- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Bulbo-Spinal Atrophy, X-Linked
Total 1852 results
-
Jiangsu Gensciences lnc.CompletedFactor VII Deficiency | Hemophilia A With Inhibitor | Hemophilia B With InhibitorChina
-
Groupe Maladies hémorragiques de BretagneCompletedHemophilia A | Hemophilia B | Anticoagulant-induced BleedingFrance
-
Duke UniversityUniversity of FloridaCompleted
-
Ultragenyx Pharmaceutical IncCompletedOrnithine Transcarbamylase DeficiencyUnited States
-
Washington University School of MedicineCompletedBarth Syndrome
-
Institut National de la Santé Et de la Recherche...RecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multiple Sulfatase Deficiency Disease | Mucopolysaccharidosis IXFrance
-
Arcturus Therapeutics, Inc.RecruitingOTC Deficiency | Ornithine Transcarbamylase Deficiency | OTCDSpain, Belgium, United Kingdom, Sweden
-
Children's Hospital of Fudan UniversityRecruitingBCG | Vitamin D3 | Chronic-granulomatous DiseaseChina
-
Masonic Cancer Center, University of MinnesotaRecruitingAplastic Anemia | Dyskeratosis CongenitaUnited States
-
National Institute of Allergy and Infectious Diseases...Active, not recruitingChronic Granulomatous Disease TransplantUnited States
-
Stealth BioTherapeutics Inc.CompletedBarth SyndromeUnited States
-
Fondazione TelethonOspedale San RaffaeleActive, not recruitingWiskott-Aldrich SyndromeItaly, United States
-
David WilliamsActive, not recruitingWiskott-Aldrich SyndromeUnited States
-
American Thrombosis and Hemostasis NetworkTakeda; CSL Behring; OctapharmaCompletedHemophilia A | Hemophilia B | Hemophilia | Hemophilia A With Inhibitor | Haemophilia | Hemophilia B With Inhibitor | Haemophilia A Without Inhibitor | Haemophilia B Without InhibitorUnited States
-
Ultragenyx Pharmaceutical IncTerminatedOrnithine Transcarbamylase DeficiencyUnited States
-
National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...Enrolling by invitationGranulomatous Disease, ChronicUnited States, Canada
-
National Institute of Allergy and Infectious Diseases...CompletedAtherosclerosis | Chronic Granulomatous Disease (CGD)United States
-
GenethonInstitute of Child Health; Great Ormond Street Hospital for Children NHS Foundation...Completed
-
GlaxoSmithKlineCompletedWiskott-Aldrich SyndromeUnited States
-
GenethonHôpital Necker-Enfants MaladesCompleted
-
Masonic Cancer Center, University of MinnesotaCompletedAplastic Anemia | Dyskeratosis CongenitaUnited States
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Netherlands, Austria, Spain, Germany, Macedonia, The Former Yugoslav Republic of, Taiwan, United Kingdom, Italy, Malaysia, Thailand, France, Greece, Turkey, Japan, South Africa, Romania
-
National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous Disease | Communicable DiseaseUnited States
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Sweden, Spain, Germany, United Kingdom, Denmark, France, Japan
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia B | HaemostasisUnited States
-
Stephen G. Kaler, MDRecruitingMenkes Disease | Occipital Horn SyndromeUnited States
-
Jakub AntczakCompletedAdrenomyeloneuropathy | Hereditary Spastic ParaplegiaPoland
-
National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease | InfectionUnited States
-
National Institute of Allergy and Infectious Diseases...Enrolling by invitationChronic Granulomatous Disease | p47 | Autosomal RecessiveUnited States
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Canada, United Kingdom, France, Malaysia, Brazil, Croatia, Germany, Italy, Japan, Taiwan
-
GenethonActive, not recruitingWiskott-Aldrich SyndromeUnited Kingdom, France
-
Washington University School of MedicineCompleted
-
Northwell HealthNational Cancer Institute (NCI); University of California, San DiegoCompletedHemophilia A | Hemophilia B | HemarthrosesUnited States
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Netherlands, Austria, Spain, Germany, Macedonia, The Former Yugoslav Republic of, Taiwan, United Kingdom, Italy, Malaysia, Thailand, France, Greece, Russian Federation, Turkey, Japan, South Africa, Romania
-
Capital Research Institute of PediatricsUnknownWiskott-Aldrich Syndrome
-
St. Jude Children's Research HospitalCompletedWiskott-Aldrich SyndromeUnited States
-
American Thrombosis and Hemostasis NetworkLFB USA, Inc.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorUnited States
-
American Thrombosis and Hemostasis NetworkGenentech, Inc.Active, not recruitingHemophilia A With Inhibitor | Hemophilia B With Inhibitor | Haemophilia A Without Inhibitor | Haemophilia B Without InhibitorUnited States
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Switzerland, Germany
-
Baylor College of MedicineActive, not recruitingFocal Dermal Hypoplasia (FDH) | Goltz SyndromeUnited States
-
Stealth BioTherapeutics Inc.AvailableMitochondrial Diseases | Barth Syndrome
-
Catalyst BiosciencesCompletedHemophilia A | Hemophilia B | Hemophilia A With Inhibitor | Hemophilia B With Inhibitor | Hemophilia A Without Inhibitor | Hemophilia B Without InhibitorBulgaria, Russian Federation
-
National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...CompletedWiskott-Aldrich SyndromeUnited States, Canada
-
Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, Spain, United Kingdom, France, Germany
-
The Korean Society of Pediatric Hematology OncologyCompletedWiskott-Aldrich SyndromeKorea, Republic of
-
Children's Hospital of PhiladelphiaIllumina, Inc.Active, not recruitingMucopolysaccharidoses | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2 Gangliosidosis | Zellweger... and other conditionsUnited States
-
Karunesh GangulyNational Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingStroke | Multiple Sclerosis | Muscular Dystrophies | ALS | SCI - Spinal Cord InjuryUnited States
-
Military University Hospital, PragueUnknownCerebral Palsy | Pineal Gland Disorder | Corpus Callosum Atrophy
-
National Institute for Mother and Child Health...Marie Curie Emergency Children's Hospital, Bucharest; Victor Gomoiu Children...RecruitingChronic Granulomatous DiseaseRomania
-
Ultragenyx Pharmaceutical IncActive, not recruitingOrnithine Transcarbamylase (OTC) DeficiencyCanada, United States, France, Spain, United Kingdom