Clinical Trials on Brain Diseases, Metabolic in United States
Total 147447 results
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University of MiamiHRSA/Maternal and Child Health BureauCompletedPhenylketonuria | Inborn Errors of Metabolism | GalactosemiaUnited States
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States
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Boston Children's HospitalBioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
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University of NebraskaCompleted
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University Hospitals Cleveland Medical CenterBioMarin PharmaceuticalCompleted
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The University of Texas Medical Branch, GalvestonTerminated
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Boston Children's HospitalBioMarin PharmaceuticalCompleted
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Oregon Health and Science UniversityTerminated
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Lumos DiagnosticsAptatek BiosciencesRecruiting
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Emory UniversityBioMarin PharmaceuticalRecruitingPhenylketonuriasUnited States
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Rubius TherapeuticsTerminated
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Boston Children's HospitalBrigham and Women's HospitalCompletedPhenylketonuriaUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedPhenylketonuriaUnited States
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University of Missouri-ColumbiaBioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Emory UniversityAtlanta Clinical and Translational Science InstituteCompleted
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The University of Texas Health Science Center,...BioMarin PharmaceuticalTerminatedPhenylketonuria | HyperphenylalaninemiaUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedPhenylketonuriaUnited States
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The University of Texas Health Science Center,...BioMarin PharmaceuticalCompleted
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Emory UniversityTerminated
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University of MinnesotaRecruitingGaucher DiseaseUnited States
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TakedaCompletedGaucher DiseaseUnited States
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Genzyme, a Sanofi CompanyCompleted
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Brigham and Women's HospitalGenzyme, a Sanofi CompanyUnknown
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Brendan LeeCompleted
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Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher DiseaseUnited States
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Vitaflo International, LtdOregon Health and Science UniversityCompleted
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Children's Hospital Medical Center, CincinnatiBioMarin PharmaceuticalCompleted
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University of MiamiCompletedPhenylketonuriaUnited States
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Children's Hospital of PhiladelphiaCompleted
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University of Southern CaliforniaNational PKU AllianceActive, not recruitingPhenylketonuriasUnited States
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Emory UniversityBioMarin Pharmaceutical; Atlanta Clinical and Translational Science InstituteCompletedPhenylketonuriaUnited States
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TakedaCompleted
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Washington University School of MedicineUniversity of Missouri-Columbia; BioMarin PharmaceuticalCompleted
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Shoji YanoBioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Duke UniversityRecruiting
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Amicus TherapeuticsTerminatedType 1 Gaucher DiseaseUnited States, United Kingdom
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SanofiCompletedGaucher's DiseaseUnited States
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National Institute of Neurological Disorders and...Completed
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University of MinnesotaRecruitingGaucher Disease, Type 3United States
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PfizerWithdrawnType 1 Gaucher DiseaseUnited States
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National Institute of Neurological Disorders and...CompletedType 2 Gaucher DiseaseUnited States
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Taysha Gene Therapies, Inc.Withdrawn
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University of Missouri-ColumbiaBioMarin PharmaceuticalEnrolling by invitationPhenylketonuriasUnited States
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University of Wisconsin, MadisonBoston Children's HospitalCompletedPhenylketonuriaUnited States
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Children's National Research InstituteGeorgetown UniversityWithdrawn
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NYU Langone HealthGenzyme, a Sanofi CompanyCompleted
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Applied Therapeutics, Inc.Active, not recruiting
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States