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Clinical Trials on Best Vitelliform Macular Dystrophy
Total 777 results
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Seoul National University HospitalRecruitingDuchenne Muscular Dystrophy | Scoliosis Neuromuscular | Lordosis LumbarKorea, Republic of
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Assistance Publique - Hôpitaux de ParisRecherche Clinique Paris Descartes Necker Cochin Sainte Anne; AFM-Téléthon...Recruiting
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PTC TherapeuticsCooperative International Neuromuscular Research Group; The John Walton Muscular...Active, not recruitingMuscular Dystrophy, DuchenneGermany, France, United Kingdom, Brazil, Italy, Austria, Sweden, Czechia, Greece, Hungary, Israel, Latvia, Norway, Portugal, Romania, Slovenia
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BioMarin PharmaceuticalTerminatedMuscular DystrophiesUnited States, Canada
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Centre Hospitalier Universitaire de Saint EtienneÖrebro University, Sweden; Association Française contre les Myopathies (AFM)...CompletedMuscular Dystrophy, FacioscapulohumeralFrance
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University of BernUniversity Hospital Inselspital, Berne; University of Lausanne Hospitals; University... and other collaboratorsRecruitingCongenital Muscular Dystrophy | SMA | DMD | BMD | IMDSwitzerland
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University Hospital, BrestUnknownDuchenne Dystrophy MuscularFrance
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Sardocor Corp.Not yet recruitingDMD-Associated Dilated Cardiomyopathy
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Virginia Commonwealth UniversityWashington University School of Medicine; University of Iowa; University of Minnesota and other collaboratorsRecruitingMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, United Kingdom
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Sarepta Therapeutics, Inc.Active, not recruiting
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ML Bio Solutions, Inc.Virginia Commonwealth UniversityCompletedMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, Denmark
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Neurogen Brain and Spine InstituteWithdrawn
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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Radboud University Medical CenterRecruitingSELENON-related Myopathy | LAMA2-related Muscular DystrophyNetherlands
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University Hospital, CaenUniversity Hospital, Rouen; Centre Hospitalier Universitaire, Amiens; University... and other collaboratorsTerminatedMuscular Dystrophy, Oculopharyngeal | PtosisFrance
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Murdoch Childrens Research InstituteCompletedFacio-Scapulo-Humeral Dystrophy | FSHD2 | FSHD1Australia
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Sarepta Therapeutics, Inc.Active, not recruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
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Assistance Publique - Hôpitaux de ParisRecruitingLimb Girdle Muscular DystrophiesFrance
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Nationwide Children's HospitalRecruiting
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Istanbul University - Cerrahpasa (IUC)CompletedFacio-Scapulo-Humeral DystrophyTurkey
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CHU de ReimsCompletedMyotonic Dystrophy Type 1 (DM1)France
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Ascidian Therapeutics, IncRecruitingStargardt Disease | Stargardt Disease 1 | Juvenile Macular Degeneration | Cone Rod DystrophyUnited States
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States, Brazil, Belgium, Canada, Germany, Italy, Spain, Sweden, Turkey, United Kingdom
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Sarepta Therapeutics, Inc.Nationwide Children's HospitalCompleted
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IRCCS San Camillo, Venezia, ItalyCompletedMyotonic Dystrophy Type 1 (DM1)
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Rigshospitalet, DenmarkCompletedSpinal Muscular Atrophy | Merosin Deficient Congenital Muscular DystrophyDenmark
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Medical University of BialystokUnknownIncrease Muscle Strength in Patients With Muscular DystrophyPoland
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Cure CMDCompletedCongenital Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States, Canada, Argentina, Australia, Israel, Italy
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Assistance Publique - Hôpitaux de ParisNot yet recruitingLimb Girdle Muscular Dystrophy
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Food and Drug Administration (FDA)National Eye Institute (NEI)RecruitingAge-Related Macular Degeneration | Retinal Degeneration | Retinitis Pigmentosa | Usher Syndromes | Cone Dystrophy | Rod Dystrophy | Cone Rod Dystrophy | Hydroxychloroquine Retinopathy | Late-Onset Retinal Degeneration | Rod Cone DystrophyUnited States
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Ohio State UniversityGilead SciencesCompletedMyotonic Dystrophy 1 | Myotonia Congenita | Paramyotonia CongenitaUnited States
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Radboud University Medical CenterCompletedMDC1A | SELENON-related MyopathyNetherlands
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Gokce Yagmur Gunes GencerHacettepe UniversityCompletedMuscular Dystrophy, Duchenne | Upper Extremity | Respiratory FunctionsTurkey
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Bahçeşehir UniversityNot yet recruitingDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Healthy Individuals
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LMU KlinikumRecruitingMyasthenia Gravis | Myotonic Dystrophy | Inclusion Body Myositis | Facioscapulohumeral Muscular Dystrophies | The Falls Efficacy Scale International | The Morse Fall ScaleGermany
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Swiss Federal Institute of TechnologyCompletedMuscle Weakness | Muscular Dystrophies | Muscular Dystrophy | Muscular Dystrophy, Facioscapulohumeral | Scapular Dyskinesis | Muscular WeaknessGermany, Switzerland
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The Cleveland ClinicNational Eye Institute (NEI)CompletedRetinal Detachment | Epiretinal Membrane | Fuchs Endothelial Dystrophy | Macular HoleUnited States
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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ARTHEx Biotech S.L.Recruiting
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Arrowhead PharmaceuticalsRecruitingMyotonic Dystrophy 1New Zealand, Australia
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Istituto Auxologico ItalianoFondazione Serena Onlus - Centro Clinico NeMO MilanoCompletedMyotonic Dystrophy 1Italy
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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Indiana University School of MedicineMuscular Dystrophy AssociationCompletedMuscular Dystrophy | Arrhythmia | Sudden Cardiac DeathUnited States
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Pitié-Salpêtrière HospitalRecruitingLaminopathies | EmerinopathiesFrance
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Merve KurtRecruitingDuchenne Muscular Dystrophy | Virtual Reality | Spinal Muscular Atrophy | Neuromuscular Disease | BiofeedbackTurkey
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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Huashan HospitalEnrolling by invitation