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Clinical Trials on Bulbo-Spinal Atrophy, X-Linked
Total 1850 results
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Stanford UniversityCompletedDevelopmental Disabilities | Fragile X SyndromeUnited States
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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University of Sao Paulo General HospitalAgência Brasileira de Desenvolvimento Industrial (Brazilian Agency For Industrial...Not yet recruitingBrain Injuries | Spinal Cord Injuries | Muscle AtrophyBrazil
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IRCCS Fondazione Stella MarisAzienda USL Toscana Nord Ovest; University of Dublin, Trinity College; Meyer...Recruiting
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Neurogene Inc.RecruitingRett SyndromeUnited States
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University of SienaRecruiting
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Vyant BioNot yet recruiting
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Rett Syndrome Research TrustVanderbilt University Medical CenterCompleted
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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ACADIA Pharmaceuticals Inc.Completed
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Rett Syndrome Research TrustCompleted
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National Human Genome Research Institute (NHGRI)CompletedRett SyndromeUnited States
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Anagnostou, Evdokia, M.D.Unity Health Toronto; Holland Bloorview Kids Rehabilitation Hospital; Ontario...Unknown
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Assistance Publique Hopitaux De MarseilleUnknown
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationCompleted
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Sheba Medical CenterUltragenyx Pharmaceutical IncUnknown
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Central Hospital, Nancy, FranceCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...Terminated
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Sheba Medical CenterUnknown
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Maastricht University Medical CenterCompleted
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Faculdades Metropolitanas UnidasUniversity of Sao PauloCompleted
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityCompletedRett Syndrome
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Eunice Kennedy Shriver National Institute of Child...UnknownRett SyndromeUnited States
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Stanford UniversityNational Heart, Lung, and Blood Institute (NHLBI); University of California... and other collaboratorsCompletedMuscular Dystrophy, DuchenneUnited States
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UMC UtrechtCompletedSpinal Muscular Atrophy | SMA | Kugelberg-Welander DiseaseNetherlands
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Nova Mentis Life Science CorpFourthWall TestingRecruitingAutism Spectrum Disorder | Fra(X) SyndromeUnited States
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Fundación Pública Andaluza para la Investigación...Delos ClinicalCompleted
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Bar-Chama, Natan, M.D.RecruitingFertility IssuesUnited States
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Kevin FlaniganMuscular Dystrophy AssociationTerminated
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BioLeaders CorporationCompleted
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Summit TherapeuticsCompletedModified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced DietMuscular Dystrophy, DuchenneUnited Kingdom
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University Hospital, Basel, SwitzerlandNovartisCompletedRett's SyndromeSwitzerland
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Hubert Serve, Prof., MDUnknown
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Stanford UniversityCompletedIntellectual Disability | Fragile X SyndromeUnited States
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Parc de Salut MarHospital Infantil Universitario Niño Jesús, Madrid, Spain; Hospital Universitario... and other collaboratorsCompletedDown Syndrome | Fragile X SyndromeSpain
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Children's Hospital of Fudan UniversityRecruiting
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, United Kingdom
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRecruiting
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... and other collaboratorsRecruiting
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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Edison Pharmaceuticals IncWithdrawn
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Anavex Life Sciences Corp.Completed
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompleted
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Neuren Pharmaceuticals Limitedrettsyndrome.orgCompleted
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUnknownRett SyndromeDenmark, Israel
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Rigshospitalet, DenmarkCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)CompletedRett SyndromeUnited States
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Edison Pharmaceuticals IncCompleted
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Boston Children's HospitalInternational Rett Syndrome FoundationCompleted