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Clinical Trials on Ceramidase Deficiency in Australia
Total 299 results
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Spark TherapeuticsCompletedHematologic Diseases | Hemophilia A | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Blood Coagulation Disorder | Factor VIII DeficiencyUnited States, Australia, Thailand, Canada
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Kirby InstituteThe Alfred; Peter MacCallum Cancer Centre, Australia; St Vincent's Hospital; Monash... and other collaboratorsActive, not recruitingHIV Infections | AgingAustralia
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BayerCompletedMale | Androgens (Deficiency)Italy, Spain, Austria, Finland, United Kingdom, Germany, Ireland, Sweden
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BioCryst PharmaceuticalsCompletedHereditary Angioedema (HAE)Canada, United Kingdom, Germany, Spain, Australia, Hungary, Italy, Austria, North Macedonia, Denmark, Switzerland
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CSL BehringCompletedEmphysema | Alpha1-proteinase Inhibitor DeficiencyAustralia, Russian Federation, United States, Denmark, Estonia, Finland, Germany, Ireland, Poland, Romania, Sweden, Canada, Czech Republic
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Hoffmann-La RocheWithdrawn
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University of California, San FranciscoNational Institute of Allergy and Infectious Diseases (NIAID); Monash University and other collaboratorsCompletedHIV | Human Immunodeficiency VirusUnited States, Australia
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Medical University of ViennaCompletedSecondary Hyperparathyroidism | CKD-MBD - Chronic Kidney Disease Mineral and Bone Disorder | Kidney ReplacementAustria
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Intellia TherapeuticsActive, not recruitingHereditary AngioedemaFrance, New Zealand, Germany, United Kingdom, Netherlands, Australia
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Orthopedic Hospital Vienna SpeisingCompleted
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Medical University of ViennaCompletedPolycystic Ovary Syndrome | Infertility, Female | Micronutrient DeficiencyAustria
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Kirby InstituteNational Heart, Lung, and Blood Institute (NHLBI); St Vincent's Hospital, SydneyCompletedCardiovascular Disease | HIV-Associated Lipodystrophy SyndromeAustralia
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rEVO BiologicsCompletedAntithrombin III DeficiencyUnited States, France, United Kingdom, Germany, Canada, Austria, Australia, Italy
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Kirby InstituteMerck Sharp & Dohme LLCCompletedHIV InfectionAustralia
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OctapharmaRecruitingCongenital Antithrombin DeficiencySpain, Italy, United States, Serbia, France, Hungary, Austria, Germany, United Kingdom, Israel
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Premier Specialists, AustraliaUnknownEpidermolysis Bullosa Simplex | Epidermolysis Bullosa Simplex Kobner | Weber-Cockayne SyndromeAustralia
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Versartis Inc.Premier Research Group plcCompletedAdult Growth Hormone DeficiencyUnited States, Australia, Germany, United Kingdom
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Murdoch Childrens Research InstituteRoyal Children's HospitalCompletedPrimary Immunodeficiency | Invasive Pneumococcal Disease, Protection Against | Invasive Pneumococcal Disease, Recurrent Isolated, 1 | Invasive Pneumococcal Disease, Recurrent Isolated, 2Australia, New Zealand
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Andrew CarrViiV Healthcare Australia Pty. LtdCompletedHuman Immunodeficiency VirusAustralia
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireTerminatedChronic Obstructive Pulmonary Disease | Alpha1-antitrypsin DeficiencyUnited States, Canada, Australia
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Medical University of GrazTechnical University of Munich; Paracelsus Medical University; University of... and other collaboratorsRecruitingInflammation | Obesity | Atherosclerosis | Fatty Liver | Adiponectin DeficiencyAustria
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St Vincent's Hospital, SydneyMerck Sharp & Dohme LLCTerminatedHuman Immunodeficiency Virus (HIV) | HIV Associated Neurocognitive Disorders (HAND)Australia
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Bruce BrewViiV HealthcareCompletedHuman Immunodeficiency Virus (HIV) | HIV Associated Neurocognitive Disorders (HAND)Australia
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Teva Branded Pharmaceutical Products R&D, Inc.TerminatedGrowth Hormone DeficiencyUnited States, Austria, Czechia, Greece, Hungary, Italy, Russian Federation
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Arbeitsgemeinschaft medikamentoese TumortherapieMerck Sharp & Dohme LLCCompleted
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Inhibrx, Inc.RecruitingEmphysema | Alpha 1-Antitrypsin DeficiencyUnited States, Australia, United Kingdom, New Zealand
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TakedaEnrolling by invitationAlpha1-Antitrypsin DeficiencyUnited Kingdom, Germany, United States, Austria, Portugal
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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Ascendis Pharma Endocrinology Division A/SCompletedA Safety, Tolerability and Efficacy Study of TransCon hGH in Children With Growth Hormone DeficiencyEndocrine System Diseases | Pituitary Diseases | Hormone Deficiency | Growth Hormone Deficiency, PediatricUnited States, Canada, Australia, New Zealand
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OctapharmaCompletedPrimary ImmunodeficiencyUnited Kingdom, Australia, Germany, Italy
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Medical University of ViennaCompletedHIV Infections | Ocular Physiology | RetinaAustria
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Ascendis Pharma Endocrinology Division A/SActive, not recruitingEndocrine System Diseases | Adult Growth Hormone Deficiency | Hormone DeficiencyUnited States, Armenia, Georgia, Greece, Ukraine, Australia, Canada, France, Israel, Italy, Japan, Malaysia, Poland, Romania, Serbia, Slovakia, Spain, Turkey, United Kingdom, Germany, Korea, Republic of
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Pharvaris Netherlands B.V.Active, not recruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Poland, Germany, Austria, Bulgaria, Canada, Ireland, Italy, United Kingdom
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Origin BiosciencesCompletedMolybdenum Cofactor DeficiencyUnited States, Australia, United Kingdom, Germany, Netherlands, Turkey
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Ultragenyx Pharmaceutical IncCompletedGlucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)United States, Spain, Australia, France, Israel, Italy, United Kingdom
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Novo Nordisk A/SCompletedGrowth Hormone Disorder | Growth Hormone Deficiency in ChildrenFrance, Israel, Austria, Spain, Switzerland, North Macedonia, Norway, Slovenia, Belgium, Sweden
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Lumos PharmaActive, not recruitingGrowth Hormone DeficiencyUnited States, Australia, Israel, New Zealand, Poland, Ukraine
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Queensland Centre for Gynaecological CancerGlaxoSmithKline Research & Development LimitedNot yet recruitingMmr Deficiency | Endometrial Cancer Stage I | Immune-related Adverse Event | Endometrioid Endometrial AdenocarcinomaAustralia
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ShireCompletedHereditary Angioedema (HAE)United States, Canada, Australia, Austria, Colombia, Germany, Hungary, Israel, Italy, Spain
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Medical University of GrazMedical University of Vienna; University Hospital, Essen; Goethe University; Guy... and other collaboratorsRecruitingCritical Illness | Covid19 | Vitamin D DeficiencyAustria, Belgium
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Grifols Therapeutics LLCEnrolling by invitationPulmonary Emphysema in Alpha-1 Antitrypsin DeficiencyUnited States, New Zealand, Denmark, Australia, Finland, Estonia, Canada, Poland, Russian Federation, Sweden, France
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Moritz OberndorferMerck Gesellschaft mbH, AustriaCompletedHIV Infections | Diabetes Mellitus | Dyslipidemias | Cardiovascular Risk FactorAustria
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Novo Nordisk A/SRecruitingGrowth Hormone Disorder | Growth Hormone Deficiency in ChildrenUnited States, Japan, Israel, India, Austria, Slovenia, Belgium, Brazil, France, Germany, Sweden, Turkey, Ukraine
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AEterna ZentarisCompletedGrowth Hormone Deficiency With Pituitary AnomaliesUnited Kingdom, United States, France, Poland, Spain, Austria, Germany, Italy, Serbia
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American Regent, Inc.Duke Clinical Research InstituteCompletedHeart Failure | Iron-deficiencyUnited States, Canada, Australia, Bulgaria, Georgia, New Zealand, Latvia, Hungary, Poland, Czechia, Lithuania, Russian Federation, Ukraine
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BeiGeneTerminatedMetastatic Castration-Resistant Prostate Cancer (mCRPC) | Homologous Recombination Deficiency (HRD)United States, Australia, Puerto Rico, Spain
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Ascendis Pharma A/SCompletedEndocrine System Diseases | Pituitary Diseases | Hormone Deficiency | Growth Hormone Deficiency, PediatricUnited States, Armenia, Belarus, Bulgaria, Georgia, Greece, Russian Federation, Ukraine, Australia, New Zealand, Poland
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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AstraZenecaRecruitingAdvanced Solid Tumours That Are MTAP DeficientUnited States, Spain, Korea, Republic of, Australia, Japan, China, Netherlands, France