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Clinical Trials on Candidates for BRCA 1/2 Genetic Testing
Total 854 results
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Expansion Therapeutics, Inc.CompletedMyotonic Dystrophy | Myotonic Dystrophy, Type 1 (DM1)United States
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Baxalta now part of ShireArriva Pharmaceuticals, Inc.CompletedAlpha1-antitrypsin DeficiencyUnited States
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Grifols Therapeutics LLCCompletedAlpha₁-Antitrypsin DeficiencyUnited States
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Vertex Pharmaceuticals IncorporatedRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, Canada, Australia
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Dyne TherapeuticsRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, France, Netherlands, Italy, Germany, New Zealand
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Grifols Therapeutics LLCGrifols Japan K.K.CompletedAlpha1-Antitrypsin DeficiencyJapan
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Baxalta now part of ShireArriva Pharmaceuticals, Inc.CompletedAlpha1-antitrypsin DeficiencyUnited States
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Grifols Therapeutics LLCActive, not recruitingPulmonary Emphysema in Alpha-1 PI DeficiencyUnited States, Australia, Denmark, New Zealand, Estonia, Poland, Russian Federation, Sweden, Brazil, Canada, France, Finland
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Avidity Biosciences, Inc.CompletedMyotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert DiseaseUnited States
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Schön Klinik Berchtesgadener LandGrifols Therapeutics LLC; Alpha-1 FoundationCompletedChronic Obstructive Pulmonary Disease | Alpha-1-antitrypsin-deficiencyGermany
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BIOTRONIK IsraelCompletedMyocardial Ischemia | Coronary Artery Disease | Diabetes Mellitus Type 1 or 2Israel
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University of Colorado, DenverOmni Bio Pharmaceutical, Inc.CompletedDiabetes | Type 1 DiabetesUnited States
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; Association...Unknown
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Edimer PharmaceuticalsCompletedX Linked Hypohidrotic Ectodermal DysplasiaUnited States
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Centre Hospitalier Universitaire DijonCompletedDiabetes Type 1 or 2 With Diabetic RetinopathyFrance
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Université du Québec à ChicoutimiRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
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Grifols Therapeutics LLCRecruiting
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Vertex Pharmaceuticals IncorporatedCompletedAlpha1-Antitrypsin DeficiencyUnited States, Germany, Canada, Ireland, Sweden, United Kingdom
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Grifols Therapeutics LLCGrifols Japan K.K.Completed
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Baxalta now part of ShireCompletedAlpha1-antitrypsin DeficiencyUnited States, Canada
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Baxalta now part of ShireTerminated
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Edimer PharmaceuticalsActive, not recruitingX-linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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Edimer PharmaceuticalsCompletedX-Linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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Grifols Therapeutics LLCEnrolling by invitationPulmonary Emphysema in Alpha-1 Antitrypsin DeficiencyUnited States, New Zealand, Denmark, Australia, Finland, Estonia, Canada, Poland, Russian Federation, Sweden, France
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Jin FengUnknown1、Enough Cases | 2、Elekta Precise 1343 Digital Control Electron Linear Accelerator | Can Undertake Nasopharyngeal Carcinoma Specimens in the Materia, | Image Department of Nose Pharynx Ministry MRI Dynamic Testing,China
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Kamada, Ltd.CompletedType 1 Diabetes MellitusIsrael
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BIOTRONIK Asia Pacific Pte LtdCompletedMyocardial Ischemia | Coronary Artery Disease | Diabetes Mellitus Type 1 or 2China, India, Malaysia, Vietnam, Sri Lanka
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Edimer PharmaceuticalsCompletedX-Linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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Edimer PharmaceuticalsCompletedHypohidrotic Ectodermal Dysplasia | X-Linked Hypohidrotic Ectodermal DysplasiaUnited States
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Edimer PharmaceuticalsNational Foundation of Ectodermal DysplasiaCompletedHypohidrotic Ectodermal Dysplasia | X-Linked Hypohidrotic Ectodermal DysplasiaUnited States
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Z Factor LimitedHammersmith Medicines Research; Centessa Pharmaceuticals plcTerminatedAlpha1 Anti-Trypsin DeficiencyUnited Kingdom
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Baxalta now part of ShireCompleted
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RWTH Aachen UniversityUnknown
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TakedaEnrolling by invitationAlpha1-Antitrypsin DeficiencyUnited Kingdom, Germany, United States, Austria, Portugal
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Alnylam PharmaceuticalsCompletedPrimary Hyperoxaluria Type 1 (PH1)France, United Kingdom, Netherlands, Israel, Germany
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University of Michigan Rogel Cancer CenterCSL Behring; The Leukemia and Lymphoma SocietyCompletedGraft vs Host DiseaseUnited States
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Ionis Pharmaceuticals, Inc.Not yet recruitingMethyl CpG Binding Protein 2 (MECP2) Duplication Syndrome
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Krystal Biotech, Inc.Active, not recruitingTGM-1 Related Autosomal Recessive Congenital IchthyosisUnited States
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TakedaRecruitingAlpha1-Antitrypsin DeficiencyItaly, United States, Poland, Portugal
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TakedaTakeda Development Center Americas, Inc.RecruitingAlpha1-Antitrypsin DeficiencyUnited States, Belgium, Switzerland, Canada, Australia, Germany, United Kingdom, Austria, France, Spain, Portugal, Italy, Poland, Brazil
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Adrian LacyUltragenyx Pharmaceutical IncCompletedGlucose Transporter Type-1 Deficiency Syndrome (Glut1 DS)United States
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Alnylam PharmaceuticalsTerminatedAntitrypsin Deficiency Liver DiseaseUnited Kingdom
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Soroka University Medical CenterUnknownPost Cardiac Surgery Systemic Inflammatory Response
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University of Alabama at BirminghamCompletedNeurofibromatosis Type 1 and Growing or Symptomatic, Inoperable PNUnited States
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Metabolic Fitness Association, ItalyUniversity of Roma La SapienzaActive, not recruitingType 1 Diabetes | Type 2 DiabetesItaly
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University Hospital, SaarlandWithdrawnEmphysema | Chronic Obstructive Lung Disease | Alpha-1-Antitrypsin DeficiencyDenmark, Germany
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Cadent TherapeuticsWithdrawnSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxias | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6 | Spinocerebellar Ataxia Type 10 | Spinocerebellar Ataxia Type 7 | Spinocerebellar Ataxia Type 8 | Spinocerebellar Ataxia Type 17 | ARCA1 - Autosomal Recessive...United States
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Centre Oscar LambretCTD-CNO; Laboratoire PRISMActive, not recruitingBRCA1 Mutation | BRCA2 Mutation | Hereditary Breast and Ovarian CancerFrance
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Avidity Biosciences, Inc.RecruitingPhase 1/2 Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD) (FORTITUDE)Muscular Dystrophies | Muscular Dystrophy, Facioscapulohumeral | FSHD | Facio-Scapulo-Humeral Dystrophy | FMD | Facioscapulohumeral Muscular Dystrophy 1 | FSHD2 | FSHD1 | FMD2 | Fascioscapulohumeral Muscular Dystrophy | Fascioscapulohumeral Muscular Dystrophy Type 1 | Fascioscapulohumeral Muscular Dystrophy... and other conditionsUnited States, United Kingdom, Canada
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University of FloridaCompletedAlpha-1 Antitrypsin Deficiency | Liver Fibrosis | AATD | AAT DeficiencyUnited States