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Clinical Trials on Arthrogryposis Multiplex Congenita
Total 16001 results
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Mario Negri Institute for Pharmacological ResearchTerminatedSirolimus In Autosomal Dominant Polycystic Kidney Disease And Severe Renal Insufficiency (SIRENA-II)Autosomal Dominant Polycystic Kidney Disease (ADPKD)Italy
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University Hospital, BrestCompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)France
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Medical University of ViennaUnknownPolycystic Kidney, Type 1 Autosomal Dominant Disease | Polycystic Kidney, Type 2 Autosomal Dominant DiseaseAustria
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Mario Negri Institute for Pharmacological ResearchCompletedAutosomal Dominant Polycystic Kidney DiseaseItaly
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Mayo ClinicPolycystic Kidney Disease FoundationCompletedKidney, Polycystic, Autosomal DominantUnited States
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The Rogosin InstituteWeill Medical College of Cornell University; New York Presbyterian HospitalWithdrawnAutosomal Dominant Polycystic Kidney DiseaseUnited States
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The Rogosin InstituteWeill Medical College of Cornell UniversityCompletedAutosomal Dominant Polycystic KidneyUnited States
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Reata, a wholly owned subsidiary of BiogenTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, United Kingdom, Australia, France, Japan, Germany, Belgium, Czechia, Italy
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Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)Germany, Italy, Belgium, United Kingdom
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Assistance Publique - Hôpitaux de ParisNovartisCompletedAutosomal Dominant Polycystic Kidney DiseaseFrance
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ShireNational Institutes of Health (NIH)CompletedAutosomal Dominant Hypocalcemia (ADH)United States
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National Human Genome Research Institute (NHGRI)CompletedMultiple AbnormalitiesUnited States
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Kamari Pharma LtdRecruiting
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Hannover Medical SchoolBoehringer IngelheimNot yet recruitingAutosomal Dominant Polycystic Kidney
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Otsuka Pharmaceutical Development & Commercialization...CompletedChronic Kidney Disease | Autosomal Dominant Polycystic Kidney DiseaseAustralia, Belgium, Italy, Spain, Sweden, United States, Canada, Netherlands, Czechia, Poland, Germany, Russian Federation, Hungary, Israel, Puerto Rico, Argentina, Denmark, South Africa, United Kingdom, Norway, France, Romania
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Ministry of Health, Labour and Welfare, JapanUnknownKidney, Polycystic, Autosomal DominantJapan
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Children's Hospital of Fudan UniversitySecond Affiliated Hospital of Wenzhou Medical University; Guangzhou Women and... and other collaboratorsRecruitingGenetic Disease | Congenital Malformation | Multiple MalformationChina
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Rege Nephro Co., Ltd.RecruitingAutosomal Dominant Polycystic Kidney Disease (ADPKD)Japan
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Weill Medical College of Cornell UniversityThe Rogosin InstituteEnrolling by invitationAutosomal Dominant Polycystic Kidney DiseaseUnited States
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University Hospital, MontpellierMinistry of Health, FranceCompletedAutosomal Dominant Retinitis PigmentosaFrance
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Palvella Therapeutics, Inc.RecruitingPachyonychia CongenitaUnited States, United Kingdom
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Pachyonychia Congenita ProjectRecruiting
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Mei changlinUnknownHypertension | Autosomal Dominant Polycystic Kidney DiseaseChina
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Regulus Therapeutics Inc.RecruitingPolycystic Kidney, Autosomal Dominant | Autosomal Dominant Polycystic Kidney Disease | ADPKDUnited States
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University of Southern CaliforniaEnrolling by invitationAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Novartis PharmaceuticalsCompletedAutosomal Dominant Polycystic Kidney DiseaseGermany, Austria, France
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Palvella Therapeutics, Inc.RecruitingPachyonychia CongenitaUnited States
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Palvella Therapeutics, Inc.Active, not recruitingPachyonychia CongenitaUnited States
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TransDerm, Inc.Pachyonychia Congenita ProjectCompletedPachyonychia CongenitaUnited States
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Pachyonychia Congenita ProjectCompletedPachyonychia CongenitaUnited States
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Palvella Therapeutics, Inc.UnknownPachyonychia CongenitaUnited States
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Tel-Aviv Sourasky Medical CenterUnknownPachyonychia Congenita
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Kyorin UniversityCompletedDisease Progression | Autosomal Dominant Polycystic Kidney DiseaseJapan
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Children's Hospital of Chongqing Medical UniversityThe First Hospital of Jilin University; Xuzhou Maternity and Child Health Care... and other collaboratorsCompletedGenetic Diseases | Birth Defect | Congenital Malformation | Multiple Malformation | Newborn; FitChina
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Radboud University Medical CenterRecruitingAutosomal Dominant Polycystic Kidney | Polycystic Liver Disease | Liver Cyst | Autosomal Dominant Polycystic Liver DiseaseNetherlands
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant HypocalcemiaUnited States, France, Denmark, Australia, Japan, Belgium, Canada, Italy, Netherlands, United Kingdom, Portugal, Finland, Germany
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Xinhua Hospital, Shanghai Jiao Tong University...UnknownIntellectual Disability | Rare Diseases | Multiple Congenital AnomalyChina
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Brugmann University HospitalNot yet recruitingCardiac Surgery | Congenital Heart Disease | Blood Transfusion | Morbidity, MultipleBelgium
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University of Erlangen-Nürnberg Medical SchoolRecruitingAutosomal Dominant Polycystic Kidney Disease | Uncontrolled Hypertension | Renal DenervationGermany
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Mayo ClinicCompletedAutosomal Dominant Polycystic Kidney Disease | Polycystic Liver Disease | Autosomal Dominant Polycystic Liver Disease | Somatostatin AnalogsUnited States
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Xiaofan ZhuAvailableFanconi Anemia | Autosomal or Sex Linked Recessive Genetic Disease | Bone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases. | Hematopoiesis Maintainance.China
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University of JohannesburgCompletedFetal Congenital Abnormalities | Prolonged Pregnancy | Multiple PregnancySouth Africa
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University of AlbertaWithdrawnHypoplastic Left Heart Syndrome | Congenital Heart Defect | TGA - Transposition of Great Arteries | Congential Absence of Heart Structure | Congenital Malformation of Heart, Unspecified | Hypoplastic Right Heart Syndrome | Congential Malformations of Aortic Valve | Congential Malformations of Great...Canada
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant Hypocalcemia (ADH)United States, Australia, Denmark, Italy, France, Japan, Canada, Czechia, Netherlands
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National Human Genome Research Institute (NHGRI)CompletedProteus SyndromeUnited States
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Johns Hopkins UniversityCompletedEpidermolysis Bullosa Simplex | Pachyonychia CongenitaUnited States
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Taipei Medical University Shuang Ho HospitalUniversity of Southern CaliforniaEnrolling by invitationChronic Kidney Diseases | Autosomal Dominant Polycystic Kidney DiseaseTaiwan
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National Human Genome Research Institute (NHGRI)Recruiting