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Clinical Trials on Birt-Hogg-Dube Syndrome in New Zealand
Total 851 results
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NYU Langone HealthCompletedNeurofibromatosis Type 2 | Vestibular SchwannomasUnited States
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NYU Langone HealthCompletedNeurofibromatosis Type 2 | Meningiomas | Vestibular SchwannomasUnited States
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C. R. BardCompletedPeripheral Vascular Disease | Venous Disease | May-Thurner Syndrome | Iliofemoral Occlusive DiseaseUnited States, Australia, Germany, Ireland, Netherlands, Spain, United Kingdom
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Vesper Medical, Inc.Active, not recruitingDeep Vein Thrombosis | Chronic Venous Insufficiency | May-Thurner SyndromeUnited States, Poland
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Baxalta now part of ShireCompleted
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Memorial Sloan Kettering Cancer CenterPfizer; Dana-Farber Cancer Institute; University of Pittsburgh; University of VirginiaCompletedNeurofibromatosis | Meningioma | CNS Cancer | Hemangioblastoma | Intracranial HemangiopericytomaUnited States
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Hoffmann-La RocheCompleted
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Brazil, Canada, France, Germany, Hungary, Israel, Italy, Netherlands, South Africa, Spain, United Kingdom
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Bellicum PharmaceuticalsActive, not recruitingStudy of Gene Modified Donor T-cells Following TCR Alpha Beta Positive Depleted Stem Cell TransplantLymphoma, Non-Hodgkin | Myelodysplastic Syndromes | Acute Lymphoblastic Leukemia | Anemia, Aplastic | Primary Immune Deficiency Disorder | Cytopenia | Osteopetrosis | Leukemia, Acute Myeloid (AML), Child | Hemoglobinopathy in ChildrenUnited States
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The University of New South WalesRecruitingHealthy | Obstructive Sleep Apnea | Cystic Fibrosis | Hirschprung's DiseaseAustralia
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NYU Langone HealthDyax Corp.WithdrawnHereditary Angioedema Types I and IIUnited States
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Ritter Pharmaceuticals, Inc.CompletedLactose IntoleranceUnited States
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Michio HiranoSanthera PharmaceuticalsCompletedMELAS SyndromeUnited States
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NYU Langone HealthGlaxoSmithKlineCompletedNeurofibromatosis 2 | Vestibular SchwannomaUnited States
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Cyprium Therapeutics, Inc.Enrolling by invitation
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Roche Sequencing SolutionsPerinatal Quality Foundation: Nuchal Translucency Quality ReviewCompletedTrisomy 21United States, Belgium, Netherlands, Sweden, Italy, Canada
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Israel, Spain, Italy, United Kingdom, Netherlands, Canada, Hungary, Sweden, France, Norway, Portugal, Slovakia
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Gordon BernardTerminatedInfluenza | Acute Respiratory Distress Syndrome | H1N1 InfluenzaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedMarfan Syndrome | Turner Syndrome | Ehlers-Danlos Syndrome | Loeys-Dietz Syndrome | Shprintzen-Goldberg Syndrome | FBN1, TGFBR1, TGFBR2, ACTA2 or MYH11 Genetic Mutation | Bicuspid Aortic Valve Without Known Family History | Bicuspid Aortic Valve With Family History | Bicuspid Aortic Valve With Coarctation and other conditionsUnited States
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University of Southern CaliforniaNational Institute on Aging (NIA); Alzheimer's Therapeutic Research Institute; Alzheimer's Clinical Trials ConsortiumRecruitingDementia | Alzheimer Disease | Down SyndromeUnited States, Spain, United Kingdom
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SCAD AlliancePERFUSE Study GroupRecruitingSpontaneous Coronary Artery DissectionUnited States, Australia
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Gary M Brittenham, MDActive, not recruitingRespiratory Tract Infections | Respiratory Tract Diseases | Respiration Disorders | Lung Diseases | Nutrition Disorders | Vitamin D Deficiency | Asthma | Sickle Cell Disease | Anemia, Sickle Cell | Anemia, Hemolytic, Congenital | Acute Chest Syndrome | Deficiency Diseases VitaminUnited States
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Recurrent Childhood Pilocytic Astrocytoma | Recurrent Childhood Visual Pathway GliomaUnited States, Canada, Australia, New Zealand
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Montefiore Medical CenterUniversity of California, Los Angeles; University of Michigan; Duke UniversityCompletedAcute Respiratory Distress Syndrome | Acute Respiratory Failure | Acute Respiratory Failure With HypoxiaUnited States
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Enyo PharmaRecruitingAlport SyndromeGermany, Spain, United States, France
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Brazil
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Chiesi Farmaceutici S.p.A.CompletedSevere Combined Immunodeficiency | Adenosine Deaminase DeficiencyUnited States
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Reata, a wholly owned subsidiary of BiogenCompletedAlport SyndromeUnited States, United Kingdom, Japan, Australia, France, Germany, Puerto Rico, Spain
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Teva Branded Pharmaceutical Products R&D, Inc.Nuvelution TS Pharma, Inc.TerminatedTourette SyndromeUnited States, Argentina, Australia, Canada, Colombia, Denmark, Hungary, Italy, Korea, Republic of, Mexico, Poland, Russian Federation, Serbia, Spain, Ukraine
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National Human Genome Research Institute (NHGRI)CompletedMelanoma | Breast Neoplasm | Ovarian Neoplasm | Hereditary Neoplastic SyndromeUnited States, Finland, Iceland, Sweden
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Leadiant Biosciences, Inc.CompletedSevere Combined Immunodeficiency | ADA-SCID | Adenosine Deaminase DeficiencyUnited States
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Bellus Health IncFDA Office of Orphan Products DevelopmentCompletedGastrointestinal Diseases | Kidney Diseases | Rheumatoid Arthritis | Nephrotic Syndrome | Secondary (AA) Amyloidosis | Familial Mediterranean SyndromeUnited States, Israel, Finland, France, Italy, Lithuania, Netherlands, Poland, Russian Federation, Spain, Turkey, United Kingdom
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BioMarin PharmaceuticalApproved for marketingMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, Puerto Rico
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Millendo Therapeutics SASTerminatedHyperphagia | Prader-Willi SyndromeUnited States, Belgium, Spain, France, Italy, United Kingdom, Australia, Netherlands
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompletedPrimary Immunodeficiency Diseases (PID)United States
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NYU Langone HealthRecruitingHereditary Sensory and Autonomic Neuropathies | Familial Dysautonomia (Riley-Day Syndrome) | Hereditary Sensory and Autonomic Neuropathy 3United States, Israel
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Mirum Pharmaceuticals, Inc.Active, not recruitingCholestatic Liver Disease | Alagille Syndrome | Progressive Familial Intrahepatic CholestasisUnited States, United Kingdom, France, Belgium, Poland, Brazil, Mexico
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Kinevant Sciences GmbHRoivant Sciences, Inc.Completed
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Seaside Therapeutics, Inc.Completed
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University of New MexicoUniversity of California, San FranciscoRecruitingCerebral Cavernous MalformationUnited States
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National Cancer Institute (NCI)CompletedRecurrent Fallopian Tube Carcinoma | Recurrent Ovarian Carcinoma | Recurrent Primary Peritoneal Carcinoma | Breast Carcinoma | Ovarian Carcinoma | Pancreatic Carcinoma | Prostate Carcinoma | Recurrent Breast Carcinoma | Estrogen Receptor Negative | HER2/Neu Negative | Progesterone Receptor Negative | Triple-Negative... and other conditionsUnited States
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Kirby InstituteGilead Sciences; Melanoma Institute Australia; St Vincent's Hospital, Sydney; Royal... and other collaboratorsActive, not recruitingCOVID-19 | Cancer | Primary Immune Deficiency Disorder | HIV-1-infection | Immunosuppression DisordersAustralia
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University of RochesterCompletedCharcot Marie Tooth DiseaseUnited States
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New York Medical CollegeJohns Hopkins University; Children's Hospital of Philadelphia; Medical College... and other collaboratorsRecruitingPrimary Immune Deficiency Disorder | Viral InfectionUnited States
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Maria I. NewNational Center for Research Resources (NCRR); Office of Rare Diseases (ORD)Completed21-hydroxylase DeficiencyUnited States, Brazil
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingDown Syndrome | Myeloid Leukemia Associated With Down Syndrome | B Acute Lymphoblastic Leukemia Associated With Down SyndromeUnited States
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ADMA Biologics, Inc.Active, not recruitingPrimary Immune Deficiency DisorderUnited States
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Columbia UniversityCompletedSarcoma | Lymphoma | Kidney Cancer | Leukemia | Neurotoxicity | Peripheral NeuropathyUnited States