- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Bone Marrow Failure Disorders
Total 9589 results
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Institute of Hematology & Blood Diseases HospitalRecruiting
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Novartis PharmaceuticalsRecruiting
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Silence Therapeutics plcRecruitingPolycythemia VeraUnited States, Australia, Malaysia, Bulgaria, Poland
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PharmaEssentiaRecruitingPolycythemia VeraUnited States, Canada
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Protagonist Therapeutics, Inc.RecruitingPolycythemia VeraUnited States, Hong Kong, Israel, Canada, Spain, Australia, Austria, Germany, United Kingdom, Hungary, Netherlands, Czechia, Portugal, Italy, Poland, France, Belgium, Chile, Turkey, Mexico
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University of BirminghamNovartis; National Cancer Institute, France; MPN VoiceRecruitingPolycythemia VeraUnited Kingdom
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Imago BioSciences, Inc., a subsidiary of Merck...Active, not recruitingPolycythemia VeraUnited States, Australia, United Kingdom
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PharmaEssentiaActive, not recruiting
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Novartis PharmaceuticalsAvailable
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AOP Orphan Pharmaceuticals AGPharmaEssentia Corporation (for the U.S.)CompletedPolycythemia VeraSpain, Austria, Bulgaria, France, Germany, Hungary, Poland, Romania, Russian Federation, Slovakia, Ukraine, Czechia
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Kartos Therapeutics, Inc.UnknownPolycythemia VeraUnited States, Poland, Spain, Germany, Hungary, France
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ItalfarmacoCompletedPolycythemia VeraGermany, Poland, United Kingdom, Italy, France
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Incyte CorporationNovartis PharmaceuticalsCompletedPolycythemia VeraUnited States, Canada, France, Italy, United Kingdom, China, Belgium, Germany, Spain, Turkey, Japan, Australia, Korea, Republic of, Netherlands, Russian Federation, Argentina, Thailand, Hungary
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Incyte CorporationCompletedPolycythemia VeraUnited States, Belgium, Germany, Spain, Italy, United Kingdom, Ireland
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AOP Orphan Pharmaceuticals AGPharmaEssentia (Co-Sponsor for USA)CompletedPolycythemia VeraSpain, Belgium, Austria, Italy, Bulgaria, Czech Republic, France, Germany, Hungary, Poland, Romania, Russian Federation, Slovakia, Ukraine
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PV-NordCompleted
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Ronald HoffmanNational Cancer Institute (NCI); Myeloproliferative Disorders-Research ConsortiumWithdrawnPolycythemia Vera
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RecruitingHaploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion (HAPLOTAB)Myelodysplastic Syndromes | Primary Immunodeficiency Diseases | Hemoglobinopathies | Chronic Myeloid Leukemia | Cytopenia | Severe Aplastic Anemia | Bone Marrow Failure Syndrome | Acute Myeloid Leukemia in Remission | Hemophagocytic Lymphohistiocytoses | Acute Lymphoblastic Leukemia in Remission | Severe...United States
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Centre Leon BerardWithdrawnMyelodysplastic Syndromes | Severe Combined Immunodeficiency | Acute Leukemia | Haematological Malignancy | Hemoglobinopathy in Children | Bone Marrow AplasiaFrance
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Christopher DvorakNo longer availableAcute Myeloid Leukemia | Leukocyte Disorders | Acute Lymphoblastic Leukemia | Chronic Myeloid Leukemia | Myelodysplastic Syndrome | Cytopenias | Immune Deficiency | Lymphomas | Bone Marrow Failure | Osteopetrosis | Hemoglobinopathy | Anemia Due to Intrinsic Red Cell AbnormalityUnited States
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Medical College of WisconsinRecruitingBone Marrow Biopsy ProcedureUnited States
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Shaymaa Mohammed El-AwadyRecruitingAllogenic Bone Marrow TransplantationEgypt
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National Institutes of Health Clinical Center (CC)CompletedBone Marrow Stromal CellsUnited States
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University of MilanCompleted
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Hadassah Medical OrganizationCompletedCytomegalovirus | Bone Marrow TransplantationIsrael
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Vidacare CorporationCompletedBone Marrow Biopsy ProceduresUnited States, Spain
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Centre Hospitalier Universitaire de NīmesActive, not recruitingMyeloproliferative DisorderFrance
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National Research Center for Hematology, RussiaUnknownSeptic Shock | Nonchemotherapy Drug-induced Neutropenia | Neutropenia After Chemotherapy in Oncohematological Patients | Neutropenia in Patients With Aplastic AnemiaRussian Federation
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Stanford UniversityCompletedBone Marrow Transplant | Advance DirectivesUnited States
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National Institutes of Health Clinical Center (CC)CompletedBone Marrow Transplantation | Adaptation, PsychologicalUnited States
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Washington University School of MedicineRecruitingBreast NeoplasmsUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingLymphoma | Follicular Lymphoma | Acute Myeloid Leukemia | Multiple Myeloma | Myelofibrosis | Juvenile Myelomonocytic Leukemia | Burkitt Lymphoma | Acute Lymphoblastic Leukemia | Lymphoblastic Lymphoma | Chronic Lymphocytic Leukemia | Lymphoplasmacytic Lymphoma | Acute Leukemia | Mantle-Cell Lymphoma | Chronic Myelogenous... and other conditionsUnited States
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University of Alabama at BirminghamEnrolling by invitationHigh Risk Pregnancy | Bone MarrowUnited States
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St. Jude Children's Research HospitalCompletedStem Cell Transplant | Bone MarrowUnited States, Canada
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States
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PharmaEssentia Japan K.K.Recruiting
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PharmaEssentia Japan K.K.CompletedPolycythemia Vera (PV)Japan
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Baxalta now part of ShireCTI BioPharmaWithdrawn
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Northwestern UniversityNational Cancer Institute (NCI)WithdrawnPrimary Myelofibrosis | Polycythemia Vera | Myelofibrosis | Thrombocytopenia
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University Hospital FreiburgCompletedMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond SyndromeSpain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
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University of RochesterRecruitingLymphoma | Myelodysplastic Syndromes | Multiple Myeloma | Solid Tumor | Acute Leukemia | Aplastic Anemia | Chronic Leukemia | Immune Deficiency Disorder | Congenital Hematological Disorder | Metabolism DisorderUnited States
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Beth Israel Medical CenterCompletedImmune Thrombocytopenia | Myelodysplasia | Chemotherapy Induced Thrombocytopenia | Aplastic AnaemiaUnited States
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St. Jude Children's Research HospitalTerminatedPain | Bone Marrow DiseaseUnited States
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Sohag UniversityRecruiting
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Ionis Pharmaceuticals, Inc.RecruitingPhlebotomy Dependent Polycythemia VeraUnited States, Canada, Hungary, United Kingdom, Australia, Poland
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Fondazione per la Ricerca Ospedale MaggioreAOP Orphan Pharmaceuticals AGCompleted
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Assistance Publique Hopitaux De MarseilleUnknown
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TargeGenCompleted
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Novartis PharmaceuticalsCompletedMyelofibrosisFrance, United Kingdom, Belgium, Germany, Netherlands, Italy, Austria, Spain, Sweden
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Consorzio Mario Negri SudAgenzia Italiana del Farmaco; A.O. Ospedale Papa Giovanni XXIIITerminated