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Clinical Trials on Bulbo-Spinal Atrophy, X-Linked
Total 1844 results
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Zhongmou TherapeuticsRecruitingX-linked RetinoschisisChina
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Shanghai General Hospital, Shanghai Jiao Tong University...Innostellar BiotherapeuticsRecruitingX-linked RetinoschisisChina
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Kaohsiung Medical University Chung-Ho Memorial...National Taiwan University Hospital; Mackay Memorial Hospital; Shin Kong Wu Ho-Su... and other collaboratorsCompletedNatural History of Type 1 Spinal Muscular Atrophy (SMA)
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Tehran University of Medical SciencesUnknownInfantile Spinal Muscular Atrophy, Type I [Werdnig- Hoffman]Iran, Islamic Republic of
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Nemours Children's ClinicCompletedMuscular Dystrophy | Spinal Muscular Atrophy | Arthrogryposis
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Rigshospitalet, DenmarkCompletedSpinal Muscular Atrophy | Merosin Deficient Congenital Muscular DystrophyDenmark
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Applied Genetic Technologies CorpCompletedX-linked RetinoschisisUnited States
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Hospices Civils de LyonNot yet recruitingSpinal Muscular AtrophyFrance
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Hoffmann-La RocheRecruiting
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingSpinal Muscular AtrophyItaly
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First Affiliated Hospital of Fujian Medical UniversityPeking Union Medical College Hospital; Fujian Medical University Union HospitalRecruiting
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Mahidol UniversityRecruitingSpinal Muscular AtrophyThailand
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Assistance Publique - Hôpitaux de ParisRecruitingSpinal Muscular AtrophyFrance
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Assistance Publique - Hôpitaux de ParisRecruiting
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, Canada, France, Poland, Brazil, Croatia, Italy, Russian Federation, Turkey, Germany, Serbia, United Kingdom
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Hoffmann-La RocheActive, not recruitingSpinal Muscular AtrophyBelgium, United States, United Kingdom, France, Poland, Italy, Switzerland, Netherlands, Germany
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Centre Hospitalier Universitaire de NiceActive, not recruitingSpinal Muscular AtrophyFrance
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BiogenCompletedSpinal Muscular AtrophyUnited States, Spain, Germany, United Kingdom, Australia, Japan, Canada, Belgium, France, Hong Kong, Italy, Korea, Republic of, Sweden, Turkey
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Novartis PharmaceuticalsCompleted
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BiogenActive, not recruitingMuscular Atrophy, SpinalUnited States, Spain, Germany, Italy, Israel
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Dr. Stéphanie DelstancheQueen Fabiola Children's University Hospital; Erasme University Hospital; SYSNAV and other collaboratorsActive, not recruiting
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyBelgium, Germany, Italy, Russian Federation, Poland, Bulgaria, Denmark
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NYU Langone HealthWinthrop University HospitalWithdrawnSpinal Muscular AtrophyUnited States
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Catalyst Pharmaceuticals, Inc.CompletedMuscular Atrophy, SpinalItaly
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BiogenCompleted
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BiogenCompleted
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Hoffmann-La RocheCompletedSpinal Muscular AtrophyUnited States
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CytokineticsAstellas Pharma Global Development, Inc.CompletedSpinal Muscular AtrophyUnited States, Canada
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National Institute of Neurological Disorders and...Completed
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Kaohsiung Medical University Chung-Ho Memorial...National Taiwan University Hospital; Mackay Memorial Hospital; China Medical... and other collaboratorsUnknown
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National Institute of Neurological Disorders and...Completed
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University of UtahCompleted
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Columbia UniversityCompletedSpinal Muscular AtrophyUnited States
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All India Institute of Medical Sciences, New DelhiUnknown
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Kaohsiung Medical University Chung-Ho Memorial...Completed
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Arcispedale Santa Maria Nuova-IRCCSUnknown
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Novartis PharmaceuticalsActive, not recruitingType 2 Spinal Muscular AtrophyUnited States, China, Saudi Arabia, Thailand, Singapore, Brazil, Malaysia, Taiwan, Colombia, Mexico, Denmark, Egypt, India, South Africa, Vietnam
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Hoffmann-La RocheCompletedHealthy Volunteer, Muscular Atrophy, SpinalSwitzerland
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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Edimer PharmaceuticalsCompletedX-linked Hypohidrotic Ectodermal Dysplasia | Hypohidrotic Ectodermal DysplasiaUnited States
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Edimer PharmaceuticalsCompletedX-linked Hypohidrotic Ectodermal Dysplasia | Hypohidrotic Ectodermal DysplasiaSpain
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Lantu BiopharmaNot yet recruitingSpinal Muscular Atrophy
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Robert Jones and Agnes Hunt Orthopaedic and District...University Hospital Birmingham NHS Foundation TrustRecruitingSpinal Muscular AtrophyUnited Kingdom
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Hoffmann-La RocheNot yet recruiting
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NMD Pharma A/SRecruitingSpinal Muscular AtrophyUnited States, Spain, Belgium, Denmark, Germany, Netherlands, Italy, Canada
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Fondazione Policlinico Universitario Agostino Gemelli...Bambino Gesù Hospital and Research Institute; University of Messina; University... and other collaboratorsRecruitingSpinal Muscular AtrophyItaly
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Holland Bloorview Kids Rehabilitation HospitalRecruiting