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Clinical Trials on beta-Thalassemia in United Kingdom
Total 215 results
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Protagonist Therapeutics, Inc.CompletedChronic Anemia | β-thalassemia | Ineffective ErythropoiesisUnited States, Malaysia, Turkey, Thailand, United Kingdom, Italy, Lebanon, Tunisia, Greece
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Paul SzabolcsRecruitingSickle Cell Anemia | Diamond-blackfan Anemia | Beta-thalassemia MajorUnited States
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Sangamo TherapeuticsEnrolling by invitationBlood and Lymphatic DiseasesUnited States
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National Heart, Lung, and Blood Institute (NHLBI)National Institutes of Health Clinical Center (CC); National Cancer Institute...RecruitingStem Cell Transplantation | Sickle Cell Disease | Thalassemia | Graft vs Host DiseaseUnited States
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bluebird bioCompletedβ-thalassemia MajorUnited States, Australia, Thailand
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Memorial Sloan Kettering Cancer CenterActive, not recruitingConfirmed Diagnosis of ß-thalassemia MajorUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoUnknown
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Weill Medical College of Cornell UniversityUnknownThalassemia MajorUnited States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Thalassemia Clinical Research...CompletedHematologic Diseases | Iron Overload | Hypertension, Pulmonary | Osteoporosis | Thalassemia | Beta-Thalassemia | Anemia, Cooley'sUnited States, Canada
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DisperSol Technologies, LLCCompletedThalassemia MajorThailand, United States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedThalassemiaUnited States, Canada
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Dana-Farber Cancer InstituteTehran University of Medical SciencesCompletedThalassemia MajorUnited States, Iran, Islamic Republic of
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Novartis PharmaceuticalsCompletedTransfusional Iron Overload in β-thalassemiaUnited States, Greece, Argentina, Germany, Belgium, Italy, United Kingdom, France, Tunisia, Canada, Turkey, Brazil
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University of California, San FranciscoCalifornia Institute for Regenerative Medicine (CIRM)Enrolling by invitationHemoglobinopathies | Alpha Thalassemia Major | Thalassemia Major | Fetal Hydrops | Hemoglobinopathy; With Thalassemia | Fetal Anemia | Alpha; Thalassemia | Thalassemia Alpha | A-ThalassemiaUnited States
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National Institute of Allergy and Infectious Diseases...TerminatedAnemia, Sickle Cell | Hemoglobinopathies | Thalassemia | Hemoglobin SC Disease | Thalassemia MajorUnited States
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Timothy OlsonActive, not recruitingSickle Cell Disease | Thalassemia MajorUnited States
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Children's Hospital of PhiladelphiaAnn & Robert H Lurie Children's Hospital of Chicago; The Cooley's Anemia Foundation...CompletedThalassemia Major With Severe Transfusional Iron OverloadUnited States
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Novartis PharmaceuticalsCompletedAnemia | HemosiderosisUnited States, Germany, Belgium, United Kingdom, Italy, Canada, France
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Mitchell CairoRecruitingHodgkin Lymphoma | Sickle Cell Disease | Acute Leukemia | Beta-Thalassemia | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Diamond Blackfan Anemia | Amegakaryocytic Thrombocytopenia | KostmannUnited States
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UCSF Benioff Children's Hospital OaklandNovartis PharmaceuticalsCompletedTHALASSEMIA MAJORUnited States
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States
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New York Medical CollegeCompletedLymphoma | Leukemia | Sickle Cell Disease | Histiocytosis | Immunodeficiencies | Inborn Errors of Metabolism | Bone Marrow Failure | Beta ThalassemiaUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Invenux, LLCState University of New York - Downstate Medical CenterActive, not recruitingSickle Cell Disease | Sickle-Beta Zero ThalassemiaUnited States
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Fairview University Medical CenterCompletedNeutropenia | Sickle Cell Anemia | Red-Cell Aplasia, Pure | Thalassemia MajorUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Imara, Inc.Quintiles, Inc.CompletedSickle Cell Disease | Sickle Beta 0 Thalassemia | Sickle-Cell; Hb-SCUnited States
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Boston Children's HospitalNovartisCompletedSickle Cell Disease | Thalassemia Major | Transfusion-dependent HemachromatosisUnited States
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Anemia | Sickle Cell-Beta0-ThalassemiaUnited States
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Columbia UniversityCompletedMyelodysplastic Syndromes | Sickle Cell Disease | Aplastic Anemia | Transfusional Iron Overload | Thalassemia MajorUnited States
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Imperial College LondonCompletedPharmacokinetics | Penicillin Allergy | Beta Lactam Adverse ReactionUnited Kingdom
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Thomas Jefferson UniversityGlaxoSmithKline; Drexel UniversityUnknownQuality of Life | Inflammation | Sickle Cell Disease | HEMOGLOBIN SS | Hemoglobin S Beta-0 ThalassemiaUnited States
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Vanderbilt University Medical CenterWashington University School of Medicine; University of Alabama at BirminghamRecruitingStroke | Sickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Thalassemia | Sickle Cell-Beta0-ThalassemiaUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingSickle Cell Disease | Severe Congenital Neutropenia | Paroxysmal Nocturnal Hemoglobinuria | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Diamond Blackfan Anemia | Transfusion Dependent Alpha- or Beta- Thalassemia | Non-Malignant Hematologic DisordersUnited States
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Brown UniversityNational Institute of General Medical Sciences (NIGMS)Recruiting
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Vanderbilt University Medical CenterMedical College of Wisconsin; VersitiCompletedSickle Cell Anemia (HbSS, or HbSβ-thalassemia0)United States
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Vanderbilt UniversityApproved for marketing
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National Institute of Allergy and Infectious Diseases...Recruiting
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Novartis PharmaceuticalsCompletedNon-transfusion Dependent ThalassemiaThailand, Turkey, Italy, Greece, China, United Kingdom, Lebanon, Tunisia
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Newcastle-upon-Tyne Hospitals NHS TrustNewcastle University; DSM Nutritional Products, Inc.CompletedVitamin A Deficiency | Beta-carotene BioavailabilityUnited Kingdom
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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Imperial College LondonCompletedAtrial Fibrillation | Cardiac Arrest | Brugada Syndrome | Athletes Heart | Ventricular Ectopic BeatUnited Kingdom
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Hartford HospitalWithdrawnBeta-CaryophylleneUnited States
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Agios Pharmaceuticals, Inc.Active, not recruitingThalassemiaUnited States, Canada, United Kingdom
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Novartis PharmaceuticalsCompletedNon-transfusion Dependent ThalassemiaGreece, Taiwan, Italy, United Kingdom, Lebanon, Turkey, Malaysia, Thailand, United States
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Washington University School of MedicineCompleted
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Catherine BollardChildren's National Research InstituteActive, not recruitingThalassemia | Sickle Cell-thalassemia DiseaseUnited States
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University of PennsylvaniaWashington University School of MedicineCompleted