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Clinical Trials on Beta-ketothiolase Deficiency
Total 9478 results
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National Institute of Diabetes and Digestive and...Completed
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States
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Groupe Hospitalier Paris Saint JosephActive, not recruitingAllergic Reaction | Beta Lactam Adverse ReactionFrance
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Washington University School of MedicineCompleted
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University Hospital, LimogesActive, not recruitingHepatocyte Nuclear Factor 1-betaFrance
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Tanta UniversityCompletedBeta Thalassemia MajorEgypt
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Novartis PharmaceuticalsCompletedIron Overload | Hemosiderosis | Beta-thalassemia Major | Rare AnemiaEgypt, Oman, Saudi Arabia, Syrian Arab Republic, Lebanon
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National Institute of Diabetes and Digestive and...CompletedBeta Thalassemia | HemoglobinopathyUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingMalaria | Sickle Cell Disease | Alpha and Beta Thalassemia | Human PhysiologyUnited States
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Nova Laboratories LimitedCompletedSickle Cell Disease | Sickle Cell Hemoglobin C | Sickle Cell-beta-thalassemia | Sickle-Cell; Hemoglobin Disease, ThalassemiaUnited Kingdom, Jamaica
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Tanta UniversityCompletedBeta Thalassemia MajorEgypt
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404 General Military Hospital, LarissaUnknownCoronary Artery Disease | Beta-Thalassemia TraitGreece
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Iron Overload | Hemoglobinopathies | Thalassemia | Beta-Thalassemia | Hemochromatosis | Anemia (Iron-Loading)
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Bioray LaboratoriesXiangya Hospital of Central South University; First Affiliated Hospital of... and other collaboratorsEnrolling by invitation
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Imara, Inc.Terminatedβ ThalassemiaIsrael, France, Malaysia, Turkey, Denmark, Georgia, Greece, Italy, Lebanon, Morocco, Netherlands, Tunisia, United Kingdom
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Acceleron Pharma Inc. (a wholly owned subsidiary...CompletedB-ThalassemiaItaly, Greece
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Genzyme, a Sanofi CompanyCompletedCerebroside Lipidosis Syndrome | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease Type I | Clucocerebrosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States
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Institute of Hematology & Blood Diseases Hospital...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingThalassemia Major | Thalassemia, BetaChina
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Children's Hospital KarachiCompleted
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Shiraz University of Medical SciencesCompletedImmune AbnormalitiesIran, Islamic Republic of
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Greenwood Genetic CenterCompletedGalactosialidosis | Sialidosis | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Beta Mannosidosis | Mucolipidosis II | Mucolipidosis III | Schindler DiseaseUnited States
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University Hospital, Basel, SwitzerlandRecruitingInfection With AmpC Beta-lactamase Producing EnterobacteralesSwitzerland
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University of Geneva, SwitzerlandUniversity Hospital, GenevaRecruitingEfficacy | Toxicity | Beta-lactam Antibiotics | Therapeutic Drug Monitoring | Ceftazidime | Amoxicillin | Meropenem | Imipenem | Piperacillin | Flucloxacillin | CefepimeSwitzerland
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CorrectSequence Therapeutics Co., LtdRecruitingBeta-Thalassemia MajorChina
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Ain Shams UniversityCompleted
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First Affiliated Hospital of Guangxi Medical UniversityUnknown
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CelgeneRecruitingBeta-thalassemia | Myelodysplastic Syndromes (MDS) | Myeloproliferative Neoplasm(MPN)-Associated MyelofibrosisUnited States, Japan, United Kingdom, Turkey, Greece, France, Australia, Belgium, Bulgaria, Canada, Germany, Israel, Italy, Malaysia, Spain, Sweden, Taiwan, Thailand, Tunisia, Lebanon, China, Netherlands
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Beta-ThalassemiaHungary
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Ain Shams UniversityRecruitingHCV Infection | Beta Thalassemia MajorEgypt
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Tanta UniversityUnknownStudy of The Therapeutic Benefits of Al-hijamah in Children With Beta Thalassemia Major (Al-hijamah)AL-Hijama in Thalassmia MajorEgypt
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University Hospital, MontpellierInstitut de Génomique Fonctionnelle (IGF) de MontpellierNot yet recruitingDepression | Suicide | Beta EndorphinFrance
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Kaleido BiosciencesTerminatedVancomycin-Resistant Enterococcus, Extended-Spectrum Beta Lactamase-Producing Enterobacteriaceae, or Carbapenem-Resistant Enterobacteriaceae Colonized SubjectsUnited States
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University of PennsylvaniaWashington University School of MedicineCompleted
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Kanglin Biotechnology (Hangzhou) Co., Ltd.Not yet recruitingTransfusion-dependent Beta-ThalassemiaChina
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Meir Medical CenterCompletedBeta-lactam AllergyIsrael
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Rigshospitalet, DenmarkUnknownCarbohydrate Metabolism, Inborn Errors | Metabolism, Inborn Errors | Lipid Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease Type V | VLCAD Deficiency | Glycogen Storage Disease Type III | Phosphoglycerate Kinase Deficiency | Neutral Lipid Storage Disease | Carnitine... and other conditionsDenmark
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Anemia | Beta ThalassemiaUnited States
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Columbia UniversityActive, not recruitingSickle Cell Disease | Beta ThalassemiaUnited States
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Azienda Ospedaliera V. CervelloCompletedBeta-Thalassemia | Thalassemia MajorItaly
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Antonio Martín DuceCompletedPain | Hernia Surgery | Beta-endorphin | DipyroneSpain
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University of ThessalyCompletedDiabetes Mellitus, Type 2 | Insulin Resistance | PreDiabetes | Beta-ThalassemiaGreece
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Chelsea TherapeuticsCompletedNeurogenic Orthostatic Hypotension | Primary Autonomic Failure | Dopamine Beta Hydroxylase Deficiency | Non-Diabetic Neuropathy
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Memorial Sloan Kettering Cancer CenterRecruitingSickle Cell Disease | Thalassemia | Thalassemia, BetaUnited States
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Imperial College LondonCompletedPharmacokinetics | Penicillin Allergy | Beta Lactam Adverse ReactionUnited Kingdom
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Tanta UniversityCompletedHepatitis C | Beta-ThalassemiaEgypt
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Tanta UniversityCompletedBeta Thalassemia MajorEgypt
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Ain Shams UniversityUnknownSickle Cell Disease | Beta-thalassemia Major | Iron HemosiderosisEgypt
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bluebird bioCompletedSickle Cell Disease | Beta-Thalassemia MajorFrance
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Nemours Children's ClinicWithdrawnSafety of Long Acting Beta Agnoists