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Clinical Trials on Autosomal Recessive Ichthyosis in New Zealand
Total 100 results
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Northwestern UniversityIcahn School of Medicine at Mount SinaiCompletedNetherton Syndrome | Ichthyosis | Lamellar Ichthyosis | Autosomal Recessive Congenital Ichthyosis | Congenital Ichthyosiform Erythroderma | Epidermolytic IchthyosisUnited States
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Otsuka Pharmaceutical Development & Commercialization...RecruitingAutosomal Recessive Polycystic Kidney (ARPKD)United States, United Kingdom, Belgium, Poland, France, Germany, Italy
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Murdoch Childrens Research InstituteUniversity of Sydney; Sydney Children's Hospitals Network; Women's and Children... and other collaboratorsActive, not recruitingAutosomal Recessive Disorder | X-Linked Genetic DiseasesAustralia
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Yale UniversityFoundation for Ichthyosis & Related Skin Types (FIRST)TerminatedIchthyosisUnited States
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Timber Pharmceuticals LLCCompletedCongenital IchthyosisUnited States, Australia
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Crown Laboratories, Inc.CompletedIchthyosis VulgarisUnited States
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Patagonia Pharmaceuticals, LLCCompletedCongenital IchthyosisUnited States
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Alkeus Pharmaceuticals, Inc.RecruitingStargardt Disease | Stargardt Macular Degeneration | Stargardt Macular Dystrophy | Autosomal Recessive Stargardt Disease 1 (ABCA4-related)United States
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Mayne Pharma International Pty LtdTerminatedLamellar IchthyosisUnited States, Spain, Canada, Germany, France, Australia, Israel, Ukraine, United Kingdom
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Northwestern UniversityIcahn School of Medicine at Mount Sinai; Galderma R&DRecruiting
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Yale UniversityTerminatedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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NYU Langone HealthCompletedKidney, Polycystic, Autosomal DominantUnited States
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The Rogosin InstituteWeill Medical College of Cornell University; New York Presbyterian HospitalWithdrawnAutosomal Dominant Polycystic Kidney DiseaseUnited States
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National Institute of Neurological Disorders and...Completed
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Weill Medical College of Cornell UniversityThe Rogosin InstituteEnrolling by invitationAutosomal Dominant Polycystic Kidney DiseaseUnited States
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AnaptysBio, Inc.Terminated
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The University of QueenslandRecruitingAutosomal Dominant Polycystic Kidney DiseaseAustralia
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Taipei Medical University Shuang Ho HospitalUniversity of Southern CaliforniaEnrolling by invitationChronic Kidney Diseases | Autosomal Dominant Polycystic Kidney DiseaseTaiwan
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Regulus Therapeutics Inc.CompletedPolycystic Kidney Disease, Autosomal DominantUnited States
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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The Rogosin InstituteWeill Medical College of Cornell UniversityCompletedAutosomal Dominant Polycystic KidneyUnited States
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Timber Pharmaceuticals Inc.Active, not recruitingIchthyosisUnited States, Canada, Germany, France, Italy
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NYU Langone HealthCompletedAnxiety Disorders | Familial Dysautonomia | Dysthymia | Paroxysmal Hypertension | Autosomal Recessive DiseaseUnited States
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Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
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Palladio BiosciencesCompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Australia, Belgium, Germany, Italy, Poland, Romania, United Kingdom, Argentina, Canada, France, Netherlands, Russian Federation
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Kadmon, a Sanofi CompanyCompletedAutosomal Dominant Polycystic Kidney | ADPKDUnited States
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedPolycystic Kidney Disease, Autosomal DominantUnited States, Belgium, United Kingdom, Russian Federation, France, Australia, Netherlands, Italy, Japan, Denmark, Romania, Poland, Canada, Argentina, Germany
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Argentina, Australia, Belgium, Brazil, Canada, Czech Republic, France, Germany, Italy, Japan, Netherlands, Norway, Poland, Romania, Spain, Sweden, Switzerland, Turkey, United Kingdom
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SanofiTerminatedCongenital Cystic Kidney DiseaseGermany, Spain, United States, Australia, Belgium, Japan, Korea, Republic of, Netherlands
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Johnson & Johnson Consumer Inc. (J&JCI)CompletedPruritus | IchthyosisUnited States
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Regulus Therapeutics Inc.RecruitingPolycystic Kidney, Autosomal Dominant | Autosomal Dominant Polycystic Kidney Disease | ADPKDUnited States
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Otsuka Pharmaceutical Development & Commercialization...CompletedChronic Kidney Disease | Autosomal Dominant Polycystic Kidney DiseaseAustralia, Belgium, Italy, Spain, Sweden, United States, Canada, Netherlands, Czechia, Poland, Germany, Russian Federation, Hungary, Israel, Puerto Rico, Argentina, Denmark, South Africa, United Kingdom, Norway, France, Romania
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The Rogosin InstituteWeill Medical College of Cornell University; Rockefeller UniversityCompletedChronic Kidney Disease | Polycystic Kidney, Autosomal DominantUnited States
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Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, Hungary, United Kingdom, Australia, Bulgaria, Poland, Turkey
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CephalonCompletedExcessive SleepinessUnited States
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Reata, a wholly owned subsidiary of BiogenTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, United Kingdom, Australia, France, Japan, Germany, Belgium, Czechia, Italy
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Icahn School of Medicine at Mount SinaiAllerganCompletedPost-operative Excessive ScarringUnited States
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedPolycystic Kidney, Autosomal DominantUnited States
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Genzyme, a Sanofi CompanyTerminatedPolycystic Kidney, Autosomal DominantBelgium, Germany, Czechia, United States, Italy, Poland, Argentina, Australia, Austria, Canada, China, Denmark, France, Israel, Japan, Korea, Republic of, Netherlands, Portugal, Romania, Spain, Taiwan, Turkey, United Kingdom
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Kadmon, a Sanofi CompanyCompletedPolycystic Kidney, Autosomal DominantUnited States
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Azitra Inc.Not yet recruiting
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Canada, Brazil, Taiwan, Singapore, South Africa, United Kingdom
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AbbottCompleted
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant Hypocalcemia (ADH)United States, Australia, United Kingdom, Denmark, Italy, France, Japan, Taiwan, Canada, Czechia, Netherlands
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State University of New York at BuffaloGeistlich Pharma AGCompletedPeriodontal DiseasesUnited States
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Inozyme PharmaActive, not recruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyUnited States, Canada, Germany, France, United Kingdom
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Otsuka Pharmaceutical Development & Commercialization...CompletedPolycystic Kidney, Autosomal DominantBelgium, Germany, Italy, Spain, Sweden, United States, Canada, Australia, Netherlands, Czechia, Poland, Denmark, Israel, Hungary, Russian Federation, South Africa, United Kingdom, Romania, Argentina, Norway
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Harmony Biosciences, LLCActive, not recruitingIdiopathic Hypersomnia | Excessive Daytime SleepinessUnited States
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant HypocalcemiaUnited States, France, Denmark, Australia, Japan, Belgium, Canada, Italy, Netherlands, United Kingdom, Portugal, Finland, Germany