Clinical Trials on Cerebrotendinous Xanthomatoses in New Zealand

Total 5 results

  • Travere Therapeutics, Inc.
    Unknown
    Cerebrotendinous Xanthomatosis (CTX)
    United States
  • US Department of Veterans Affairs
    Withdrawn
    Cerebrotendinous Xanthomatosis
    United States
  • Mirum Pharmaceuticals, Inc.
    Completed
  • Albert Einstein College of Medicine
    Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaborators
    Enrolling by invitation
    Mucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditions
    United States
  • The Hospital for Sick Children
    Active, not recruiting
    Rare Histiocytic Disorders (RHDs) | Juvenile Xanthogranuloma (JXG) | Reticulohistiocytoma (Epithelioid Histiocytoma) | Xanthoma Disseminatum (XD) | Multicentric Reticulohistiocytosis (MRH) | Systemic Juvenile Xanthogranuloma | Erdheim-Chester Disease (ECD) | Multi-system Rosai-Dorfman Disease (RDD)
    Canada, United States, Poland, Argentina, Austria, Czechia, Germany, Italy, Russian Federation, Spain
3
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