- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Aromatic L-Amino Acid Decarboxylase Deficiency
Total 112 results
-
University Hospital, MontpellierRecruitingAromatic L-Amino Acid Decarboxylase DeficiencyFrance
-
Shanghai Jiao Tong University School of MedicineShanghai Vitalgen BioPharma Co., Ltd.RecruitingAromatic L-amino Acid Decarboxylase (AADC) DeficiencyChina
-
Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingAromatic L-amino Acid Decarboxylase Deficiency
-
National Taiwan University HospitalPTC TherapeuticsCompletedAromatic L-amino Acid Decarboxylase (AADC) DeficiencyTaiwan
-
National Taiwan University HospitalPTC TherapeuticsCompletedAromatic Amino Acid Decarboxylase DeficiencyTaiwan
-
National Taiwan University HospitalCompletedAromatic L-amino Acid Decarboxylase DeficiencyTaiwan
-
Fondation Ophtalmologique Adolphe de RothschildCompleted
-
West Kazakhstan Medical UniversityRecruitingOrnithine Transcarbamylase Deficiency | Biotinidase Deficiency | Citrullinemia | Glutaric Acidemia Type II | Argininosuccinic Aciduria | Maple Syrup Urine Disease | Primary Carnitine Deficiency | Homocystinuria | Carnitine Palmitoyltransferase II Deficiency | Arginase Deficiency | Very Long-chain Acyl-CoA... and other conditionsKazakhstan
-
Washington University School of MedicineUniversity of California, Davis; Universidad San Francisco de Quito; Pan American...CompletedCholine Deficiency | Vitamin B-12 Deficiency | Lipids Deficiency | Amino Acids DeficiencyEcuador
-
University Hospital, Strasbourg, FranceUnknownThe Glutathione Synthetase DeficiencyFrance
-
SingHealth PolyclinicsCompletedVitamin D Deficiency | Fall | Vitamin B 12 Deficiency | Folate Deficiency | Muscle Strength | HyperhomocysteinemiaSingapore
-
Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University...Recruiting
-
Origin BiosciencesCompletedMolybdenum Cofactor Deficiency | Isolated Sulfite Oxidase DeficiencySpain, Israel, United States, United Kingdom, Canada, Netherlands, Germany, Saudi Arabia, Tunisia, Japan, Italy, Malaysia, Poland, Turkey
-
National Center for Research Resources (NCRR)UNC Lineberger Comprehensive Cancer CenterCompletedMetabolism, Inborn Errors | Methionine Adenosyltransferase Deficiency
-
Beijing Chest HospitalNot yet recruitingMalnutrition | Lung Cancer | Amino Acid Deficiency
-
University of West LondonCompletedVitamin B12 DeficiencyUnited Kingdom
-
S.LAB (SOLOWAYS)Center of New Medical TechnologiesRecruiting
-
Huilian ZhuNot yet recruiting
-
Peking UniversityNational Natural Science Foundation of China; Institute of reproductive and...CompletedHyperhomocysteinemiaChina
-
Baylor Research InstituteNational Institutes of Health (NIH)CompletedHyperhomocysteinemiaUnited States
-
Center for Health, Exercise and Sport Sciences,...Completed
-
University of Novi Sad, Faculty of Sport and Physical...Completed
-
Queen Sirikit National Institute of Child HealthChulalongkorn UniversityCompletedObesity | HyperhomocysteinemiaThailand
-
London School of Hygiene and Tropical MedicineCompletedHyperhomocysteinemia | Micronutrient DeficienciesGambia
-
National Institute of Cardiology, Laranjeiras,...CompletedEndothelial Dysfunction | HyperhomocysteinemiaBrazil
-
Smt. Kashibai Navale Medical College and General...CompletedType 2 Diabetes | Vitamin B12 Deficiency | HyperhomocysteinemiaIndia
-
SEAMEO Regional Centre for Food and NutritionLondon School of Hygiene and Tropical Medicine; University College, London; University... and other collaboratorsRecruitingProtozoan Infections | Birth Weight | Weight Gain | Vitamin A Deficiency | Folate Deficiency | Zinc Deficiency | Child Development | Salmonella Infections | Anemia, Iron Deficiency | Fatty Acid Deficiency | Birth Length | B12 Deficiency Vitamin | Mineral Deficiency | E. Coli Infection | Shigella Infection | Amino Acid Deficiency and other conditionsIndonesia
-
IRCCS Azienda Ospedaliero-Universitaria di BolognaUniversity of BolognaCompletedInflammation | Mortality | HyperhomocysteinemiaItaly
-
National Institute of Neurological Disorders and...CompletedSuccinic Semialdehyde Dehydrogenase Deficiency | SSADH DeficiencyUnited States
-
Arcturus Therapeutics, Inc.RecruitingOTC Deficiency | Ornithine Transcarbamylase Deficiency | OTCDSpain, Belgium, United Kingdom, Sweden
-
S.LAB (SOLOWAYS)Center of New Medical Technologies; Triangel ScientificCompletedHyperlipoproteinemias | HyperhomocysteinemiaRussian Federation
-
Aeglea BiotherapeuticsTerminatedArginase I Deficiency | HyperargininemiaCanada
-
Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
-
National Institute of Neurological Disorders and...CompletedSuccinic Semialdehyde | Dehydrogenase Deficiency | DiseasesUnited States
-
CENTOGENE GmbH RostockWithdrawnMetabolic Disorders | Tyrosinosis | Hepatorenal Tyrosinemia | Fumarylacetoacetase Deficiency | Fah DeficiencyGermany, Sri Lanka, India
-
Eunice Kennedy Shriver National Institute of Child...Children's National Research InstituteTerminatedPhase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency Disease
-
Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn... and other collaboratorsCompletedMethylmalonic Acidemia | Carbamoyl-Phosphate Synthase I Deficiency Disease | Propionic Acidemia, Type I and/or Type II | Ornithine Carbamoyltransferase DeficiencyUnited States
-
University of PennsylvaniaTerminatedOrnithine Transcarbamylase Deficiency Disease
-
Ultragenyx Pharmaceutical IncCompletedOrnithine Transcarbamylase DeficiencyUnited States
-
Second Affiliated Hospital of Nanchang UniversityPeking University First HospitalUnknownHypertension | HyperhomocysteinemiaChina
-
Shenzhen Ausa Pharmed Co.,LtdPeking University First Hospital; China Medical University, China; Fudan University and other collaboratorsUnknownEssential HypertensionChina
-
Radboud University Medical CenterCompletedMild HyperhomocysteinemiaNetherlands
-
Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Australia, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
-
University College, LondonRecruitingOrnithine Transcarbamylase DeficiencyUnited Kingdom
-
Arcturus Therapeutics, Inc.Active, not recruitingOrnithine Transcarbamylase DeficiencyUnited States
-
BioMarin PharmaceuticalQuintiles, Inc.CompletedTetrahydrobiopterin DeficiencyChina
-
Ultragenyx Pharmaceutical IncActive, not recruitingOrnithine Transcarbamylase (OTC) DeficiencyCanada, United States, France, Spain, United Kingdom
-
Arcturus Therapeutics, Inc.CompletedOrnithine Transcarbamylase DeficiencyNew Zealand