlexionRecruiting
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NYU Langone HealthCompletedAnxiety Disorders | Familial Dysautonomia | Dysthymia | Paroxysmal Hypertension | Autosomal Recessive DiseaseUnited States
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National Center for Research Resources (NCRR)CompletedRetinitis Pigmentosa | Usher Syndrome | Congenital Hearing ImpairmentUnited States
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Dana-Farber Cancer InstituteNovartis PharmaceuticalsCompletedTuberous Sclerosis Complex | TSC1 | TSC2 | MTORUnited States
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Alkeus Pharmaceuticals, Inc.RecruitingStargardt Disease | Stargardt Macular Degeneration | Stargardt Macular Dystrophy | Autosomal Recessive Stargardt Disease 1 (ABCA4-related)United States
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Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
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UCSF Benioff Children's Hospital OaklandNational Cancer Institute (NCI)Completed
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John Jay High SchoolUnknownNeurofibromatosis Type 1United States
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University of RochesterCompletedCharcot Marie Tooth DiseaseUnited States
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University of New MexicoCompletedRetinitis Pigmentosa | Age Related Macular Degeneration | Congenital Stationary Night Blindness | ColorblindnessUnited States
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National Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Stage III Colon Cancer AJCC v8 | Colon Adenocarcinoma | DNA Repair DisorderUnited States, Puerto Rico, Germany
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Genzyme, a Sanofi CompanyCompletedAlport Syndrome Patients With eGFR Between 45-90 ml/Min/1.73 m2France, Germany, Australia, United States, United Kingdom, Canada
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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Novartis PharmaceuticalsCompletedIron Overload | Hereditary HemochromatosisUnited States, Germany, Italy, Australia, Canada, France
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedKidney CancerUnited States, Canada, Puerto Rico, Australia, Netherlands, New Zealand, Switzerland
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedKidney CancerUnited States, Canada, Puerto Rico, Australia, Netherlands, Switzerland, New Zealand
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AstraZenecaApproved for marketingNF type1 With Inoperable Plexiform NeurofibromasUnited States
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UCSF Benioff Children's Hospital OaklandNational Cancer Institute (NCI)CompletedNeoplastic SyndromeUnited States
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ProQR TherapeuticsActive, not recruitingEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, Netherlands, United Kingdom, Germany
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Massachusetts General HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... and other collaboratorsCompletedNervous System Diseases | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Lou Gehrig's Disease | Hereditary Spastic ParaparesisUnited States, Canada
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NightstaRx Ltd, a Biogen CompanyCompletedX-Linked Retinitis PigmentosaUnited States, France, United Kingdom, Finland, Netherlands, Germany, Canada
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyCanada, United States, Bulgaria
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The Cleveland ClinicCompletedFamilial Mediterranean FeverUnited States
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Horizon Pharma USA, Inc.Approved for marketingThyroid Eye Disease | Graves' OrbitopathyUnited States
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NYU Langone HealthWithdrawnEpilepsy | Tuberous Sclerosis | Dravet Syndrome | Focal Seizures | Lennox-Gastaut SyndromeUnited States
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National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiCompletedMetabolism, Inborn Errors | Leukodystrophy, Globoid Cell | Tay-Sachs Disease | Porphyria, ErythropoieticUnited States
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National Cancer Institute (NCI)RecruitingRenal Cell Carcinoma | Stage III Renal Cell Cancer AJCC v8 | Stage IV Renal Cell Cancer AJCC v8 | Papillary Renal Cell Carcinoma | Hereditary Leiomyomatosis and Renal Cell Carcinoma | Sporadic Papillary Renal Cell CarcinomaUnited States
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Astellas Pharma Global Development, Inc.Active, not recruitingStargardt's Macular DystrophyItaly, United States, Israel, United Kingdom, Germany, Spain, Hungary, France
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Johns Hopkins UniversityPentax MedicalActive, not recruitingFamilial Adenomatous Polyposis | Duodenal AdenomasUnited States
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Viridian Therapeutics, Inc.Recruiting
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UCSF Benioff Children's Hospital OaklandGenentech, Inc.CompletedBasal Cell Nevus Syndrome | Gorlin's SyndromeUnited States
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedNon-melanomatous Skin CancerUnited States
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UCSF Benioff Children's Hospital OaklandGenentech, Inc.CompletedBasal Cell Nevus Syndrome | Gorlin SyndromeUnited States
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National Eye Institute (NEI)CompletedRetinitis Pigmentosa | Usher Syndrome | Retinitis Pigmentosa Syndromic | Congenital Deafness | Retinitis Pigmentosa and DeafnessUnited States
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Jersey Shore University Medical CenterRutgers University; Rutgers Cancer Institute of New JerseyCompletedPancreatic Cancer | Parathyroid Disease | Thymic Cancer | MEN1 SyndromeUnited States
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Cure HHTUniversity of Colorado, Denver; Massachusetts General Hospital; Mayo Clinic; Children... and other collaboratorsRecruitingArteriovenous Malformations | Epistaxis | Hereditary Hemorrhagic Telangiectasia | GastroIntestinal Bleeding | Telangiectasia | Vascular Malformation | Cerebral Arteriovenous MalformationsUnited States
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Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan
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University Hospital TuebingenCompleted
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Rhythm Pharmaceuticals, Inc.CompletedBardet Biedl Syndrome (BBS) | Alström Syndrome (AS)United States, United Kingdom, France, Canada, Puerto Rico, Spain