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Clinical Trials on Congenital Muscular Dystrophy Type 1A
Total 7569 results
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Newcastle UniversityRecruitingFacioscapulohumeral Muscular DystrophyUnited Kingdom
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Hillel Yaffe Medical CenterRecruiting
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University of Kansas Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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Robert Jones and Agnes Hunt Orthopaedic and District...CompletedFacioscapulohumeral Muscular Dystrophy
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Hugo W. Moser Research Institute at Kennedy Krieger...Concord Hospital; FSHD Global Research FoundationCompletedFacioscapulohumeral Muscular DystrophyUnited States, Australia
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Bioblast Pharma Ltd.CompletedMuscular Dystrophy, Oculopharyngeal (OPMD)Canada
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Rigshospitalet, DenmarkUnknownOculopharyngeal Muscular DystrophyDenmark
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Centre Hospitalier Universitaire de NiceCompletedFacioscapulohumeral Muscular DystrophyFrance
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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InCor Heart InstituteUniversity of Sao Paulo; Federal University of Minas GeraisCompletedMyocardial Fibrosis | Muscular Dystrophies
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, United Kingdom
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Belgium, Australia, Canada, France, Germany, Israel, Italy, Spain, Sweden, United Kingdom
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University Hospital, AngersFederico II University; University of Modena and Reggio EmiliaNot yet recruitingFacioscapulohumeral Muscular Dystrophy
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Centre Hospitalier Universitaire de NiceCompletedMuscular DystrophiesFrance
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University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
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University of Kansas Medical CenterNational Institutes of Health (NIH)CompletedFacioscapulohumeral Muscular DystrophyUnited States
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Istanbul University - Cerrahpasa (IUC)CompletedFacioscapulohumeral Muscular DystrophyTurkey
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Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedFacioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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University of New MexicoUniversity of FloridaWithdrawnOculopharyngeal Muscular Dystrophy
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Bioblast Pharma Ltd.CompletedOculopharyngeal Muscular DystrophyUnited States, Israel, Canada
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Radboud University Medical CenterUnknownMyotonic Dystrophy Type 2 | McArdle Disease | Nemaline Myopathy Type 6
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Nationwide Children's HospitalBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedCardiomyopathy | Duchenne Muscular Dystrophy (DMD)United States
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Centre Hospitalier Universitaire de NiceCompletedFacio-Scapulo-Humeral DystrophyFrance
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University Hospital, Clermont-FerrandCompletedCharcot-Marie-Tooth Type 1A NeuropathyFrance
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth Disease | Facioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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IRCCS San RaffaeleRecruiting
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ENCellNot yet recruitingDuchenne Muscular DystrophyKorea, Republic of
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Not yet recruiting
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Percheron TherapeuticsRecruitingDuchenne Muscular DystrophyTurkey, United Kingdom, Australia, Serbia, Bulgaria
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Sqy TherapeuticsBiotrialRecruitingDuchenne Muscular DystrophyFrance
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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PfizerRecruitingDuchenne Muscular DystrophyUnited States
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Gülsena UtkuRecruiting
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Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital Medical... and other collaboratorsRecruiting
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Samsung Medical CenterRecruitingDuchenne Muscular DystrophyKorea, Republic of
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Sohag UniversityNot yet recruitingDuchenne Muscular DystrophyEgypt
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Massachusetts General HospitalBoston Children's HospitalRecruitingDuchenne Muscular DystrophyUnited States
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University of PittsburghRecruitingDuchenne Muscular DystrophyUnited States
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Ning Wang, MD., PhD.Recruiting
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CHU de Quebec-Universite LavalRecruitingDuchenne Muscular DystrophyCanada
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitationDuchenne Muscular DystrophyUnited States
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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Daiichi Sankyo Co., Ltd.Orphan Disease Treatment Institute Co., Ltd.Completed
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Belgium, Spain, United Kingdom, Netherlands, Germany, Canada, Italy
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Lokman Hekim ÜniversitesiCompletedDuchenne Muscular DystrophyTurkey
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Capricor Inc.Active, not recruiting
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States