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Clinical Trials on Bulbo-Spinal Atrophy, X-Linked
Total 1844 results
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National Taiwan University HospitalNot yet recruiting
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Fondazione Policlinico Universitario Agostino Gemelli...IRCCS Eugenio Medea; Azienda Ospedaliera Universitaria Policlinico "G. Martino... and other collaboratorsNot yet recruitingSpinal Muscular Atrophy
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Hoffmann-La RocheRecruiting
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GeneCradle IncRecruitingSpinal Muscular AtrophyChina
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Fondazione Policlinico Universitario Agostino Gemelli...University of Milan; Ospedale Pediatrico Bambino GesùRecruiting
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University of Castilla-La ManchaRecruiting
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University of OxfordHoffmann-La Roche; Oxford University Hospitals NHS Trust; Novartis Gene TherapiesRecruiting
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Genentech, Inc.RecruitingSpinal Muscular AtrophyUnited States, Puerto Rico
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Bakri ElsheikhGenentech, Inc.RecruitingSpinal Muscular AtrophyUnited States
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BiogenRecruiting
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSpinal Muscular AtrophyUnited Kingdom
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Kaohsiung Medical University Chung-Ho Memorial...The Chinese Foundation of Health; Taipei Institute of PathologyRecruiting
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Hospital Israelita Albert EinsteinBiogenActive, not recruitingSpinal Muscular AtrophyBrazil, Argentina, Chile, Colombia, Mexico, Uruguay
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Hospices Civils de LyonCompletedSpinal Muscular AtrophyFrance
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Istanbul Medipol University HospitalActive, not recruitingMuscular Atrophy, SpinalTurkey
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University of UtahAbbott; Leadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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BiogenActive, not recruitingSpinal Muscular AtrophyUnited States, Taiwan, Israel, Australia, Qatar, United Kingdom, Turkey, Italy, Germany, Argentina, Canada
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Columbia UniversityThe Spinal Muscular Atrophy FoundationCompleted
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University Medical Centre LjubljanaCompleted
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Ohio State UniversityBiogen; Cure SMACompleted
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Institut de Myologie, FranceCompletedSpinal Muscular AtrophyFrance
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Centre Hospitalier Régional de la CitadelleRoche Pharma AG; Biogen; AveXis, Inc.; Association Belge contre les Maladies neuro...CompletedSpinal Muscular AtrophyBelgium
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BiogenCompletedSpinal Muscular AtrophyUnited States
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BiogenCompletedSpinal Muscular AtrophyUnited States, Canada
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BiogenTerminatedSpinal Muscular AtrophyKorea, Republic of, United States, Spain, Canada, Germany, Australia, Japan, Sweden, Belgium, France, Italy, Turkey, United Kingdom
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BiogenTerminatedSpinal Muscular AtrophyUnited States, Germany
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United BioSource, LLCAveXis, Inc.Approved for marketing
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National Institute of Neurological Disorders and...Terminated
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United Kingdom, Germany, France, Italy, Netherlands, Poland
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University of Texas Southwestern Medical CenterCompleted
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Hoffmann-La RocheTerminatedMuscular Atrophy, SpinalFrance, Turkey, Canada, United States, Italy, Netherlands, Sweden, Switzerland, United Kingdom
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National Taiwan University HospitalCompleted
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University of UtahEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedSpinal Muscular AtrophyUnited States
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University of UtahAbbott; Leadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States, Canada
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University of Sao Paulo General HospitalCompletedSpinal Muscular AtrophyBrazil
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National Taiwan University HospitalUnknown
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University Hospital, Strasbourg, FranceRecruitingFeasibility of Neonatal Screening for Spinal AmyotrophyFrance
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University of California, Los AngelesNational Heart, Lung, and Blood Institute (NHLBI); Boston Children's Hospital; California Institute for Regenerative Medicine (CIRM) and other collaboratorsRecruitingGranulomatous Disease, Chronic, X-linkedUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Centre Hospitalier Régional de la CitadelleCompletedSafety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3 (EMOTAS)Spinal Muscular Atrophy Type 3Belgium
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular Atrophy Type IKorea, Republic of, Taiwan, Japan
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Stanford UniversityCompletedA Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy PatientsMuscular Atrophy, SpinalUnited States
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University of UtahLeadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular Atrophy Type IUnited States, Canada, Germany
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Ankara City Hospital BilkentCompletedAnesthesia | Child, Only | Muscular Atrophy, SpinalTurkey
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University of Erlangen-Nürnberg Medical SchoolCompletedMuscular Diseases | Spinal Muscular AtrophyGermany
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University of Erlangen-Nürnberg Medical SchoolUnknownMuscular Diseases | Spinal Muscular AtrophyGermany
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Applied Genetic Technologies CorpFoundation Fighting BlindnessCompletedX-linked Retinoschisis | XLRSUnited States
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Charles University, Czech RepublicRecruiting
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BiogenCompletedSpinal Muscular AtrophyGermany
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Centre d'Investigation Clinique et Technologique...CompletedSpinal Muscular Atrophy | Assessment, SelfFrance