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Clinical Trials on Autosomal Recessive Degenerative and Progressive Cerebellar Ataxia
Total 610 results
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University of NottinghamNottingham University Hospitals NHS Trust; Royal Papworth HospitalActive, not recruitingAtaxia TelangiectasiaUnited Kingdom
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Johns Hopkins UniversityCompleted
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Johann Wolfgang Goethe University HospitalCompletedAtaxia Telangiectasia
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Sheba Medical CenterUnknownAtaxia TelangiectasiaIsrael
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Sheba Medical CenterUnknownAtaxia TelangiectasiaIsrael
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Johns Hopkins UniversityVirginia Polytechnic Institute and State University; Johns Hopkins Discovery...Completed
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Samsung Medical CenterCompletedSpinocerebellar Ataxias | Multiple System Atrophy, Cerebellar Variant (Disorder)Korea, Republic of
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University of PlymouthRecruitingAtaxia Telangiectasia | Ataxia Telangiectasia in ChildrenUnited Kingdom
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Johann Wolfgang Goethe University HospitalCompletedAtaxia TelangiectasiaGermany
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Assistance Publique - Hôpitaux de ParisRecruitingSpinocerebellar Ataxias | Inherited Movement Disorders | Hyperkinetic DisordersFrance
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Radboud University Medical CenterA-T Children's Project; Twan foundation (https://twanfoundation.nl)CompletedAtaxia Telangiectasia | ATM Gene MutationNetherlands
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Federal Research Institute of Pediatric Hematology...CompletedAtaxia Telangiectasia | DysmetriaRussian Federation
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IntraBio IncRecruitingAtaxia Telangiectasia | Louis Bar SyndromeSpain, United States, Germany, United Kingdom
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Wayne State UniversityUnknownAneuploidy | Autosomal Recessive DisorderUnited States
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Santhera PharmaceuticalsCompletedFreidreich's AtaxiaGermany, Netherlands, France, Austria, Belgium
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Institut National de la Santé Et de la Recherche...Not yet recruiting
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsActive, not recruitingFriedreich AtaxiaUnited States
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research Alliance; Stealth BioTherapeutics Inc.Active, not recruitingFriedreich AtaxiaUnited States
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Metro International Biotech, LLCChildren's Hospital of PhiladelphiaCompleted
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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Design TherapeuticsCompleted
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Minoryx Therapeutics, S.L.CompletedFriedreich AtaxiaSpain, Belgium, France, Germany
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLCCompletedFriedreich AtaxiaUnited States
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ShireCompletedFriedreich's AtaxiaUnited States
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National Institute of Neurological Disorders and...Completed
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University of South FloridaFriedreich's Ataxia Research Alliance; Edison Pharmaceuticals IncCompleted
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University of South FloridaUnknownFriedreich's AtaxiaUnited States
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Penwest Pharmaceuticals Co.CompletedFriedreich's AtaxiaUnited States
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Federico II UniversityCompleted
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National Institute of Neurological Disorders and...Completed
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ErydelCompletedGenetic Syndrome | Nervous System DiseaseIndia, United States, Israel, Australia, Belgium, Germany, Italy, Norway, Poland, Spain, Tunisia, United Kingdom
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Shenzhen Beike Bio-Technology Co., Ltd.The Affiliated Nanjing Drum Tower Hospital of Nanjing University Medical... and other collaboratorsUnknown
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University of Sao Paulo General HospitalUnknownCerebellar AtaxiaBrazil
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S. Andrea HospitalAgenzia Italiana del FarmacoCompleted
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Dr. Rebecca SchuleGerman Research Foundation; German Center for Neurodegenerative Diseases (DZNE)RecruitingSpastic AtaxiaCanada, France, Germany, Italy, Netherlands, Turkey, United Kingdom
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BiogenNot yet recruiting
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University of FloridaNational Institutes of Health (NIH); National Center for Advancing Translational... and other collaboratorsRecruiting
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European Friedreich's Ataxia Consortium for Translational...RecruitingFriedreich's AtaxiaAustria, Germany, Italy, Spain, Belgium, Czechia, France, Greece, Ireland, United Kingdom
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Murdoch Childrens Research InstituteActive, not recruiting
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Design Therapeutics, Inc.CompletedFriedreich AtaxiaUnited States
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RWTH Aachen UniversityAssistance Publique - Hôpitaux de ParisWithdrawnFriedreich AtaxiaSpain, Italy, Austria, Germany, United Kingdom, France
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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University of MinnesotaCompleted
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Children's Hospital of PhiladelphiaUniversity of California, Los Angeles; University of FloridaCompleted
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research Alliance; Vidara Therapeutics Research LtdCompleted
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLCCompletedFriedreich AtaxiaUnited States