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Clinical Trials on Congenital Fibrinogen Deficiency in New Zealand
Total 2333 results
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EMD SeronoCompletedPituitary Dwarfism | Childhood-onset Growth Hormone DeficiencyUnited States
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State University of New York - Upstate Medical...CompletedBreast DiseaseUnited States
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Zynerba Pharmaceuticals, Inc.Enrolling by invitationFragile X SyndromeUnited States, United Kingdom, New Zealand, Australia
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Columbia UniversityAlpha-1 FoundationRecruitingChronic Obstructive Pulmonary Disease | Acute Exacerbation Copd | Alpha-1 Anti-trypsin DeficiencyUnited States
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn... and other collaboratorsCompletedMethylmalonic Acidemia | Carbamoyl-Phosphate Synthase I Deficiency Disease | Propionic Acidemia, Type I and/or Type II | Ornithine Carbamoyltransferase DeficiencyUnited States
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Kirby InstituteCompletedHepatitis CAustralia, United States, United Kingdom, New Zealand, Switzerland, Canada, Germany, Netherlands
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Columbia UniversityAbbott NutritionRecruitingHeart Failure | Gut Microbiome | Nutritional DeficiencyUnited States
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Columbia UniversityAlpha-1 Foundation; Stony Wold-Herbert Fund, Inc.CompletedChronic Obstructive Pulmonary Disease | Emphysema | Alpha-1 Antitrypsin DeficiencyUnited States
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State University of New York - Upstate Medical...Carol M. Baldwin Breast Cancer Research Fund, Inc.TerminatedAbnormalities, Radiation-InducedUnited States
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University of RochesterCompletedPatent Ductus Arteriosus in Premature InfantsUnited States
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Applied GeneticsUnknownPrecancerous ConditionUnited States, Germany, United Kingdom
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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New York Medical CollegeChildren's Hospital of Philadelphia; Washington University School of Medicine; University of California, Los Angeles and other collaboratorsRecruitingEpstein-Barr Virus Infections | Primary Immune Deficiency DisorderUnited States
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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AO Foundation, AO SpineScoliosis Research SocietyCompletedAdult Spinal DeformityUnited States, Spain, Denmark, China, United Kingdom, Canada, Japan
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Wojciech ZarebaCompletedArrhythmogenic Right Ventricular CardiomyopathyUnited States
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University of California, San FranciscoCompletedPatent Ductus ArteriosusUnited States
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Stealth BioTherapeutics Inc.Active, not recruitingMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial Complex I Deficiency | Mitochondrial Pathology | Mitochondrial DNA Depletion | Mitochondrial DNA Mutation | Mitochondrial DNA Deletion | Mitochondrial Metabolism DefectSpain, United States, Italy, Netherlands, Australia, Germany, Hungary, New Zealand, Norway, United Kingdom
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Versartis Inc.CompletedPediatric Growth Hormone DeficiencyUnited States
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Cardiox CorporationTerminated
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Albany Medical CollegeEnrolling by invitation
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NYU Langone HealthNew York UniversityRecruiting
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Fresenius KabiIqvia Pty LtdCompletedMalnutrition | Nutritional Status | Protein Deficiency | Caloric DeficitKorea, Republic of, Philippines, Taiwan, Thailand, India, Indonesia, Vietnam
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IWK Health CentreThe Hospital for Sick Children; Sunnybrook Health Sciences Centre; Canadian Institutes... and other collaboratorsRecruitingPatent Ductus Arteriosus | Extreme PrematurityCanada
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EMD SeronoCompletedGrowth Hormone Deficiency | Growth FailureGermany
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Yale UniversityRecruiting
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Abbott Medical DevicesCompletedAtrial Septal DefectUnited States
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KalVista Pharmaceuticals, Ltd.TerminatedAngioedema, Hereditary, Types I and IIUnited States, Czechia, Germany, Hungary, Italy, North Macedonia, United Kingdom, Australia, Bulgaria, Canada, France, New Zealand, Puerto Rico
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Medtronic Heart ValvesActive, not recruitingCongenital Heart Disease | Pulmonary Regurgitation | Tetrology of Fallot | RVOT AnomalyUnited States, Canada, Japan
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Adrianna Vlachos, MDTerminatedPure Red Cell Aplasia | Diamond Blackfan AnemiaUnited States
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Children's Hospital Medical Center, CincinnatiRecruitingHypoplastic Left Heart Syndrome (HLHS)United States, United Kingdom, Canada
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Columbia UniversityGrifols Therapeutics LLCCompletedLung Transplantation | HypogammaglobulinemiaUnited States
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha 1 Antitrypsin Deficiency | AATDUnited States
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RWTH Aachen UniversityCompletedIron Deficiency | Heart Failure, SystolicGermany
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Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States
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University Hospital, EssenCompletedRight-Sided Heart Failure | Phosphodiesterase Inhibitor Adverse ReactionGermany
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Pharmacosmos A/SMax Neeman InternationalCompletedInflammatory Bowel DiseaseUnited Kingdom, Denmark, India
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W.L.Gore & AssociatesCompletedAtrial Septal DefectUnited States
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Edwards LifesciencesActive, not recruitingHeart Diseases | Cardiovascular Diseases | Congenital Abnormalities | Heart Defects, Congenital | Pulmonary Valve Insufficiency | Pulmonary Valve StenosisUnited States
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Fudan UniversityCompletedPregnancy Related | Fetal Heart Rate or Rhythm Abnormality Affecting Fetus | Uterine Contractions; Prolonged | Home RangeChina
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IpsenTerminatedPrimary Insulin-like Growth Factor-1 DeficiencyUnited States
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Watson PharmaceuticalsCompletedAnemiaUnited States, Poland, Mexico, Serbia, Russian Federation
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Emmaus Medical, Inc.FDA Office of Orphan Products DevelopmentCompletedSickle Cell Anemia | ThalassemiaUnited States
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NYU Langone HealthDyax Corp.WithdrawnHereditary Angioedema Types I and IIUnited States
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Abbott Medical DevicesTerminatedAtrial Septal Defect SecundumUnited States
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Mitchell CairoRecruitingHodgkin Lymphoma | Sickle Cell Disease | Acute Leukemia | Beta-Thalassemia | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Diamond Blackfan Anemia | Amegakaryocytic Thrombocytopenia | KostmannUnited States
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Teva Branded Pharmaceutical Products R&D, Inc.TerminatedGrowth Hormone DeficiencyUnited States, Austria, Czechia, Greece, Hungary, Italy, Russian Federation
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Abbott Medical DevicesCompletedMembranous Ventricular Septal DefectsUnited States
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State University of New York at BuffaloRecruitingCritical Illness | Nutritional Deficiency | Tracheostomy ComplicationUnited States