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Clinical Trials on Ataxia Telangiectasia
Total 595 results
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Larimar Therapeutics, Inc.Enrolling by invitationFriedreich AtaxiaUnited States
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Larimar Therapeutics, Inc.CompletedFriedreich AtaxiaUnited States
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Monash UniversityChildren's Hospital of Philadelphia; McGill University; University of Florida; University... and other collaboratorsActive, not recruitingFriedreich AtaxiaUnited States, Canada, Australia, Brazil, Germany
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Berta AlemanyInstitut d'Investigació Biomèdica de Girona Dr. Josep Trueta; Universitat de... and other collaboratorsCompleted
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IRCCS Eugenio MedeaUniversity of Rome Tor VergataCompleted
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Neurocrine BiosciencesTakedaCompletedFriedreich AtaxiaUnited States
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research AllianceCompleted
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research AllianceCompleted
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Institut National de la Santé Et de la Recherche...Completed
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Larimar Therapeutics, Inc.Children's Hospital of PhiladelphiaCompletedFriedreich AtaxiaUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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H. Lundbeck A/SCompletedFriedreich's AtaxiaGermany, Austria, Italy
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Assistance Publique - Hôpitaux de ParisCompletedEffect of Pioglitazone Administered to Patients With Friedreich's Ataxia: Proof of Concept (ACTFRIE)Friedreich's AtaxiaFrance
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ApoPharmaCompletedFriedreich's AtaxiaBelgium, France, Italy, Spain
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ApoPharmaCompletedFriedreich's AtaxiaCanada, Australia, Belgium, France, Italy, Spain
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Assistance Publique - Hôpitaux de ParisCompleted
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Cure HHTUniversity of Colorado, Denver; Massachusetts General Hospital; Mayo Clinic; Children... and other collaboratorsRecruitingArteriovenous Malformations | Epistaxis | Hereditary Hemorrhagic Telangiectasia | GastroIntestinal Bleeding | Telangiectasia | Vascular Malformation | Cerebral Arteriovenous MalformationsUnited States
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Friedreich's Ataxia Research AllianceChildren's Hospital of Philadelphia; University of RochesterRecruitingFriedreich Ataxia | Neuro-Degenerative DiseaseUnited States, Canada, New Zealand, Australia, India
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University of MinnesotaFriedreich's Ataxia Research Alliance; Bob Allison Ataxia Research CenterCompletedFriedreich AtaxiaUnited States
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Adverum Biotechnologies, Inc.Adverum Biotechnologies SAS, a wholly owned subsidiary of Adverum Biotechnologies...CompletedFriedreich's AtaxiaFrance
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Weill Medical College of Cornell UniversityRecruitingFriedreich's AtaxiaUnited States
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University of PittsburghFriedreich's Ataxia Research AllianceCompleted
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Murdoch Childrens Research InstituteFriedreich's Ataxia Research AllianceCompleted
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Cairo UniversityCompleted
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Universidade Federal de PernambucoUnknownCerebellar Ataxia | Balance | Cerebellum; InjuryBrazil
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Shenzhen Beike Bio-Technology Co., Ltd.The Affiliated Nanjing Drum Tower Hospital of Nanjing University Medical... and other collaboratorsUnknown
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Manhattan Eye, Ear & Throat HospitalGenentech, Inc.CompletedPolypoidal Choroidal Vasculopathy | Pseudoxanthoma Elasticum | Pathological Myopia | Retinal Angiomatous Proliferation | Coats' Disease | Idiopathic Retinal Telangiectasia | Multi-focal Choroiditis | Rubeosis Iridis | Von Hippel Lindau Disease | BEST VITELLIFORM MACULAR DYSTROPHY, MULTIFOCAL (Disorder)United States
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Centre Hospitalier Universitaire de NīmesCompletedCerebellar AtaxiaFrance
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Second Affiliated Hospital, School of Medicine,...Recruiting
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Lexeo TherapeuticsRecruitingFriedreich Ataxia | Cardiomyopathy, SecondaryUnited States, Canada
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Hospices Civils de LyonRecruitingGAD-receptor Antibodies-associated EncephalitisFrance
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Second Affiliated Hospital, School of Medicine,...RecruitingHereditary AtaxiaChina
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University of California, DavisWithdrawn
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University Hospital, LimogesCompleted
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Cairo UniversityCompletedCerebellar AtaxiaEgypt
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Weill Medical College of Cornell UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingMyocardial Fibrosis | Cardiomyopathies | Friedreich Ataxia | Cardiac HypertrophyUnited States
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Centre Hospitalier Universitaire de NīmesCompletedNeurodegenerative Diseases | Cerebellar Ataxia | NeuropathyFrance
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Oregon Health and Science UniversityPortland VA Medical CenterTerminatedAtaxia | Essential Tremor | Cerebellar Diseases | Deep Brain StimulationUnited States
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Larimar Therapeutics, Inc.Clinilabs, Inc.CompletedHealthy Volunteers | Friedreich AtaxiaUnited States
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Cutera Inc.Completed
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Johns Hopkins UniversityVirginia Polytechnic Institute and State University; Johns Hopkins Discovery...Completed
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Hacettepe UniversityCompleted
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Cutera Inc.Completed
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University of California, DavisNational Institute on Aging (NIA); Forest LaboratoriesCompletedFragile X-Associated Tremor/Ataxia Syndrome | Fragile X Premutation CarriersUnited States
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Hacettepe UniversityCompleted
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Carrick Institute for Graduate StudiesCompletedAtaxiaUnited States
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UPECLIN HC FM Botucatu UnespFundação de Amparo à Pesquisa do Estado de São PauloCompletedVaricose Veins | TelangiectasisBrazil
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Prof. Dr. Matthis SynofzikRecruitingAtaxiaGermany, Italy, Australia, Brazil, France, New Zealand, Turkey