- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Birth Injuries
Total 56208 results
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Sidney Kimmel Comprehensive Cancer Center at Johns...National Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative DiseasesUnited States
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University of AarhusCompletedCardiovascular Disease | Diabetes | Metabolic Syndrome | Osteoporosis | Klinefelter SyndromeDenmark
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Oslo University HospitalUniversity of Oslo; Lovisenberg Diakonale HospitalRecruitingQuality of Life | Sleep Apnea, Obstructive | Sleep Apnea | Surgery | Pediatric Disorder | Laryngomalacia | Ear, Nose and Throat DisorderNorway
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PYC TherapeuticsNot yet recruitingAutosomal Dominant Optic Atrophy | Kjer Optic Atrophy | OPA1 Gene Mutation | Hereditary Optic Atrophies
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Hacettepe UniversityRecruitingQuality of Life | Congenital Adrenal Hyperplasia | Physical Activity | Exercise CapacityTurkey
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Apollo Therapeutics LtdNot yet recruitingMyelodysplastic Syndrome With Excess Blasts | Acute Myeloid Leukemia, in Relapse | Acute Myeloid Leukemia Refractory | Myelodysplastic Syndrome Acute Myeloid Leukemia
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Hans BahlmannLinkoeping UniversityRecruitingRenal Cancer | Ureter Cancer | Other Specified Disorders of Kidney and Ureter | Benign Neoplasm of Ureter | Calculus of Kidney and Ureter | Ureteric Reflux | Congenital Ureteric Anomaly | Benign Renal NeoplasmSweden
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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Foundation For Rare Disease ResearchInstitute for Asthma & Allergy; Virant Diagnostics, Inc.; MedBio Reference Laboratories...Not yet recruitingAngioedema | Urticaria | C1 Inhibitor Deficiency | Angioedemas, Hereditary | Mastocytosis | Indolent Systemic Mastocytosis | Systemic Mastocytoses | ACE Inhibitor-Induced Angioedema
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McGill University Health Centre/Research Institute...Canadian Institutes of Health Research (CIHR)RecruitingZellweger Spectrum DisorderCanada
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Azienda Ospedaliero-Universitaria di ModenaRecruitingTurner Syndrome | Anomaly HeartItaly
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Five Liters, Inc.RecruitingHeavy Menstrual Bleeding | Von Willebrand Disease, Type 1United States
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Masonic Cancer Center, University of MinnesotaRecruiting
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Assiut UniversityRecruitingBehcet's Disease With Multisystem InvolvementEgypt
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University Hospital, Strasbourg, FranceRecruitingRheumatoid Arthritis | Systemic Lupus Erythematosus | Sjogren's Syndrome | GoutFrance
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Assistance Publique - Hôpitaux de ParisBraintaleNot yet recruitingX-linked Adrenoleukodystrophy
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Minoryx Therapeutics, S.L.RecruitingCerebral Adrenoleukodystrophy (cALD)United States, Brazil, Argentina
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Woman's Health University Hospital, EgyptRecruitingPCOS (Polycystic Ovary Syndrome) of Bilateral OvariesQatar
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IRCCS Policlinico S. DonatoUniversity of MilanRecruitingMarfan Syndrome | Rare Diseases | Ehlers-Danlos SyndromeItaly
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Centre Hospitalier Universitaire DijonNovartis PharmaceuticalsRecruitingMegalencephaly-capillary Malformation Polymicrogyria Syndrome (MCAP)France
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University of Wisconsin, MadisonRecruitingCerebral Autosomal Dominant Ateriopathy With Subcortical Infarcts and LeukoencephalopathyUnited States
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University of MinnesotaRecruitingDNA Repair Disorder | Xeroderma Pigmentosum | Cockayne Syndrome | TrichothiodystrophyUnited States
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AC Immune SAWorldwide Clinical TrialsRecruitingAlzheimer's Disease | Prodromal Alzheimer's Disease | Amyloid Plaque | Beta-Amyloid | Alzheimer's Disease in Down SyndromeUnited States, Spain, United Kingdom
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University of Erlangen-Nürnberg Medical SchoolRecruitingAutosomal Dominant Polycystic Kidney Disease | Uncontrolled Hypertension | Renal DenervationGermany
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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Poxel SANot yet recruiting
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West China HospitalRecruitingSarcoma | Lymphoma | Neuroblastoma | Wilms' Tumor | Teratoma | Germ Cell TumorChina
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingCardiovascular Disease | Arterial Stiffness | Germline Mutation in the NOTCH 3 Gene | Pathogenesis of CADASIL | Clinical Phenotype of CADASILUnited States
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University of Colorado, DenverRecruitingTurner SyndromeUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...IRCCS Azienda Ospedaliero-Universitaria di Bologna; Hospital Clinic of Barcelona and other collaboratorsRecruitingFamilial Adenomatous PolyposisNetherlands
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C. R. BardRecruitingArteriovenous Fistula | End-stage Renal Disease | Kidney Disease, End-StageUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingStage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor | Recurrent Kidney Wilms Tumor | Anaplastic Kidney Wilms TumorUnited States, Canada, Puerto Rico, Australia, New Zealand, Saudi Arabia
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Aesculap AGRecruitingMeningioma | Craniotomy | Hydrocephalus | Spinal Surgery | Tumor, Brain | Chiari Malformation | Vascular Malformation | Tethered Cord | Dural Fistula | DuraplastyGermany
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National Cancer Institute (NCI)RecruitingNeurofibromatosis Type 1 | Low Grade Glioma | Visual Pathway GliomaUnited States, Canada, Puerto Rico
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Wuerzburg University HospitalCharite University, Berlin, Germany; University Hospital Muenster; Health Care...RecruitingQuality of Life | Adherence, Medication | Fabry Disease | Rare DiseasesGermany
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Target PharmaSolutions, Inc.RecruitingPsoriasis | Atopic Dermatitis | Vitiligo | Hidradenitis Suppurativa | Alopecia Areata | Chronic Spontaneous UrticariaUnited States, Spain, Canada, Germany
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Edgar JaeggiLabatt Family Heart CentreRecruitingAtrial Flutter | Tachycardia, Supraventricular | Tachycardia, Atrioventricular Nodal Reentry | Tachycardia Atrial | Tachycardia, Reciprocating | Tachycardia, Paroxysmal | Fetal Hydrops | Tachycardia, Atrial EctopicUnited States, Hong Kong, Canada, Netherlands, Sweden, Australia, Brazil, Finland, France, Russian Federation, Spain, Czechia, Switzerland, United Kingdom
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases...RecruitingPyruvate Dehydrogenase Complex Deficiency DiseaseUnited States
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Children's Hospital of PhiladelphiaRecruitingParoxysmal Nocturnal Hemoglobinuria | Acquired Aplastic Anemia | Inherited Bone Marrow Failure SyndromesUnited States
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingIntellectual Disability | Tuberous Sclerosis | Autism DisorderUnited States
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsRecruitingCystinuria | Primary Hyperoxaluria | Dent Disease | APRT DeficiencyUnited States, Iceland
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Japan, Ireland, United Kingdom, France, Italy
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Kyowa Kirin Co., Ltd.Kyowa Hakko Kirin Pharma, Inc.Completed
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National Human Genome Research Institute (NHGRI)CompletedUndiagnosed Disease | Healthy Volunteer (Adult With Typically Developing Child) | Inherited Neurodegenerative Disorders | Inherited Metabolic Disorders (Inborn Errors of Metabolism) | Alzheimer's Disease and Related DementiasUnited States
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Tze-Woei TanBoston University; University of Southern California; University of Utah; Rancho...Active, not recruitingHemodialysis Access Failure | End Stage Renal Failure | Arterio-venous FistulaUnited States
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Sheffield Teaching Hospitals NHS Foundation TrustSociety for Endocrinology; The Clinical Endocrinology TrustCompletedCongenital Adrenal HyperplasiaUnited Kingdom
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Ultragenyx Pharmaceutical IncKyowa Kirin Co., Ltd.AvailableX-linked Hypophosphatemia | Tumor-Induced Osteomalacia
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National Institute of Allergy and Infectious Diseases...Enrolling by invitationSafety and Efficacy of Tofacitinib for Chronic Granulomatous Disease With Inflammatory ComplicationsChronic Granulomatous Disease | Inflammatory Gastrointestinal Disease | Inflammatory Skin Disease | Inflammatory Lung DiseaseUnited States
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom
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University of California, Los AngelesOregon Health and Science UniversityCompletedPolycystic Ovary Syndrome (PCOS)United States