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Clinical Trials on Bulbo-Spinal Atrophy, X-Linked
Total 1856 results
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Cedars-Sinai Medical CenterCompletedBecker Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterTerminatedMuscular DystrophyUnited States
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Cedars-Sinai Medical CenterParent Project Muscular DystrophyCompleted
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Eli Lilly and CompanyTerminatedMuscular Dystrophy, DuchenneGermany, United States, Spain, Belgium, France, Italy, Taiwan, Netherlands, Turkey, Korea, Republic of, Argentina, Canada, Japan, Puerto Rico, Russian Federation, United Kingdom
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Wave Life Sciences Ltd.CompletedDuchenne Muscular DystrophyBelgium, United Kingdom, France, United States, Italy, Canada, Netherlands
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedDuchenne Muscular DystrophyUnited States
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Washington University School of MedicineUniversity of California, Davis; Nationwide Children's Hospital; University of... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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BioMarin PharmaceuticalCompletedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
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Children's Hospital of Eastern OntarioCompletedDuchenne Muscular DystrophyCanada
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Cooperative International Neuromuscular Research...UnknownBecker Muscular DystrophyUnited States, Canada, Italy, United Kingdom
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | BalanceTurkey
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National Human Genome Research Institute (NHGRI)Completed
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Kevin FlaniganWithdrawnDuchenne Muscular DystrophyUnited States
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyNetherlands, Belgium, Italy, Sweden
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BioMarin PharmaceuticalNo longer availableDuchenne Muscular DystrophyUnited States, Germany, United Kingdom, Japan, Netherlands, France, Spain, Korea, Republic of, Italy, Belgium, Taiwan, Argentina, Australia, Bulgaria, Czechia, Israel, Norway, Poland, Russian Federation, Turkey
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Assiut UniversityUnknownDuchenne Muscular Dystrophy
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited Kingdom, Italy, Belgium, Netherlands, France
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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University of Sao PauloCompletedDuchenne Muscular Dystrophy
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University of Sao PauloCompletedDuchenne Muscular DystrophyBrazil
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GenethonInstitute of MyologyUnknownDuchenne Muscular DystrophyUnited Kingdom, France
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Sarepta Therapeutics, Inc.British Medical Research CouncilCompletedDuchenne Muscular DystrophyUnited Kingdom
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Kobe UniversityNobelpharma; Japan Medical AssociationUnknownMuscular Dystrophy, DuchenneJapan
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Cooperative International Neuromuscular Research...UnknownDuchenne Muscular DystrophyUnited States, Canada
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Alan Neuromedical Technologies, LLCCompleted
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Acibadem UniversityUnknownDuchenne Muscular DystrophyTurkey
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GlaxoSmithKlineCompletedMuscular DystrophiesGermany, Belgium, Turkey, Netherlands, Spain, Israel, Australia, France, United Kingdom
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University of MessinaCompleted
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Cedars-Sinai Medical CenterCompleted
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Cooperative International Neuromuscular Research...United States Department of DefenseTerminated
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Cedars-Sinai Medical CenterMuscular Dystrophy AssociationCompleted
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Rigshospitalet, DenmarkGlostrup University Hospital, CopenhagenCompletedBecker Muscular DystrophyDenmark
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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Santhera PharmaceuticalsCompletedDuchenne Muscular DystrophyBelgium
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Assistance Publique - Hôpitaux de ParisCompletedMuscular Dystrophy, DuchenneFrance
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National Center for Research Resources (NCRR)Children's National Research InstituteCompletedMuscular Dystrophy, DuchenneUnited States
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Ohio State UniversityCompletedSpinal Cord Injuries | Metabolic Disease | Skeletal Muscle AtrophyUnited States
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IRCCS San RaffaeleRecruiting
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ENCellNot yet recruitingDuchenne Muscular DystrophyKorea, Republic of
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Not yet recruiting
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Sqy TherapeuticsBiotrialRecruitingDuchenne Muscular DystrophyFrance
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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PfizerRecruitingDuchenne Muscular DystrophyUnited States
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Gülsena UtkuRecruiting
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Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital Medical... and other collaboratorsRecruiting
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Samsung Medical CenterRecruitingDuchenne Muscular DystrophyKorea, Republic of
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Sohag UniversityNot yet recruitingDuchenne Muscular DystrophyEgypt
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Massachusetts General HospitalBoston Children's HospitalRecruitingDuchenne Muscular DystrophyUnited States
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University of PittsburghRecruitingDuchenne Muscular DystrophyUnited States