Example: Heart Attack
Clinical Trials on Brain Diseases, Metabolic, Inborn
Total 824 results
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NCT00472732CompletedConditions: Brain Diseases, Metabolic, Inborn; Urea Cycle Disorder; Ornithine Transcarbamylase Deficiency
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NCT00237315RecruitingConditions: Brain Diseases, Metabolic, Inborn; Amino Acid Metabolism, Inborn Errors; Urea Cycle Disorders
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NCT02254863RecruitingConditions: Adrenoleukodystrophy; Batten Disease; Mucopolysaccharidosis II; Leukodystrophy, Globoid Cell; Leukodystrophy, Metachromatic; Neimann Pick Disease; Pelizaeus-Merzbacher Disease; Sandhoff Disease; Tay-Sachs Disease; Brain Diseases, Metabolic, Inborn; Alpha-Mannosidosis; Sanfilippo Mucopolysaccharidoses
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NCT04675749RecruitingConditions: X-linked Adrenoleukodystrophy
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NCT03233841CompletedConditions: Farber Disease; Farber's Disease; Farber Lipogranulomatosis; Acid Ceramidase Deficiency; Ceramidase Deficiency; N-Laurylsphingosine Deacylase Deficiency; ASAH1 Mutation
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NCT04602325RecruitingConditions: Urea Cycle Disorder; Organic Acidemia; Maple Syrup Urine Disease; Glutaric Acidemia I; Fatty Acid Oxidation Disorder; Hypoxic-Ischemic Encephalopathy
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NCT01341379WithdrawnConditions: Urea Cycle Disorders, Inborn; Inborn Errors of Metabolism; Propionic Acidemia; Methylmalonic Acidemia; Carbamyl Phosphate Synthetase Deficiency
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NCT04248062CompletedConditions: Inborn Errors of Metabolism; Urea Cycle Disorder; Maple Syrup Urine Disease; Phenylketonurias; Methylmalonicacidemia; OTC Deficiency; Aminoacidopathy; Patient Reported Outcome Measurements
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NCT01780168RecruitingConditions: Oxidative Phosphorylation Deficiencies; Electron Transport Chain Disorders, Mitochondrial; Mitochondrial Disorders; Leigh Disease
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NCT00668564TerminatedConditions: Hurler's Syndrome; Maroteaux-Lamy Syndrome; Sly Syndrome; Alpha Mannosidosis; Fucosidosis; Aspartylglucosaminuria; Sphingolipidoses; Krabbe Disease; Wolman's Disease; Niemann-Pick Disease Type B; Niemann-Pick Disease, Type C
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NCT00176904CompletedConditions: Adrenoleukodystrophy; Metachromatic Leukodystrophy; Globoid Cell Leukodystrophy; Gaucher's Disease; Fucosidosis; Wolman Disease; Niemann-Pick Disease; Batten Disease; GM1 Gangliosidosis; Tay Sachs Disease; Sandhoff Disease
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NCT00007020CompletedConditions: Infantile Refsum's Disease; Zellweger Syndrome; Adrenoleukodystrophy; Peroxisomal Disorders; Cholestasis
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NCT02297347CompletedConditions: Phenylketonuria
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NCT00004307Unknown statusConditions: Amino Acid Metabolism, Inborn Errors
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NCT01917344CompletedConditions: Phenylketonuria
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NCT02410239WithdrawnConditions: Cerebral Adrenoleukodystrophy
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NCT03911089Active, not recruitingConditions: Urea Cycle Disorder; Inborn Errors of Metabolism
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NCT02948062WithdrawnConditions: Adrenoleukodystrophy
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NCT04204642RecruitingConditions: Cerebral Amyloid Angiopathy
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NCT00964236CompletedConditions: Phenylketonuria
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NCT04528706RecruitingConditions: Cerebral Adrenoleukodystrophy
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NCT03168399CompletedConditions: Phenylketonuria; Inborn Errors of Metabolism
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NCT03058848CompletedConditions: Phenylketonuria; Inborn Errors of Metabolism
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NCT03852498RecruitingConditions: Cerebral Adrenoleukodystrophy (CALD)
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NCT02124330CompletedConditions: Urea Cycle Disorders, Inborn; Other Metabolic Diseases