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Clinical Trials on Birt-Hogg-Dube Syndrome in New Zealand
Total 851 results
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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ONYCompletedRespiratory Distress SyndromeUnited States
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Massachusetts General HospitalNational Heart, Lung, and Blood Institute (NHLBI)CompletedCritical Illness | Vitamin D Deficiency | Acute Respiratory Distress SyndromeUnited States
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, United Kingdom, Canada, Germany
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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University of Central FloridaNational Institute on Deafness and Other Communication Disorders (NIDCD); University...CompletedDown Syndrome | Speech Sound Disorder | Speech Disorders in Children | Speech Intelligibility | Speech and Language DisorderUnited States
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Newron Pharmaceuticals SPATerminatedRett SyndromeUnited States, India, United Kingdom, Australia, Italy
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ADMA Biologics, Inc.CompletedPrimary Immune Deficiency DisorderUnited States
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AlbireoActive, not recruitingAlagille SyndromeUnited Kingdom, United States, France, Germany, Netherlands, Italy, Belgium, Malaysia, Poland, Turkey
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NYU Langone HealthNational Institutes of Health (NIH)CompletedObsessive-Compulsive Disorder | Tourette Syndrome | Tic DisordersUnited States
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Weill Medical College of Cornell UniversityUniversity of Alabama at BirminghamCompletedTourette Disorder | Chronic Tic DisorderUnited States
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Northwestern UniversityIcahn School of Medicine at Mount SinaiCompletedNetherton Syndrome | Ichthyosis | Lamellar Ichthyosis | Autosomal Recessive Congenital Ichthyosis | Congenital Ichthyosiform Erythroderma | Epidermolytic IchthyosisUnited States
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Baxalta now part of ShireCompletedPrimary Immunodeficiency Diseases (PID)United States
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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ACADIA Pharmaceuticals Inc.Completed
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Zafgen, Inc.TerminatedObesity | Prader-Willi SyndromeUnited States
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Stockton UniversityNova Southeastern UniversityCompletedCommon Variable Immunodeficiency | Hypergammaglobulinemia | Primary Immune Deficiency Disorder | Specific Antibody DeficiencyUnited States
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Dartmouth-Hitchcock Medical CenterGenentech, Inc.TerminatedVon Hippel Lindau Disease | HemangioblastomasUnited States
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Teva Branded Pharmaceutical Products R&D, Inc.Nuvelution TS Pharma, Inc.CompletedTourette SyndromeUnited States, Canada, Denmark, Russian Federation, Serbia, Spain
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
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Tetra Discovery PartnersEnrolling by invitationFragile X SyndromeUnited States
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Switzerland, Germany, Australia, Canada, Denmark, France, Italy, Spain, United Kingdom
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University of MinnesotaBill and Melinda Gates FoundationCompletedAcute Respiratory Distress Syndrome | Corona Virus Infection | SARS-CoV InfectionUnited States
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Natera, Inc.Houston Perinatal Associates; Lyndhurst Clinical Research; Dr. Carpenter Maternal... and other collaboratorsCompletedTrisomy 21 | Trisomy 18 | Trisomy 13 | Sex Chromosome AbnormalitiesUnited States, India, Malaysia
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Natera, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsTerminatedAneuploidy | Trisomy 21 | Trisomy 18 | Trisomy 13United States, Ireland, Canada, Italy, Korea, Republic of, Spain
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
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Jazz PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Spain, Italy, United Kingdom
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NYU Langone HealthNovartis Pharmaceuticals; The Children's Tumor FoundationCompletedNeurofibromatosis Type IIUnited States
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Adrianna Vlachos, MDTerminatedPure Red Cell Aplasia | Diamond Blackfan AnemiaUnited States
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Emalex Biosciences Inc.CompletedTourette SyndromeUnited States, Poland, France, Canada, Germany
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Gary M Brittenham, MDCompletedVitamin D Deficiency | Asthma | Sickle Cell Disease | Acute Chest Syndrome | Respiratory InfectionsUnited States
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The Children's Tumor FoundationRecruitingNeurofibromatosis 1 | Neurofibromatosis 2 | SchwannomatosisUnited States
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NYU Langone HealthBayer Healthcare Pharmaceuticals, Inc./Bayer Schering PharmaTerminatedneurofibromatosis1 (NF1) | Recurrent or Progressive Optic Pathway Gliomas (OPG) | Recurrent or Progressive Low-grade GliomaUnited States
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Marinus PharmaceuticalsCompletedTuberous SclerosisUnited States
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KalVista Pharmaceuticals, Ltd.TerminatedAngioedema, Hereditary, Types I and IIUnited States, Czechia, Germany, Hungary, Italy, North Macedonia, United Kingdom, Australia, Bulgaria, Canada, France, New Zealand, Puerto Rico
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Dartmouth-Hitchcock Medical CenterTerminatedAcute Coronary Syndrome | Pulmonary Hypertension | Congenital Heart Disease | Valvular Heart Disease | Pulmonary Embolism | Congestive Heart FailureUnited States
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NICHD Neonatal Research NetworkEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedInfant, Newborn, Diseases | Early Onset Neonatal Sepsis | Early-Onset MeningitisUnited States
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
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Carelon ResearchNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedDown Syndrome | Congenital Heart DiseaseUnited States, Canada
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Neuren Pharmaceuticals LimitedCompleted
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Jazz PharmaceuticalsGW PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Canada, Italy, Spain, United Kingdom, Australia
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Eisai Inc.PfizerTerminated
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Icahn School of Medicine at Mount SinaiNational Institute for Occupational Safety and Health (NIOSH/CDC)CompletedCardiovascular Disease | Obstructive Sleep Apnea | Pulmonary Disease | Cardiac Disease | Cardiopulmonary DiseaseUnited States
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National Cancer Institute (NCI)RecruitingDown Syndrome | B Acute Lymphoblastic Leukemia | B Lymphoblastic LymphomaUnited States, Canada, Puerto Rico, Australia, New Zealand
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National Hospital Organization Nagoya Medical CenterRecruitingAcute Lymphoblastic Leukemia | Down Syndrome | Childhood CancerTaiwan, Thailand, Hong Kong, Singapore, Malaysia, Japan
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Roswell Park Cancer InstituteNational Cancer Institute (NCI); Teva Pharmaceutical Industries, Ltd.TerminatedAcute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic Syndrome | Adult Acute Megakaryoblastic Leukemia (M7) | Adult Acute Minimally Differentiated Myeloid Leukemia (M0) | Adult Acute Monoblastic Leukemia (M5a) | Adult Acute Monocytic Leukemia (M5b) | Adult Acute Myeloblastic... and other conditionsUnited States
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AstraZenecaCompletedPuberty, Precocious | McCune-Albright SyndromeItaly, United States, Germany, France, Russian Federation, United Kingdom
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Gynecologic Oncology GroupNational Cancer Institute (NCI)CompletedOsteoporosis | Ovarian Carcinoma | Hereditary Breast and Ovarian Cancer SyndromeUnited States
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Eisai Inc.PfizerCompleted
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Natera, Inc.RecruitingPregnancy Complications | Twin to Twin Transfusion Syndrome | Multiple Gestation; Maternal CareUnited States