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- US Clinical Trials Registry
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Clinical Trials on Bietti's Crystalline Dystrophy in United States
Total 607 results
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Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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Retrotope, Inc.Active, not recruitingInfantile Neuroaxonal DystrophyUnited States
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University of UtahCompletedMacular Dystrophy, CornealUnited States
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Virginia Commonwealth UniversityEdgewise Therapeutics, Inc.RecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Muscular Dystrophy in Children | Muscular Dystrophy, BeckerUnited States, New Zealand, United Kingdom
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Hugo W. Moser Research Institute at Kennedy Krieger...Concord Hospital; FSHD Global Research FoundationCompletedFacioscapulohumeral Muscular DystrophyUnited States, Australia
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Red Nucleus Enterprise Solutions, LLCRecruiting
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Virginia Commonwealth UniversityNorthwestern University; University of RochesterRecruitingDuchenne Muscular DystrophyUnited States
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University of FloridaRecruiting
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Phrixus Pharmaceuticals, Inc.Charley's FundTerminated
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Children's Hospital Medical Center, CincinnatiIpsen; Charley's FundCompletedDuchenne Muscular DystrophyUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedDuchenne Muscular DystrophyUnited States
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National Human Genome Research Institute (NHGRI)Completed
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Kevin FlaniganWithdrawnDuchenne Muscular DystrophyUnited States
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Alan Neuromedical Technologies, LLCCompleted
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Cooperative International Neuromuscular Research...United States Department of DefenseTerminated
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Trefoil Therapeutics, Inc.CompletedCorneal Endothelial DystrophyUnited States
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PYC TherapeuticsRecruitingRetinal Dystrophy | PRPF31 Mutationassociated Retinal Dystrophy | RP11United States
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Hoffmann-La RocheActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, United Kingdom, Italy, Denmark
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Denmark, Italy
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Not yet recruiting
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
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Massachusetts General HospitalBoston Children's HospitalRecruitingDuchenne Muscular DystrophyUnited States
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University of PittsburghRecruitingDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Cure Rare Disease, IncUniversity of Massachusetts, WorcesterActive, not recruiting
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Craig McDonald, MDCardero Therapeutics, Inc.Completed
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University of FloridaEngage Health Inc.CompletedDuchenne Muscular DystrophyUnited States
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University of FloridaCureDuchenneCompletedMuscular Dystrophy, DuchenneUnited States
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University of FloridaUnited States Department of DefenseCompletedDuchenne Muscular DystrophyUnited States
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Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDuchenne Muscular DystrophyUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical CenterCompletedDuchenne Muscular DystrophyUnited States
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Kowa Research Institute, Inc.CompletedFuchs' Endothelial Corneal DystrophyUnited States, Australia, Germany, Spain, Denmark
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterCompletedBecker Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterTerminatedMuscular DystrophyUnited States
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Cedars-Sinai Medical CenterParent Project Muscular DystrophyCompleted
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Cedars-Sinai Medical CenterCompleted
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Cedars-Sinai Medical CenterMuscular Dystrophy AssociationCompleted
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National Center for Research Resources (NCRR)Children's National Research InstituteCompletedMuscular Dystrophy, DuchenneUnited States
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Cooperative International Neuromuscular Research...United States Department of DefenseCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Japan, Canada
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Cedars-Sinai Medical CenterCompleted
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Hoffmann-La RocheNot yet recruitingDuchenne Muscular DystrophyUnited States
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National Institute of Neurological Disorders and...CompletedMuscular Dystrophy | Muscular DiseaseUnited States
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedLimb-Girdle Muscular DystrophyUnited States
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EmmecellActive, not recruitingEndothelial Dysfunction | Corneal Edema | Fuchs Dystrophy | Corneal Endothelial Dystrophy | Bullous Keratopathy | Pseudophakic Bullous Keratopathy | Corneal Endothelial Dysfunction | Fuchs Endothelial Corneal Dystrophy | Moderate Corneal Endothelial DecompensationUnited States
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Astellas Pharma IncTerminatedDuchenne Muscular Dystrophy (DMD)United States
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Medpace, Inc.CompletedBecker Muscular DystrophyUnited States
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Kevin FlaniganSarepta Therapeutics, Inc.Completed