- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Congenital Abnormalities in Austria
Total 1412 results
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyTaiwan, Belgium, Canada, United States, Australia, France, Italy, Portugal, United Kingdom
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisCanada, France, Germany, United Kingdom, Israel, Australia, Spain, Netherlands, Denmark, Switzerland
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University Medicine GreifswaldRecruitingRetinopathy of PrematurityGermany, Greece, Austria, Bulgaria, Estonia, France, Kosovo, Poland, Spain, Switzerland, Turkey, Ukraine
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia B | Hemophilia B With InhibitorUnited States, Spain, Australia, Taiwan, France, United Kingdom, Italy, Turkey, Armenia, India, Germany
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PedNet Haemophilia Research FoundationLund University HospitalRecruitingFactor IX Deficiency | Factor VIII DeficiencyNorway, Austria, Belgium, Canada, Czechia, Denmark, Finland, France, Germany, Greece, Ireland, Israel, Italy, Netherlands, Portugal, Spain, Sweden, Switzerland, United Kingdom
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Kymera Therapeutics, Inc.CompletedAtopic Dermatitis | Healthy Volunteer | Hidradenitis SuppurativaUnited States
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedHemophilia AUnited States, Poland, United Kingdom, Netherlands, South Africa, Hong Kong, Australia, Ireland
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Ralexar Therapeutics, Inc.Unknown
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic Neuropathy (LHON)United States, United Kingdom, Spain, Poland, Austria, Belgium, Bulgaria, Germany, Italy, Portugal
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | HAEUnited States, Austria, Canada, Czechia, France, Germany, Hungary, North Macedonia, Romania, Spain, United Kingdom
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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Genzyme, a Sanofi CompanyCompletedHemophiliaUnited States, Australia, China, Denmark, France, Ireland, Israel, Italy, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Mexico
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Eli Lilly and CompanyDermira, Inc.CompletedAtopic DermatitisUnited States, Canada, Australia, Poland
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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BiogenTerminatedCognitive Dysfunction | Alzheimer's DiseaseUnited States
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
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AbbVieEuropean Organisation for Research and Treatment of Cancer - EORTCCompletedGlioblastomaUnited States, Australia, Austria, Belgium, Canada, Czechia, Finland, France, Germany, Hungary, Ireland, Italy, Korea, Republic of, Mexico, Netherlands, Poland, Singapore, Spain, Switzerland, Taiwan, United Kingdom
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, France, United Kingdom, Germany, Belgium, Denmark, Canada, Australia, Sweden
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Ionis Pharmaceuticals, Inc.RecruitingAlexander DiseaseUnited States, United Kingdom, Australia, Canada, Israel, Italy, Japan, Netherlands
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Sangamo TherapeuticsEnrolling by invitationFabry Disease | Fabry Disease, Cardiac VariantUnited States, Australia, United Kingdom
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaIsrael, Korea, Republic of, Taiwan, Sweden, Germany, Italy, Turkey, China, Poland, United States, France, Australia, Thailand, United Kingdom, Mexico, Vietnam, Argentina, Belgium, Brazil, Canada, Spain
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaCzechia, France, Denmark, Netherlands, Austria, Mexico, Spain, United States, Argentina, Brazil, Bulgaria, Canada, Finland, Hungary, Italy, Lebanon, Norway, Poland, Russian Federation, Slovenia, South Africa, Sweden, Taiwan, Turkey
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Revolution Medicines, Inc.SanofiCompletedSolid TumorUnited States, Korea, Republic of
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisCanada, France, United Kingdom, Israel, Australia, Spain, Germany, Netherlands, Denmark, Switzerland
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Novartis PharmaceuticalsActive, not recruitingSpinal Muscular AtrophyJapan, Belgium, Spain, Canada, United States, Australia, Italy, France, Netherlands
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | Prophylaxis | HAEAustria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Switzerland, United Kingdom, United States, Australia, Hong Kong, Korea, Republic of, New Zealand, Serbia, Slovakia, South Africa, Spain
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Suzhou Connect Biopharmaceuticals, Ltd.CompletedModerate-to-severe Atopic DermatitisUnited States, Australia, China, New Zealand
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Novartis PharmaceuticalsTerminated
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SanofiCompletedAtopic DermatitisNetherlands, Chile, United States, Canada, Czechia, Germany, Poland
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisFrance, Spain, Belgium, Netherlands, Australia, Italy, Czechia
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Astellas Pharma Global Development, Inc.Active, not recruitingStargardt's Macular DystrophyItaly, United States, Israel, United Kingdom, Germany, Spain, Hungary, France
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PrileniaHuntington Study Group; European Huntington's Disease NetworkCompletedHuntington's DiseaseUnited States, Australia, Austria, Canada, Denmark, France, Germany, Italy, Netherlands, Poland, Russian Federation, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
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BayerCompletedHemophilia ABelgium, New Zealand, Netherlands, Greece, United Kingdom, Austria, United States, Italy, Romania, Bulgaria, Canada, Israel, Poland, Lithuania, Norway, Argentina, Spain
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PfizerCompletedPlaque Psoriasis | Atopic DermatitisUnited States, Australia, Canada, Poland
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Genzyme, a Sanofi CompanyActive, not recruitingHemophiliaChina, Hungary, Turkey, Canada, Korea, Republic of, United States, Australia, Denmark, France, Germany, India, Ireland, Israel, Italy, Japan, Malaysia, South Africa, Taiwan, Ukraine, United Kingdom
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Austria, Czechia, Germany, Hungary, Italy, Netherlands, North Macedonia, Poland, United Kingdom
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ShireCompletedHunter SyndromeUnited States, Spain, Canada, United Kingdom, Mexico, Australia, France
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Vertex Pharmaceuticals IncorporatedModerna, IncRecruitingCystic FibrosisUnited States, United Kingdom, Australia, Canada
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AstraZenecaCompletedAtopic DermatitisUnited States, Germany, Australia, Spain, United Kingdom, Poland
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PTC TherapeuticsCompletedPhenylketonuriaSpain, United States, Australia, Germany, United Kingdom, Brazil, Denmark, Canada, France, Georgia, Italy, Mexico, Netherlands, Portugal, Turkey
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PfizerCompletedDermatitis, AtopicChina, United States, Australia, Poland, Hungary, Korea, Republic of, Germany, Bulgaria, Canada, Czechia, Japan, Latvia, United Kingdom
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy, Australia
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SK Life Science, Inc.RecruitingSeizures | Lennox Gastaut SyndromeUnited States, Korea, Republic of, Taiwan, Colombia, Australia, Poland, Serbia, Mexico, Spain, Greece, Italy, Portugal, Germany, Argentina, Israel
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Novartis PharmaceuticalsCompletedChronic Iron Overload Due to Transfusion-dependant AnemiasItaly, Austria, Thailand, Spain, Germany, Mexico, Malaysia, Greece, United Kingdom, France, Saudi Arabia, United Arab Emirates, Lebanon, Russian Federation, United States, Argentina
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AbbVieCompletedAtopic DermatitisUnited States, Australia, Canada, Croatia, Czechia, Finland, France, Germany, Hungary, Ireland, Israel, Italy, Malaysia, Netherlands, New Zealand, Norway, Poland, Singapore, Spain, Taiwan, Ukraine, United Kingdom
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Belgium, Spain, United Kingdom, Netherlands, Germany, Canada, Italy