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Clinical Trials on Carbohydrate Metabolism, Inborn Errors in Korea, Republic of
Total 220 results
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Green Cross CorporationCompleted
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Green Cross CorporationUnknownThe Long-term Safety Study of Idursulfase-beta in Hunter Syndrome(Mucopolysaccharidosis II) PatientsHunter SyndromeKorea, Republic of
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Green Cross CorporationCompleted
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Tehran University of Medical SciencesUnknownMucopolysaccharidosisIran, Islamic Republic of
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Seoul National University HospitalCompleted
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GC Biopharma CorpRecruitingMucopolysaccharidosis II | Hunter SyndromeKorea, Republic of
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JW PharmaceuticalRecruitingGoutKorea, Republic of
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JW PharmaceuticalCompletedGoutKorea, Republic of
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Sang Hak LeeUnknownMixed HyperlipidemiaKorea, Republic of
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HLB Cell Co., Ltd.WithdrawnUrea Cycle DisorderKorea, Republic of
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Korea United Pharm. Inc.Active, not recruiting
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Green Cross CorporationCompletedMucopolysaccharidosis IIKorea, Republic of
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Kuhnil Pharmaceutical Co., Ltd.UnknownHyperlipidemia, Familial CombinedKorea, Republic of
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CinnagenCompletedMucopolysaccharidosis Type 1Iran, Islamic Republic of
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JW PharmaceuticalCompletedHyperuricemia | GoutKorea, Republic of
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JW PharmaceuticalCompletedHyperuricemia | GoutKorea, Republic of
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Kyowa Kirin Korea Co., Ltd.RecruitingFGF23-related Hypophosphataemic Rickets and OsteomalaciaKorea, Republic of
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Yonsei UniversityRecruitingFabry DiseaseKorea, Republic of
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Yonsei UniversityRecruitingFabry DiseaseKorea, Republic of
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Yonsei UniversityRecruitingFabry's DiseaseKorea, Republic of
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Yonsei UniversityRecruitingFabry DiseaseKorea, Republic of
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Kyowa Kirin Co., Ltd.CompletedX-linked Hypophosphatemic Rickets/OsteomalaciaJapan, Korea, Republic of
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SanofiRecruitingOsteochondrodysplasiaAustralia, Spain, Korea, Republic of, China, Italy
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ISU Abxis Co., Ltd.RecruitingFabry DiseaseKorea, Republic of
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Chong Kun Dang PharmaceuticalUnknownMixed HyperlipidemiaKorea, Republic of
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Isfahan University of Medical SciencesUnknownFamilial HypercholesterolemiaIran, Islamic Republic of
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University of TehranCompletedHypercholesterolemia, FamilialIran, Islamic Republic of
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Agios Pharmaceuticals, Inc.RecruitingPyruvate Kinase DeficiencyUnited States, Germany, Spain, Italy, United Kingdom, Czechia, France, Canada, Korea, Republic of, Netherlands, Turkey, Portugal, Denmark, Ireland, Switzerland, Thailand
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Bundang CHA HospitalCompletedHutchinson-Gilford Progeria SyndromeKorea, Republic of
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Agios Pharmaceuticals, Inc.Active, not recruitingPyruvate Kinase DeficiencyUnited States, Spain, Japan, Canada, United Kingdom, Korea, Republic of, Ireland, Thailand, Italy, Turkey, Denmark, Brazil, France, Germany, Netherlands, Switzerland
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BioMarin PharmaceuticalCompletedMPS IV AUnited States, Canada, France, United Kingdom, Taiwan, Argentina, Colombia, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, Germany, Portugal, Italy, Qatar
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Kyowa Kirin Co., Ltd.CompletedA Study of KRN23 in Adult and Pediatric Patients With X-linked Hypophosphatemic Rickets/OsteomalaciaXLHJapan, Korea, Republic of
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Agios Pharmaceuticals, Inc.CompletedAnemia, Hemolytic | Pyruvate Kinase DeficiencyUnited States, Spain, Switzerland, Turkey, Germany, France, United Kingdom, Japan, Netherlands, Brazil, Canada, Czechia, Denmark, Italy, Korea, Republic of, Thailand
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Green Cross CorporationCompleted
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Seoul National University HospitalCompletedDiabetes Mellitus Type 2 | Carbohydrate IntoleranceKorea, Republic of
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BioMarin PharmaceuticalTerminatedLate-onset Pompe Patients Untreated or Treated With rhGAASpain, Slovenia, Serbia, Korea, Republic of, Greece, Australia, Singapore, Brazil, Canada, Taiwan, Ireland, Poland, Romania
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Yungjin Pharm. Co., Ltd.CompletedMELAS Syndrome | Mitochondrial Respiratory Chain DeficienciesKorea, Republic of
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Isfahan University of Medical SciencesCompletedTangier Disease | Body Mass Index Quantitative Trait Locus 7 DisorderIran, Islamic Republic of
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Isfahan University of Medical SciencesCompletedTangier Disease | Body Mass Index Quantitative Trait Locus 5 DisorderIran, Islamic Republic of
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Netherlands
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Tehran University of Medical SciencesMashhad University of Medical Sciences; Kashan University of Medical SciencesRecruitingEffects of Miglustat Therapy on Infantile Type of Sandhoff and Taysachs Diseases (EMTISTD) (EMTISTD)Supportive Care | GM2 GangliosidosisIran, Islamic Republic of
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Genzyme, a Sanofi CompanyCompleted
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | Mucopolysaccharidosis VII | MPS VIISpain, United States, Portugal
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SanofiRecruitingGlycogen Storage Disease Type IIBelgium, United States, Italy, Spain, Taiwan, United Kingdom, Netherlands, France, Germany
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SanofiRecruitingGlycogen Storage Disease Type IIBelgium, United States, China, Germany, Italy, Netherlands, Spain, Taiwan, United Kingdom
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IV AUnited States, Canada, France, Taiwan, Argentina, Colombia, Spain, Turkey, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, United Kingdom, Germany, Norway, Portugal, Italy, Qatar
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Isfahan University of Medical SciencesUnknownAcute Coronary Syndrome | Familial Hypercholesterolemia | Cardiac EventIran, Islamic Republic of
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Genzyme, a Sanofi CompanyRecruitingMucopolysaccharidosis I (MPS I)Croatia, United States, Argentina, Australia, Belgium, Brazil, Canada, Denmark, France, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Lebanon, Malaysia, Netherlands, Pakistan, Philippines, Poland, Saudi Arabia, Singapore, Slovaki... and more
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National Human Genome Research Institute (NHGRI)RecruitingInborn Errors of Metabolism | Methylmalonic Acidemia | Organic AcidemiaUnited States