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Clinical Trials on Atrophie musculaire spinale de type 2
Total 516 results
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Gianni SoraruMario Negri Institute for Pharmacological ResearchRecruitingSpinal and Bulbar Muscular AtrophyItaly
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Novartis PharmaceuticalsActive, not recruitingSpinal Muscular AtrophyJapan, Belgium, Spain, Canada, United States, Australia, Italy, France, Netherlands
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyTaiwan, Belgium, Canada, United States, Australia, France, Italy, Portugal, United Kingdom
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Assistance Publique - Hôpitaux de ParisCompleted
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Synchron Medical, Inc.Active, not recruitingParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Neurologic Disorder | Spinal Muscular Atrophy | Cervical Spinal Cord Injury | Stroke, Lacunar | Paralysis; Stroke | Stroke Brainstem | Tetraplegic; Paralysis | Quadriplegia/TetraplegiaUnited States
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LMU KlinikumRecruitingPompe Disease (Late-onset) | FSHD | Spinal Muscular Atrophy Type 3 | Inclusion Body MyositisGermany
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ML Bio Solutions, Inc.RecruitingLimb-Girdle Muscular Dystrophy Type 2I (LGMD2I)United States, Netherlands, United Kingdom, Denmark, Australia, Italy, Norway
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TakedaRecruitingSpinal and Bulbar Muscular AtrophyJapan
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Novartis PharmaceuticalsCompletedSpinal and Bulbar Muscular AtrophyUnited States, Germany, Italy, Denmark
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Bar-Chama, Natan, M.D.RecruitingFertility IssuesUnited States
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Synchron Medical, Inc.WithdrawnParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Neurologic Disorder | Spinal Muscular Atrophy | Spinal Cord Injury | Stroke, Lacunar | Upper Limb Injury | Paralysis; Stroke | Stroke, BrainstemAustralia
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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National Institute of Neurological Disorders and...CompletedSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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University Hospital of North NorwayUniversity of Tromso; Norwegian Muscle Disease Association (FFM); Norwegian National... and other collaboratorsActive, not recruitingMuscular Dystrophies | Limb Girdle Muscular Dystrophy | Limb Girdle Muscular Dystrophy, Type 2I | Limb Girdle Muscular Dystrophy R9 FKRP-relatedNorway
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AdventHealth Translational Research InstituteRecruitingType 2 Diabetes | Aging | Muscle Atrophy | Sedentary Behavior | Pre-diabetesUnited States
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AnnJi Pharmaceutical Co., Ltd.Active, not recruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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Karen Brorup Heje PedersenCompletedHealthy Subjects | Spinal and Bulbar Muscular AtrophyDenmark
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Rio de Janeiro State UniversityLaboratory for Clinical and Experimental Research on Vascular BiologyCompletedType 2 Diabetes | Sarcopenia | Aging | MicrocirculationBrazil
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National Center for Research Resources (NCRR)Ohio State UniversityCompletedAmyotrophic Lateral Sclerosis | Spinal Muscular Atrophy | Spinobulbar Muscular Atrophy
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Mads Peter Godtfeldt StemmerikEdgewise Therapeutics, Inc.CompletedBecker Muscular Dystrophy | McArdle Disease | Limb-Girdle Muscular Dystrophy Type 2Denmark
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IRCCS Burlo GarofoloRecruiting
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Universidad Autonoma de MadridKing's College London; Centro Superior de Estudios Universitarios LasalleCompletedMuscle Atrophy | Intervertebral Disc Compression | Spine InjurySpain, United Kingdom
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The Children's Hospital of Zhejiang University...Withdrawn
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MarsiBionicsHospital General Universitario Gregorio Marañon; Hospital Infantil Universitario... and other collaboratorsRecruitingCerebral Palsy | Acquired Brain Injury | Spinal Muscular AtrophySpain
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National Taiwan University HospitalUnknownColon Cancer | Spinal Muscular Atrophy | Neonatal HyperbilirubinemiaTaiwan
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy Type 2France, Italy, Spain
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University Hospital, Basel, SwitzerlandCompletedLumbar Spinal Stenosis (LSS)Switzerland
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Nationwide Children's HospitalMyonexus TherapeuticsRecruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
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BiogenRecruitingObservational, Postmarketing Surveillance Study of Spinraza Injection (Nusinersen Sodium) (STANDARD)Muscular Atrophy, SpinalKorea, Republic of
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Fondazione Policlinico Universitario Agostino Gemelli...CompletedMuscular Atrophy, Spinal | UltrasoundItaly
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalUnited States
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Hoffmann-La RocheCompleted
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National Institutes of Health Clinical Center (CC)RecruitingCerebral Palsy | Muscular Dystrophy | Spina Bifida | Incomplete Spinal Cord InjuryUnited States
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National Institutes of Health Clinical Center (CC)RecruitingCerebral Palsy | Muscular Dystrophy | Spina Bifida | Incomplete Spinal Cord InjuryUnited States
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Fondazione Policlinico Universitario Agostino Gemelli...University of Messina; Istituto Giannina Gaslini; University of Milan; Ospedale...Recruiting
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Hoffmann-La RochePTC TherapeuticsCompletedMuscular Atrophy, SpinalUnited States
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Rigshospitalet, DenmarkCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy Type 2IDenmark
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Cystinose StiftungLabor Becker & Kollegen, Munich, Germany; Screening Labor Hannover; Genetikum... and other collaboratorsCompletedSpinal Muscular Atrophy | Cystinosis | Cystinosis, NephropathicGermany
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Lupin Ltd.WithdrawnMyotonic Dystrophy Type 1 and Type 2
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy | Kennedys DiseaseUnited States
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BiogenRecruitingMuscular Atrophy, SpinalUnited States
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BiogenCompletedMuscular Atrophy, SpinalChina
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Indiana University School of MedicineCure SMACompleted
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University Hospital FreiburgNovo Nordisk A/SCompleted
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Ramathibodi HospitalAstraZenecaCompletedSpinobulbar Muscular Atrophy | Kennedy's DiseaseThailand
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AdventHealth Translational Research InstituteActive, not recruitingType 2 Diabetes | Exercise | Muscular Atrophy | Sedentary Behavior | Pre-diabetesUnited States
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Seoul National University HospitalNational Research Foundation of KoreaNot yet recruitingSarcopenia | Spinal Disease
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National Institute of Neurological Disorders and...CompletedMotor Neuron DiseaseUnited States
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Politecnico di MilanoIRCCS Eugenio Medea; Villa Beretta Rehabilitation CenterCompletedMuscular Dystrophies | Muscular Dystrophy, Duchenne | Muscular Dystrophy, Becker | Muscular Dystrophy, Limb-Girdle Type 2Italy
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BiogenRecruitingHealthy Volunteer | Muscular Atrophy, SpinalKorea, Republic of, Germany, Belgium, Netherlands, France, Italy, Poland, Canada, United Kingdom, Israel